Investigational Liver Gene Transfer of C1-INH for the Treatment of Hereditary Angioedema

被引：0

作者：

Riling, Christopher R. ^{[1
]}

Pankowicz, Frank ^{[1
]}

Hanby, Hayley ^{[1
]}

Scriver, Michelle ^{[1
]}

Ioele, Steve ^{[1
]}

Posternak-Ball, Valeriya ^{[1
]}

Quinn, William J. ^{[1
]}

Cohen, Daniel M. ^{[1
]}

Preston, George M. ^{[1
]}

Crosariol, Marco ^{[1
]}

Armour, Sean M. ^{[1
]}

Mingozzi, Federico ^{[1
]}

机构：

[1] Spark Therapeut Inc, Liver Res & Dev, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

359

引用

页码：177 / 178

页数：2

共 50 条

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