CRISPR technology for gene therapy

被引：15

作者：

High, Katherine ^{[1
]}

Gregory, Philip D. ^{[2
]}

Gersbach, Charles ^{[3
]}

机构：

[1] Childrens Hosp Philadelphia, Howard Hughes Med Inst, Philadelphia, PA 19104 USA

[2] Sangamo BioSci, Richmond, CA USA

[3] Duke Univ, Dept Biomed Engn, Durham, NC 27706 USA

来源：

NATURE MEDICINE | 2014年 / 20卷 / 05期

关键词：

HEMOPHILIA; MOUSE;

D O I：

10.1038/nm.3566

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

[No abstract available]

引用

页码：476 / 477

页数：2

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