Investigational Liver Gene Transfer of C1-INH for the Treatment of Hereditary Angioedema

被引：0

作者：

Riling, Christopher R. ^{[1
]}

Pankowicz, Frank ^{[1
]}

Hanby, Hayley ^{[1
]}

Scriver, Michelle ^{[1
]}

Ioele, Steve ^{[1
]}

Posternak-Ball, Valeriya ^{[1
]}

Quinn, William J. ^{[1
]}

Cohen, Daniel M. ^{[1
]}

Preston, George M. ^{[1
]}

Crosariol, Marco ^{[1
]}

Armour, Sean M. ^{[1
]}

Mingozzi, Federico ^{[1
]}

机构：

[1] Spark Therapeut Inc, Liver Res & Dev, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

359

引用

页码：177 / 178

页数：2

共 50 条

[31] Considerations in the management of hereditary angioedema due to C1-INH deficiency in women of childbearing age [J].

Hsu, Florence Ida ;

Lumry, William ;

Riedl, Marc ;

Tachdjian, Raffi .

ALLERGY ASTHMA AND CLINICAL IMMUNOLOGY, 2022, 18 (01)

[32] A patient with hereditary angioedema (HAE) with normal C1-INH, and systemic lupus erythematosus with pregnancy [J].

Taha, Omar S. ;

Abi-Melhem, Racha ;

Taha, Yousef ;

Meyer, David ;

Assaad, Marc .

ALLERGY AND ASTHMA PROCEEDINGS, 2022, 43 (06) :567-567

[33] Considerations in the management of hereditary angioedema due to C1-INH deficiency in women of childbearing age [J].

Florence Ida Hsu ;

William Lumry ;

Marc Riedl ;

Raffi Tachdjian .

Allergy, Asthma & Clinical Immunology, 18

[34] Practicalities of a reduced volume formulation of a C1-INH concentrate for the treatment of hereditary angioedema: real-life experience [J].

John Dempster .

Allergy, Asthma & Clinical Immunology, 14

[35] Long-term treatment with Danazol increases expression of C1-INH mRNA in PBMC of patients with hereditary angioedema [J].

Cicardi, M ;

Pappalardo, E ;

Zingale, LC ;

Gioffré, D ;

Agostoni, A .

MOLECULAR IMMUNOLOGY, 1999, 36 (4-5) :313-313

[36] Practicalities of a reduced volume formulation of a C1-INH concentrate for the treatment of hereditary angioedema: real-life experience [J].

Dempster, John .

ALLERGY ASTHMA AND CLINICAL IMMUNOLOGY, 2018, 14

[37] Long-term treatment with danazol increases expression of C1-INH mRNA in PBMC of patients with hereditary angioedema [J].

Pappalardo, E ;

Zingale, LC ;

Gioffré, D ;

Agostoni, A ;

Cicardi, M .

FASEB JOURNAL, 2000, 14 (06) :A957-A957

[38] Adverse effects of danazol prophylaxis in female patients with hereditary angioedema due to C1-INH deficiency (HAE-C1-INH) [J].

Zotter, Z. ;

Czaller, I ;

Csuka, D. ;

Szabo, E. ;

Kohalmi, K., V ;

Varga, L. ;

Farkas, H. .

ALLERGY, 2013, 68 :430-430

[39] Clinical and genetic features of hereditary angioedema with and without C1-inhibitor (C1-INH) deficiency in Japan [J].

Hashimura, Chinami ;

Kiyohara, Chikako ;

Fukushi, Jun-Ichi ;

Hirose, Tomoya ;

Ohsawa, Isao ;

Tahira, Tomoko ;

Horiuchi, Takahiko .

ALLERGY, 2021, 76 (11) :3529-3534

[40] DIAGNOSING HEREDITARY ANGIOEDEMA (HAE) WITH NORMAL C1-INH (HAE-NC1-INH) - A REAL WORLD ACARE SURVEY [J].

Riedl, M. ;

Magerl, M. ;

Maurer, M. ;

Danese, S. ;

Ulloa, J. ;

Desai, V. ;

Audhya, P. .

ANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2023, 131 (05) :S34-S34

← 1 2 3 4 5 →