Newborn Screening and Emerging Therapies for X-Linked Adrenoleukodystrophy

被引:18
作者
Moser, Ann B. [1 ]
Fatemi, Ali [1 ]
机构
[1] Kennedy Krieger Inst, 707 N Broadway, Baltimore, MD 21205 USA
关键词
HEMATOPOIETIC-CELL TRANSPLANTATION;
D O I
10.1001/jamaneurol.2018.1585
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
引用
收藏
页码:1175 / 1176
页数:2
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