Investigational Liver Gene Transfer of C1-INH for the Treatment of Hereditary Angioedema

被引：0

作者：

Riling, Christopher R. ^{[1
]}

Pankowicz, Frank ^{[1
]}

Hanby, Hayley ^{[1
]}

Scriver, Michelle ^{[1
]}

Ioele, Steve ^{[1
]}

Posternak-Ball, Valeriya ^{[1
]}

Quinn, William J. ^{[1
]}

Cohen, Daniel M. ^{[1
]}

Preston, George M. ^{[1
]}

Crosariol, Marco ^{[1
]}

Armour, Sean M. ^{[1
]}

Mingozzi, Federico ^{[1
]}

机构：

[1] Spark Therapeut Inc, Liver Res & Dev, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

359

引用

页码：177 / 178

页数：2

共 50 条

[21] JOINT PAIN: A RARE SYMPTOM IN PATIENTS WITH HEREDITARY ANGIOEDEMA WITH NORMAL C1-INH [J].

Jones, D. ;

Park, N. ;

Thompson, A. .

ANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2021, 127 (05) :S82-S82

[22] Fatal laryngeal attacks and mortality in hereditary angioedema due to C1-INH deficiency [J].

Bork, Konrad ;

Hardt, Jochen ;

Witzke, Guenther .

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2012, 130 (03) :692-697

[23] REFINING PREVALENCE ESTIMATES OF HEREDITARY ANGIOEDEMA (HAE) WITH NORMAL C1-INH (HAE-NC1-INH) [J].

Magerl, M. ;

Riedl, M. ;

Maurer, M. ;

Danese, S. ;

Ulloa, J. ;

Desai, V. ;

Audhya, P. .

ANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2023, 131 (05) :S34-S34

[24] Hereditary Angioedema with Normal C1-INH with Versus without a Specific Mutation in the F12 Gene [J].

Bork, Konrad ;

Wulff, Karin ;

Witzke, Guenther ;

Hardt, Jochen .

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2015, 135 (02) :AB198-AB198

[25] TREATMENT OF HEREDITARY ANGIOEDEMA (HAE) WITH NORMAL C1-INH (HAE-NC1-INH) A REAL-WORLD ACARE SURVEY [J].

Maurer, M. ;

Magerl, M. ;

Riedl, M. ;

Danese, S. ;

Ulloa, J. ;

Desai, V. ;

Audhya, P. .

ANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2023, 131 (05) :S30-S30

[26] The influence of individualized treatment on the quality of life (QoL) in 100 patients with Hereditary Angioedema (HAE C1-INH) [J].

Saguer, Inmaculada Martinez ;

Ettingshausen, Carmen Escuriola ;

Gutowski, Zeynep ;

Linde, Richard .

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2018, 141 (02) :AB51-AB51

[27] Clinical trial of C1-INH for treatment of ACEi-induced angioedema [J].

Wilkerson, Gentry ;

Dakessian, Alik ;

Moellman, Joseph J. ;

Bernstein, Jonathan A. .

AMERICAN JOURNAL OF EMERGENCY MEDICINE, 2023, 68 :196-197

[28] Hereditary angioedema with C1 inhibitor (C1-INH) deficit: the strength of recognition (51 cases) [J].

Fragnan, N. T. M. L. ;

Tolentino, A. L. N. ;

Borba, G. B. ;

Oliveira, A. C. ;

Simoes, J. A. ;

Palma, S. M. U. ;

Constantino-Silva, R. N. ;

Grumach, A. S. .

BRAZILIAN JOURNAL OF MEDICAL AND BIOLOGICAL RESEARCH, 2018, 51 (12)

[29] In Search of an Association Between Genotype and Phenotype in Hereditary Angioedema due to C1-INH Deficiency [J].

Loli-Ausejo, David ;

Lopez-Lera, Alberto ;

Drouet, Christian ;

Lluncor, Marina ;

Phillips-Angles, Elsa ;

Pedrosa, Maria ;

Cabanas, Rosario ;

Caballero, Teresa .

CLINICAL REVIEWS IN ALLERGY & IMMUNOLOGY, 2021, 61 (01) :1-14

[30] In Search of an Association Between Genotype and Phenotype in Hereditary Angioedema due to C1-INH Deficiency [J].

David Loli-Ausejo ;

Alberto López-Lera ;

Christian Drouet ;

Marina Lluncor ;

Elsa Phillips-Anglés ;

María Pedrosa ;

Rosario Cabañas ;

Teresa Caballero .

Clinical Reviews in Allergy & Immunology, 2021, 61 :1-14

← 1 2 3 4 5 →