共 15 条
[1]
A Molecular Revolution in the Treatment of Hemophilia
[J].
Butterfield, John S. S.
;
Hege, Kerry M.
;
Herzog, Roland W.
;
Kaczmarek, Radoslaw
.
MOLECULAR THERAPY,
2020, 28 (04)
:997-1015

Butterfield, John S. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Dept Pediat, Gainesville, FL USA Univ Florida, Dept Pediat, Gainesville, FL USA

Hege, Kerry M.
论文数: 0 引用数: 0
h-index: 0
机构:
Indiana Univ Sch Med, Dept Pediat, IUPUI Wells Ctr Pediat Res, 1044 West Walnut St, Indianapolis, IN 46202 USA Univ Florida, Dept Pediat, Gainesville, FL USA

Herzog, Roland W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Florida, Dept Pediat, Gainesville, FL USA
Indiana Univ Sch Med, Dept Pediat, IUPUI Wells Ctr Pediat Res, 1044 West Walnut St, Indianapolis, IN 46202 USA Univ Florida, Dept Pediat, Gainesville, FL USA

Kaczmarek, Radoslaw
论文数: 0 引用数: 0
h-index: 0
机构:
Indiana Univ Sch Med, Dept Pediat, IUPUI Wells Ctr Pediat Res, 1044 West Walnut St, Indianapolis, IN 46202 USA
Hirszfeld Inst Immunol & Expt Therapy, Lab Glycobiol, Wroclaw, Poland Univ Florida, Dept Pediat, Gainesville, FL USA
[2]
Emicizumab for the treatment of haemophilia A: a narrative review
[J].
Franchini, Massimo
;
Marano, Giuseppe
;
Pati, Ilaria
;
Candura, Fabio
;
Profili, Samantha
;
Veropalumbo, Eva
;
Masiello, Francesca
;
Catalano, Liviana
;
Piccinini, Vanessa
;
Vaglio, Stefania
;
Pupella, Simonetta
;
Liumbruno, Giancarlo M.
.
BLOOD TRANSFUSION,
2019, 17 (03)
:223-228

Franchini, Massimo
论文数: 0 引用数: 0
h-index: 0
机构:
Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Marano, Giuseppe
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Pati, Ilaria
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Candura, Fabio
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Profili, Samantha
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Veropalumbo, Eva
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Masiello, Francesca
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Catalano, Liviana
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Piccinini, Vanessa
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Vaglio, Stefania
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Pupella, Simonetta
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy

Liumbruno, Giancarlo M.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Inst Hlth, Italian Natl Blood Ctr, Rome, Italy Carlo Poma Hosp, Dept Haematol & Transfus Med, Str Lago Paiolo 10, I-46100 Mantua, Italy
[3]
Past, present and future of hemophilia: a narrative review
[J].
Franchini, Massimo
;
Mannucci, Pier Mannuccio
.
ORPHANET JOURNAL OF RARE DISEASES,
2012, 7

Franchini, Massimo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Parma, Immunohematol & Transfus Ctr, Dept Pathol & Lab Med, Milan, Italy IRCCS Ca Granda Fdn Maggiore Policlin Hosp, Sci Direct, I-20122 Milan, Italy

Mannucci, Pier Mannuccio
论文数: 0 引用数: 0
h-index: 0
机构:
IRCCS Ca Granda Fdn Maggiore Policlin Hosp, Sci Direct, I-20122 Milan, Italy IRCCS Ca Granda Fdn Maggiore Policlin Hosp, Sci Direct, I-20122 Milan, Italy
[4]
Women with bleeding disorders
[J].
Hermans, C.
;
Kulkarni, R.
.
HAEMOPHILIA,
2018, 24
:29-36

Hermans, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Clin Univ St Luc, Haemostasis & Thrombosis Unit, Div Haematol, Brussels, Belgium Clin Univ St Luc, Haemostasis & Thrombosis Unit, Div Haematol, Brussels, Belgium

Kulkarni, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Michigan State Univ, Dept Pediat & Human Dev, E Lansing, MI 48824 USA Clin Univ St Luc, Haemostasis & Thrombosis Unit, Div Haematol, Brussels, Belgium
[5]
Novel approach to genetic analysis and results in 3000 hemophilia patients enrolled in the My Life, Our Future initiative
[J].
Johnsen, Jill M.
;
Fletcher, Shelley N.
;
Huston, Haley
;
Roberge, Sarah
;
Martin, Beth K.
;
Kircher, Martin
;
Josephson, Neil C.
;
Shendure, Jay
;
Ruuska, Sarah
;
Koerper, Marion A.
;
Morales, Jaime
;
Pierce, Glenn F.
;
Aschman, Diane J.
;
Konkle, Barbara A.
.
BLOOD ADVANCES,
2017, 1 (13)
:824-834

Johnsen, Jill M.
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA
Univ Washington, Dept Med, Seattle, WA USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Fletcher, Shelley N.
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Huston, Haley
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Roberge, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Martin, Beth K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Genome Sci, Seattle, WA 98195 USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Kircher, Martin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Genome Sci, Seattle, WA 98195 USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Josephson, Neil C.
论文数: 0 引用数: 0
h-index: 0
机构:
Seattle Genet, Bothell, WA USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Shendure, Jay
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Genome Sci, Seattle, WA 98195 USA
Howard Hughes Med Inst, Chevy Chase, MD USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Ruuska, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Koerper, Marion A.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Hemophilia Fdn, New York, NY USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Morales, Jaime
论文数: 0 引用数: 0
h-index: 0
机构:
Bioverativ, Waltham, MA USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Pierce, Glenn F.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Hemophilia Fdn, New York, NY USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Aschman, Diane J.
论文数: 0 引用数: 0
h-index: 0
机构:
Amer Thrombosis & Hemostasis Network, Chicago, IL USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA

Konkle, Barbara A.
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA
Univ Washington, Dept Med, Seattle, WA USA Bloodworks Northwest, 921 Terry Ave, Seattle, WA 98104 USA
[6]
Emicizumab Prophylaxis in Patients Who Have Hemophilia A without Inhibitors
[J].
Mahlangu, J.
;
Oldenburg, J.
;
Paz-Priel, I.
;
Negrier, C.
;
Niggli, M.
;
Mancuso, M. E.
;
Schmitt, C.
;
Jimenez-Yuste, V.
;
Kempton, C.
;
Dhalluin, C.
;
Callaghan, M. U.
;
Bujan, W.
;
Shima, M.
;
Adamkewicz, J. I.
;
Asikanius, E.
;
Levy, G. G.
;
Kruse-Jarres, R.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2018, 379 (09)
:811-822

论文数: 引用数:
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机构:

Oldenburg, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Klinikum Bonn, Bonn, Germany Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Paz-Priel, I.
论文数: 0 引用数: 0
h-index: 0
机构:
Genentech Inc, San Francisco, CA 94080 USA Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Negrier, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Louis Pradel Univ Hosp, Lyon, France Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Niggli, M.
论文数: 0 引用数: 0
h-index: 0
机构:
F Hoffmann La Roche, Basel, Switzerland Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Mancuso, M. E.
论文数: 0 引用数: 0
h-index: 0
机构:
Osped Maggiore Policlin, Fdn IRCCS Ca Granda, Angelo Bianchi Bonomi Hemophilia & Thrombosis Ctr, Milan, Italy Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Schmitt, C.
论文数: 0 引用数: 0
h-index: 0
机构:
F Hoffmann La Roche, Basel, Switzerland Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Jimenez-Yuste, V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Autonoma Madrid, Hosp Univ La Paz, Hematol Dept, Madrid, Spain Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Kempton, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Emory Sch Med, Dept Hematol & Med Oncol, Atlanta, GA USA Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Dhalluin, C.
论文数: 0 引用数: 0
h-index: 0
机构:
F Hoffmann La Roche, Basel, Switzerland Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Callaghan, M. U.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Michigan, Detroit, MI 48201 USA Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Bujan, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Costarricense Invest Cient, San Jose, Costa Rica Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Shima, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Nara Med Univ, Dept Pediat, Kashihara, Nara, Japan Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Adamkewicz, J. I.
论文数: 0 引用数: 0
h-index: 0
机构:
Genentech Inc, San Francisco, CA 94080 USA Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Asikanius, E.
论文数: 0 引用数: 0
h-index: 0
机构:
F Hoffmann La Roche, Basel, Switzerland Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Levy, G. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Genentech Inc, San Francisco, CA 94080 USA Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa

Kruse-Jarres, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, Washington Ctr Bleeding Disorders, Seattle, WA USA Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa
[7]
Association between phenotype and genotype in carriers of haemophilia A
[J].
Miesbach, W.
;
Alesci, S.
;
Geisen, C.
;
Oldenburg, J.
.
HAEMOPHILIA,
2011, 17 (02)
:246-251

Miesbach, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Goethe Univ, Inst Transfus Med, Med Clin 3, Frankfurt, Germany Goethe Univ, Inst Transfus Med, Med Clin 3, Frankfurt, Germany

Alesci, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Goethe Univ, Inst Transfus Med, Med Clin 3, Frankfurt, Germany Goethe Univ, Inst Transfus Med, Med Clin 3, Frankfurt, Germany

Geisen, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Goethe Univ, Inst Transfus Med & Immunohaematol, Frankfurt, Germany Goethe Univ, Inst Transfus Med, Med Clin 3, Frankfurt, Germany

Oldenburg, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Clin Bonn, Inst Expt Haematol & Transfus Med, Bonn, Germany Goethe Univ, Inst Transfus Med, Med Clin 3, Frankfurt, Germany
[8]
Emicizumab Prophylaxis in Hemophilia A with Inhibitors
[J].
Oldenburg, Johannes
;
Mahlangu, Johnny N.
;
Kim, Benjamin
;
Schmitt, Christophe
;
Callaghan, Michael U.
;
Young, Guy
;
Santagostino, Elena
;
Kruse-Jarres, Rebecca
;
Negrier, Claude
;
Kessler, Craig
;
Valente, Nancy
;
Asikanius, Elina
;
Levy, Gallia G.
;
Windyga, Jerzy
;
Shima, Midori
.
NEW ENGLAND JOURNAL OF MEDICINE,
2017, 377 (09)
:809-818

Oldenburg, Johannes
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Klinikum Bonn, Bonn, Germany Univ Klinikum Bonn, Bonn, Germany

Mahlangu, Johnny N.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa
Natl Hlth Lab Serv, Johannesburg, South Africa Univ Klinikum Bonn, Bonn, Germany

Kim, Benjamin
论文数: 0 引用数: 0
h-index: 0
机构:
Genentech Inc, San Francisco, CA 94080 USA Univ Klinikum Bonn, Bonn, Germany

Schmitt, Christophe
论文数: 0 引用数: 0
h-index: 0
机构:
F Hoffmann La Roche, Basel, Switzerland Univ Klinikum Bonn, Bonn, Germany

Callaghan, Michael U.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Michigan, Detroit, MI 48201 USA Univ Klinikum Bonn, Bonn, Germany

论文数: 引用数:
h-index:
机构:

Santagostino, Elena
论文数: 0 引用数: 0
h-index: 0
机构:
Osped Maggiore Policlin, Ist Ricovero & Cura Carattere Sci, Angelo Bianchi Bonomi Hemophilia & Thrombosis Ctr, Ca Granda Fdn, Milan, Italy Univ Klinikum Bonn, Bonn, Germany

Kruse-Jarres, Rebecca
论文数: 0 引用数: 0
h-index: 0
机构:
Bloodworks Northwest, Seattle, WA USA Univ Klinikum Bonn, Bonn, Germany

论文数: 引用数:
h-index:
机构:

Kessler, Craig
论文数: 0 引用数: 0
h-index: 0
机构:
Georgetown Univ, Med Ctr, Washington, DC 20007 USA Univ Klinikum Bonn, Bonn, Germany

Valente, Nancy
论文数: 0 引用数: 0
h-index: 0
机构:
Genentech Inc, San Francisco, CA 94080 USA Univ Klinikum Bonn, Bonn, Germany

Asikanius, Elina
论文数: 0 引用数: 0
h-index: 0
机构:
F Hoffmann La Roche, Basel, Switzerland Univ Klinikum Bonn, Bonn, Germany

Levy, Gallia G.
论文数: 0 引用数: 0
h-index: 0
机构:
Genentech Inc, San Francisco, CA 94080 USA Univ Klinikum Bonn, Bonn, Germany

Windyga, Jerzy
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Hematol & Transfus Med, Dept Disorders Hemostasis & Internal Med, Warsaw, Poland Univ Klinikum Bonn, Bonn, Germany

Shima, Midori
论文数: 0 引用数: 0
h-index: 0
机构:
Nara Med Univ, Dept Pediat, Kashihara, Nara, Japan Univ Klinikum Bonn, Bonn, Germany
[9]
Optimal treatment strategies for hemophilia: achievements and limitations of current prophylactic regimens
[J].
Oldenburg, Johannes
.
BLOOD,
2015, 125 (13)
:2038-2044

Oldenburg, Johannes
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Clin Bonn, Inst Expt Haematol & Transfus Med, Bonn, Germany Univ Clin Bonn, Inst Expt Haematol & Transfus Med, Bonn, Germany
[10]
IgG Placental Transfer in Healthy and Pathological Pregnancies
[J].
Palmeira, Patricia
;
Quinello, Camila
;
Silveira-Lessa, Ana Lucia
;
Zago, Claudia Augusta
;
Carneiro-Sampaio, Magda
.
CLINICAL & DEVELOPMENTAL IMMUNOLOGY,
2012,

Palmeira, Patricia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil
Hosp Clin Sao Paulo, Inst Crianca, Lab Invest Med LIM 36, BR-05403900 Sao Paulo, Brazil Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil

Quinello, Camila
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Clin Sao Paulo, Inst Crianca, Lab Invest Med LIM 36, BR-05403900 Sao Paulo, Brazil Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil

Silveira-Lessa, Ana Lucia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sao Paulo, Inst Ciencias Biomed, Dept Parasitol, BR-05508000 Sao Paulo, Brazil Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil

Zago, Claudia Augusta
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Clin Sao Paulo, Inst Crianca, Lab Invest Med LIM 36, BR-05403900 Sao Paulo, Brazil Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil

Carneiro-Sampaio, Magda
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil
Hosp Clin Sao Paulo, Inst Crianca, Lab Invest Med LIM 36, BR-05403900 Sao Paulo, Brazil Univ Sao Paulo, Fac Med, Dept Pediat, BR-05403900 Sao Paulo, Brazil