Hematopoietic Stem Cell Transplantation Beyond Severe Combined Immunodeficiency: Seeking a Cure for Primary Immunodeficiency

被引：3
作者：
Mitchell, Richard [1 ,2 ]
机构：
[1] Sydney Childrens Hosp, Kids Canc Ctr, Level 1,High St, Randwick, NSW 2031, Australia
[2] Univ New South Wales, Sch Women & Childrens Hlth, Sydney, NSW, Australia
来源：
JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY-IN PRACTICE | 2019年 / 7卷 / 03期
关键词：
Primary immunodeficiency; Hematopoietic stem cell transplantation; Reduced intensity conditioning; CHRONIC GRANULOMATOUS-DISEASE; CORD BLOOD TRANSPLANTATION; WISKOTT-ALDRICH-SYNDROME; SINGLE-CENTER EXPERIENCE; HYPER-IGM SYNDROME; SEVERE CONGENITAL NEUTROPENIA; NERVOUS-SYSTEM INVOLVEMENT; DAILY INTRAVENOUS BUSULFAN; CD40 LIGAND DEFICIENCY; HEMOPHAGOCYTIC LYMPHOHISTIOCYTOSIS;
D O I：
10.1016/j.jaip.2018.12.011
中图分类号：
R392 [医学免疫学];
学科分类号：
100102 ;
摘要：
Hematopoietic stem cell transplantation (HSCT) can provide definitive therapy for patients with primary immunodeficiency disease (PIDD). Modern HSCT techniques and supportive care have significantly improved outcomes for patients with PIDD. This review examines current HSCT practice for PIDD other than severe combined immunodeficiency, and explores indications, risks, and long-term outcomes for this group of challenging diseases. Crown Copyright (C) 2018 Published by Elsevier Inc. on behalf of the American Academy of Allergy, Asthma & Immunology
引用
收藏
页码：776 / 785
页数：10
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