Investigational Liver Gene Transfer of C1-INH for the Treatment of Hereditary Angioedema

被引:0
|
作者
Riling, Christopher R. [1 ]
Pankowicz, Frank [1 ]
Hanby, Hayley [1 ]
Scriver, Michelle [1 ]
Ioele, Steve [1 ]
Posternak-Ball, Valeriya [1 ]
Quinn, William J. [1 ]
Cohen, Daniel M. [1 ]
Preston, George M. [1 ]
Crosariol, Marco [1 ]
Armour, Sean M. [1 ]
Mingozzi, Federico [1 ]
机构
[1] Spark Therapeut Inc, Liver Res & Dev, Philadelphia, PA USA
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D O I
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
359
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页码:177 / 178
页数:2
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