Investigational Liver Gene Transfer of C1-INH for the Treatment of Hereditary Angioedema

被引：0
|
作者：
Riling, Christopher R. [1 ]
Pankowicz, Frank [1 ]
Hanby, Hayley [1 ]
Scriver, Michelle [1 ]
Ioele, Steve [1 ]
Posternak-Ball, Valeriya [1 ]
Quinn, William J. [1 ]
Cohen, Daniel M. [1 ]
Preston, George M. [1 ]
Crosariol, Marco [1 ]
Armour, Sean M. [1 ]
Mingozzi, Federico [1 ]
机构：
[1] Spark Therapeut Inc, Liver Res & Dev, Philadelphia, PA USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
359
引用
收藏
页码：177 / 178
页数：2
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