Newborn Screening and Emerging Therapies for X-Linked Adrenoleukodystrophy

被引：18
|
作者：
Moser, Ann B. [1 ]
Fatemi, Ali [1 ]
机构：
[1] Kennedy Krieger Inst, 707 N Broadway, Baltimore, MD 21205 USA
来源：
JAMA NEUROLOGY | 2018年 / 75卷 / 10期
关键词：
HEMATOPOIETIC-CELL TRANSPLANTATION;
D O I：
10.1001/jamaneurol.2018.1585
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：1175 / 1176
页数：2
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