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- [21] Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trialLANCET NEUROLOGY, 2023, 22 (10): : 900 - 911Machado, Pedro M.论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, England UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandMcDermott, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Med Ctr, Dept Biostat & Computat Biol, Rochester, NY USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandBlaettler, Thomas论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandSundgreen, Claus论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandAmato, Anthony A.论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens Hosp, Dept Neurol, 75 Francis St, Boston, MA 02115 USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandCiafaloni, Emma论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Med Ctr, Dept Neurol, Rochester, NY USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandFreimer, Miriam论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Wexner Med Ctr, Dept Neurol, Columbus, OH USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandGibson, Summer B.论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Neuromuscular Div, Sch Med, Salt Lake City, UT USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandJones, Sarah M.论文数: 0 引用数: 0 h-index: 0机构: Univ Virginia, Dept Neurol, Charlottesville, VA USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandLevine, Todd D.论文数: 0 引用数: 0 h-index: 0机构: HonorHealth, Dept Neurol, Phoenix, AZ USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandLloyd, Thomas E.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Dept Neurol, Baltimore, MD 21218 USA Johns Hopkins Univ, Dept Neurosci, Baltimore, MD USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandMozaffar, Tahseen论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Div Neuromuscular Disorders, Orange, CA 92668 USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandShaibani, Aziz, I论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Nerve & Muscle Ctr Texas, Houston, TX 77030 USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandWicklund, Matthew论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Hlth Sci Ctr San Antonio, Dept Neurol, San Antonio, TX 78229 USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandRosholm, Anders论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandCarstensen, Tim Dehli论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandBonefeld, Karen论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandJorgensen, Anders Norkaer论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandPhonekeo, Karina论文数: 0 引用数: 0 h-index: 0机构: Orphazyme, Copenhagen, Denmark UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandHeim, Andrew J.论文数: 0 引用数: 0 h-index: 0机构: Univ Kansas, Med Ctr, Dept Neurol, Kansas City, KS 66103 USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandHerbelin, Laura论文数: 0 引用数: 0 h-index: 0机构: Univ Kansas, Med Ctr, Dept Neurol, Kansas City, KS 66103 USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandBarohn, Richard J.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Neurol, Columbia, MO USA UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandHanna, Michael G.论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, England UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, EnglandDimachkie, Mazen M.论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Queen Sq Inst Neurol, Dept Neuromuscular Dis, London WC1N 3BG, England
- [22] Safety and efficacy of thalidomide in patients with POEMS syndrome: a multicentre, randomised, double-blind, placebo-controlled trialLANCET NEUROLOGY, 2016, 15 (11): : 1129 - 1137Misawa, Sonoko论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanSato, Yasunori论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ Hosp, Clin Res Ctr, Chiba, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKatayama, Kanako论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ Hosp, Clin Res Ctr, Chiba, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanNagashima, Kengo论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ Hosp, Clin Res Ctr, Chiba, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanAoyagi, Reiko论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ Hosp, Clin Res Ctr, Chiba, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanSekiguchi, Yukari论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanSobue, Gen论文数: 0 引用数: 0 h-index: 0机构: Nagoya Univ, Grad Sch Med, Dept Neurol, Nagoya, Aichi, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKoike, Haruki论文数: 0 引用数: 0 h-index: 0机构: Nagoya Univ, Grad Sch Med, Dept Neurol, Nagoya, Aichi, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanYabe, Ichiro论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Neurol, Sapporo, Hokkaido, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanSasaki, Hidenao论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Neurol, Sapporo, Hokkaido, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanWatanabe, Osamu论文数: 0 引用数: 0 h-index: 0机构: Kagoshima Univ, Grad Sch Med & Dent Sci, Dept Neurol & Geriatr, Kagoshima, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanTakashima, Hiroshi论文数: 0 引用数: 0 h-index: 0机构: Kagoshima Univ, Grad Sch Med & Dent Sci, Dept Neurol & Geriatr, Kagoshima, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanNishizawa, Masatoyo论文数: 0 引用数: 0 h-index: 0机构: Niigata Univ, Brain Res Inst, Dept Neurol, Niigata, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKawachi, Izumi论文数: 0 引用数: 0 h-index: 0机构: Niigata Univ, Brain Res Inst, Dept Neurol, Niigata, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, Japan论文数: 引用数: h-index:机构:Mitsui, Yoshiyuki论文数: 0 引用数: 0 h-index: 0机构: Kindai Univ, Dept Neurol, Fac Med, Osaka, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKikuchi, Seiji论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Med Ctr, Natl Hosp Org, Dept Neurol, Sapporo, Hokkaido, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanNakashima, Ichiro论文数: 0 引用数: 0 h-index: 0机构: Tohoku Univ, Grad Sch Med, Dept Neurol, Sendai, Miyagi, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanIkeda, Shu-ichi论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Sch Med, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKohara, Nobuo论文数: 0 引用数: 0 h-index: 0机构: Kobe City Med Ctr, Gen Hosp, Dept Neurol, Kobe, Hyogo, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKanda, Takashi论文数: 0 引用数: 0 h-index: 0机构: Yamaguchi Univ, Grad Sch Med, Dept Neurol & Clin Neurosci, Ube, Yamaguchi, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKira, Jun-ichi论文数: 0 引用数: 0 h-index: 0机构: Kyushu Univ, Grad Sch Med Sci, Dept Neurol, Neurol Inst, Fukuoka, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanHanaoka, Hideki论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ Hosp, Clin Res Ctr, Chiba, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, JapanKuwabara, Satoshi论文数: 0 引用数: 0 h-index: 0机构: Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, Japan Chiba Univ, Grad Sch Med, Dept Neurol, Chiba 2608670, Japan
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T.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Medisch Ctr, Dept Pulmonol, Rotterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsBos, Lieuwe D. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam UMC, AMC, Dept Resp Med, Amsterdam, Netherlands Amsterdam UMC, AMC, Dept Intens Care, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsBragt, Job J. M. H. van论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam UMC, AMC, Dept Resp Med, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsBraunstahl, Gert-Jan论文数: 0 引用数: 0 h-index: 0机构: Sint Franciscus Ziekenhuis, Dept Pulmonol, Rotterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsCelant, Lucas R.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsEger, Katrien A. B.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam UMC, AMC, Dept Resp Med, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsGeelhoed, J. J. Miranda论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Dept Pulmonol, Leiden, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsGlabbeek, Yurika L. E. van论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsGrotjohan, Hans P.论文数: 0 引用数: 0 h-index: 0机构: Isala Ziekenhuizen, Dept Pulmonol, Zwolle, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHagens, Laura A.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHappe, Chris M.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHazes, Boaz D.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHeunks, Leo M. A.论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC, VUMC, Dept Intens Care, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHeuvel, Michel van den论文数: 0 引用数: 0 h-index: 0机构: Radboud UMC, Dept Pulmonol, Nijmegen, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHoefsloot, Wouter论文数: 0 引用数: 0 h-index: 0机构: Radboud UMC, Dept Pulmonol, Nijmegen, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHoek, Rianne J. A.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHoekstra, Romke论文数: 0 引用数: 0 h-index: 0机构: Antonius Ziekenhuis, Dept Pulmonol, Sneek, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsHofstee, Herman M. A.论文数: 0 引用数: 0 h-index: 0机构: Haaglanden Medisch Centrum, Dept Internal Med, The Hague, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsJuffermans, Nicole P.论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC, AMC, Dept Intens Care, Amsterdam, Netherlands Onze Lieve Vrouw Hosp, Dept Intens Care, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsKemper, E. Marleen论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC, AMC, Hosp Pharm, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsKos, Renate论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam UMC, AMC, Dept Resp Med, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsKunst, Peter W. A.论文数: 0 引用数: 0 h-index: 0机构: Onze Lieve Vrouw Hosp, Dept Pulmonol, Amsterdam, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, Netherlands论文数: 引用数: h-index:机构:Lee, Ivo van der论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, Netherlands Spaarne Gasthuis, Dept Pulmonol, Haarlem, Netherlands Vrije Univ Amsterdam, Amsterdam UMC, VUMC, Dept Pulm Med,Amsterdam Cardiovasc Sci, Amsterdam, NetherlandsLee, E. 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