共 50 条
[31]
A Mortal Complication in a Case with Mucopolysaccharidosis Type I Following Hematopoietic Stem Cell Transplantation: Pulmonary Haemorrhage
[J].
Yazici, Havva
;
Canda, Ebru
;
Er, Esra
;
Malbora, Baris
;
Hismi, Burcu Ozturk
;
Onay, Huseyin
;
Aksoylar, Serap
;
Ucar, Sema Kalkan
;
Ozkinay, Ferda
;
Coker, Mahmut
.
IZMIR DR BEHCET UZ COCUK HASTANESI DERGISI,
2021, 11 (02)
:198-201

Yazici, Havva
论文数: 0 引用数: 0
h-index: 0
机构:
Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

Canda, Ebru
论文数: 0 引用数: 0
h-index: 0
机构:
Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

Er, Esra
论文数: 0 引用数: 0
h-index: 0
机构:
Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

Malbora, Baris
论文数: 0 引用数: 0
h-index: 0
机构:
Tepecik Egitim Arastirma Hastanesi, Pediatr Hematol Klin, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

Hismi, Burcu Ozturk
论文数: 0 引用数: 0
h-index: 0
机构:
Tepecik Egitim Arastirma Hastanesi, Pediat Metabolizma & Beslenme Klin, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

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Ucar, Sema Kalkan
论文数: 0 引用数: 0
h-index: 0
机构:
Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

Ozkinay, Ferda
论文数: 0 引用数: 0
h-index: 0
机构:
Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey

Coker, Mahmut
论文数: 0 引用数: 0
h-index: 0
机构:
Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey
[32]
Progression of Hip Dysplasia in Mucopolysaccharidosis Type I Hurler After Successful Hematopoietic Stem Cell Transplantation
[J].
Langereis, Eveline J.
;
den Os, Matthijs M.
;
Breen, Catherine
;
Jones, Simon A.
;
Knaven, Olga C.
;
Mercer, Jean
;
Miller, Weston P.
;
Kelly, Paula M.
;
Kennedy, Jim
;
Ketterl, Tyler G.
;
O'Meara, Anne
;
Orchard, Paul J.
;
Lund, Troy C.
;
van Rijn, Rick R.
;
Sakkers, Ralph J.
;
White, Klane K.
;
Wijburg, Frits A.
.
JOURNAL OF BONE AND JOINT SURGERY-AMERICAN VOLUME,
2016, 98 (05)
:386-395

Langereis, Eveline J.
论文数: 0 引用数: 0
h-index: 0
机构:
Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

den Os, Matthijs M.
论文数: 0 引用数: 0
h-index: 0
机构:
Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Breen, Catherine
论文数: 0 引用数: 0
h-index: 0
机构:
St Marys Hosp, NHS Fdn Trust, Cent Manchester Univ Hosp, Genet Med,Manchester Acad Hlth Sci Ctr, Manchester M13 0JH, Lancs, England Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Jones, Simon A.
论文数: 0 引用数: 0
h-index: 0
机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Knaven, Olga C.
论文数: 0 引用数: 0
h-index: 0
机构:
Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands
St Marys Hosp, NHS Fdn Trust, Cent Manchester Univ Hosp, Genet Med,Manchester Acad Hlth Sci Ctr, Manchester M13 0JH, Lancs, England Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Mercer, Jean
论文数: 0 引用数: 0
h-index: 0
机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Miller, Weston P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Kelly, Paula M.
论文数: 0 引用数: 0
h-index: 0
机构:
Our Ladys Childrens Hosp, Dept Orthopaed Surg, Dublin, Ireland Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Kennedy, Jim
论文数: 0 引用数: 0
h-index: 0
机构:
Our Ladys Childrens Hosp, Dept Orthopaed Surg, Dublin, Ireland Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Ketterl, Tyler G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

O'Meara, Anne
论文数: 0 引用数: 0
h-index: 0
机构:
Our Ladys Childrens Hosp, Natl HSCT Dept, Dublin, Ireland Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Orchard, Paul J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Lund, Troy C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

van Rijn, Rick R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Radiol, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Sakkers, Ralph J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Utrecht, Dept Orthopaed Surg, Utrecht, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

White, Klane K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle Childrens Hosp, Dept Orthoped & Sports Med, Seattle, WA 98195 USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands

Wijburg, Frits A.
论文数: 0 引用数: 0
h-index: 0
机构:
Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands
[33]
Growth patterns in children with mucopolysaccharidosis type I-Hurler after hematopoietic stem cell transplantation: Comparison with untreated patients
[J].
Cattoni, Alessandro
;
Chiaraluce, Sofia
;
Gasperini, Serena
;
Molinari, Silvia
;
Biondi, Andrea
;
Rovelli, Attilio
;
Parini, Rossella
.
MOLECULAR GENETICS AND METABOLISM REPORTS,
2021, 28

论文数: 引用数:
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Chiaraluce, Sofia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy

Gasperini, Serena
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy

Molinari, Silvia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy

论文数: 引用数:
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Rovelli, Attilio
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy

论文数: 引用数:
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[34]
Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure
[J].
de Ru, Minke H.
;
Boelens, Jaap J.
;
Das, Anibh M.
;
Jones, Simon A.
;
van der Lee, Johanna H.
;
Mahlaoui, Nizar
;
Mengel, Eugen
;
Offringa, Martin
;
O'Meara, Anne
;
Parini, Rossella
;
Rovelli, Attilio
;
Sykora, Karl-Walter
;
Valayannopoulos, Vassili
;
Vellodi, Ashok
;
Wynn, Robert F.
;
Wijburg, Frits A.
.
ORPHANET JOURNAL OF RARE DISEASES,
2011, 6

de Ru, Minke H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Boelens, Jaap J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Utrecht, Dept Pediat, Pediat Blood & Marrow Transplantat Program, Utrecht, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Das, Anibh M.
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Pediat, Clin Kidney Liver & Metab Dis, D-3000 Hannover, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Jones, Simon A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, St Marys Hosp, Cent Manchester Univ Hosp NHS Fdn Trust, Manchester Acad Hlth Sci Ctr, Manchester M13 0JH, Lancs, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

van der Lee, Johanna H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Pediat Clin Epidemiol, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Mahlaoui, Nizar
论文数: 0 引用数: 0
h-index: 0
机构:
Necker Enfants Malad Hosp, AP HP, Pediat Immunol Hematol Unit, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Mengel, Eugen
论文数: 0 引用数: 0
h-index: 0
机构:
Johannes Gutenberg Univ Mainz, Childrens Hosp, D-6500 Mainz, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Offringa, Martin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Pediat Clin Epidemiol, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

O'Meara, Anne
论文数: 0 引用数: 0
h-index: 0
机构:
Our Ladys Childrens Hosp, Dept Haematol Oncol, Dublin, Ireland Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Parini, Rossella
论文数: 0 引用数: 0
h-index: 0
机构:
San Gerardo Hosp, Dept Pediat, Rare Metab Dis Unit, Monza, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Rovelli, Attilio
论文数: 0 引用数: 0
h-index: 0
机构:
San Gerardo Hosp, Dept Pediat, Bone Marrow Transplant Unit, Monza, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Sykora, Karl-Walter
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Pediat Hematol Oncol, D-3000 Hannover, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Valayannopoulos, Vassili
论文数: 0 引用数: 0
h-index: 0
机构:
Necker Enfants Malad Hosp, Reference Ctr Inherited Metab Disorders, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Vellodi, Ashok
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, Metab Unit, London WC1N 3JH, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Wynn, Robert F.
论文数: 0 引用数: 0
h-index: 0
机构:
Royal Manchester Childrens Hosp, Dept Blood & Marrow Transplant, Manchester M27 1HA, Lancs, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Wijburg, Frits A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
[35]
Treatment of hip dysplasia in patients with mucopolysaccharidosis type I after hematopoietic stem cell transplantation: results of an international consensus procedure
[J].
Langereis, Eveline J.
;
Borgo, Andrea
;
Crushell, Ellen
;
Harmatz, Paul R.
;
van Hasselt, Peter M.
;
Jones, Simon A.
;
Kelly, Paula M.
;
Lampe, Christina
;
van der Lee, Johanna H.
;
Odent, Thierry
;
Sakkers, Ralph
;
Scarpa, Maurizio
;
Schafroth, Matthias U.
;
Struijs, Peter A.
;
Valayannopoulos, Vassili
;
White, Klane K.
;
Wijburg, Frits A.
.
ORPHANET JOURNAL OF RARE DISEASES,
2013, 8

Langereis, Eveline J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Borgo, Andrea
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Orthopaed & Traumatol, Padua, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Crushell, Ellen
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Univ Hosp, Natl Ctr Inherited Metab Disorders, Dublin, Ireland Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Harmatz, Paul R.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp & Res Ctr Oakland, Oakland, CA USA Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

van Hasselt, Peter M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Utrecht, Dept Pediat, Utrecht, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Jones, Simon A.
论文数: 0 引用数: 0
h-index: 0
机构:
St Marys Hosp, NHS Fdn Trust, Cent Manchester Univ Hosp, Manchester Acad Hlth Sci Ctr, Manchester, Lancs, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Kelly, Paula M.
论文数: 0 引用数: 0
h-index: 0
机构:
Our Ladys Childrens Hosp, Dept Orthopaed Surg, Dublin, Ireland Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Lampe, Christina
论文数: 0 引用数: 0
h-index: 0
机构:
Johannes Gutenberg Univ Mainz, Univ Med Ctr, Dept Pediat & Adolescent Med, Mainz, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

van der Lee, Johanna H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Clin Res Unit, Woman Child Ctr, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Odent, Thierry
论文数: 0 引用数: 0
h-index: 0
机构:
Paris Descartes Univ, Necker Enfants Malades Hosp, Dept Orthopaed Surg, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Sakkers, Ralph
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Utrecht, Dept Orthopaed Surg, Utrecht, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Scarpa, Maurizio
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Pediat, Padua, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Schafroth, Matthias U.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Orthopaed Surg, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Struijs, Peter A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Orthopaed Surg, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Valayannopoulos, Vassili
论文数: 0 引用数: 0
h-index: 0
机构:
IMAGINE Inst, Paris, France
Paris Descartes Univ, Reference Ctr Inherited Metab Dis, Necker Enfants Malades Hosp, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

White, Klane K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Orthoped & Sports Med, Seattle Childrens Hosp, Seattle, WA 98195 USA Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands

Wijburg, Frits A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
Univ Amsterdam, Acad Med Ctr, Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
[36]
Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure
[J].
Minke H de Ru
;
Jaap J Boelens
;
Anibh M Das
;
Simon A Jones
;
Johanna H van der Lee
;
Nizar Mahlaoui
;
Eugen Mengel
;
Martin Offringa
;
Anne O'Meara
;
Rossella Parini
;
Attilio Rovelli
;
Karl-Walter Sykora
;
Vassili Valayannopoulos
;
Ashok Vellodi
;
Robert F Wynn
;
Frits A Wijburg
.
Orphanet Journal of Rare Diseases,
6

Minke H de Ru
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Jaap J Boelens
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Anibh M Das
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Simon A Jones
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Johanna H van der Lee
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Nizar Mahlaoui
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Eugen Mengel
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Martin Offringa
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Anne O'Meara
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Rossella Parini
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Attilio Rovelli
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Karl-Walter Sykora
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Vassili Valayannopoulos
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Ashok Vellodi
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Robert F Wynn
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center

Frits A Wijburg
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center
[37]
Treatment of hip dysplasia in patients with mucopolysaccharidosis type I after hematopoietic stem cell transplantation: results of an international consensus procedure
[J].
Eveline J Langereis
;
Andrea Borgo
;
Ellen Crushell
;
Paul R Harmatz
;
Peter M van Hasselt
;
Simon A Jones
;
Paula M Kelly
;
Christina Lampe
;
Johanna H van der Lee
;
Thierry Odent
;
Ralph Sakkers
;
Maurizio Scarpa
;
Matthias U Schafroth
;
Peter A Struijs
;
Vassili Valayannopoulos
;
Klane K White
;
Frits A Wijburg
.
Orphanet Journal of Rare Diseases,
8

Eveline J Langereis
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Andrea Borgo
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Ellen Crushell
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Paul R Harmatz
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Peter M van Hasselt
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Simon A Jones
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Paula M Kelly
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Christina Lampe
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Johanna H van der Lee
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Thierry Odent
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Ralph Sakkers
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Maurizio Scarpa
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Matthias U Schafroth
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Peter A Struijs
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Vassili Valayannopoulos
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Klane K White
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center

Frits A Wijburg
论文数: 0 引用数: 0
h-index: 0
机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center
[38]
A novel preclinical model of mucopolysaccharidosis type II for developing human hematopoietic stem cell gene therapy
[J].
Yohta Shimada
;
Natsumi Ishii
;
Takashi Higuchi
;
Motohito Goto
;
Toya Ohashi
;
Hiroshi Kobayashi
.
Gene Therapy,
2023, 30
:288-296

Yohta Shimada
论文数: 0 引用数: 0
h-index: 0
机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences

Natsumi Ishii
论文数: 0 引用数: 0
h-index: 0
机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences

Takashi Higuchi
论文数: 0 引用数: 0
h-index: 0
机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences

Motohito Goto
论文数: 0 引用数: 0
h-index: 0
机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences

Toya Ohashi
论文数: 0 引用数: 0
h-index: 0
机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences

Hiroshi Kobayashi
论文数: 0 引用数: 0
h-index: 0
机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences
[39]
An empowered, clinically viable hematopoietic stem cell gene therapy for the treatment of multisystemic mucopolysaccharidosis type II
[J].
Das, Sabyasachi
;
Rruga, Fatlum
;
Montepeloso, Annita
;
Dimartino, Agnese
;
Spadini, Silvia
;
Corre, Guillaume
;
Patel, Janki
;
Cavalca, Eleonora
;
Ferro, Francesca
;
Gatti, Alessandra
;
Milazzo, Rita
;
Galy, Anne
;
Politi, Letterio S.
;
Rizzardi, Gian Paolo
;
Vallanti, Giuliana
;
Poletti, Valentina
;
Bif, Alessandra
.
MOLECULAR THERAPY,
2024, 32 (03)
:619-636

Das, Sabyasachi
论文数: 0 引用数: 0
h-index: 0
机构:
Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA
Massachusetts Gen Hosp, Ctr Genom Med, Boston, MA 02115 USA
Harvard Med Sch, Boston, MA 02115 USA Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Rruga, Fatlum
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Women & Childs Hlth, Div Hematol Oncol & Stem Cell Transplantat, I-35128 Padua, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Montepeloso, Annita
论文数: 0 引用数: 0
h-index: 0
机构:
Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA
Univ Padua, Gene Therapy Consulting, I-35128 Padua, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Dimartino, Agnese
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Women & Childs Hlth, Div Hematol Oncol & Stem Cell Transplantat, I-35128 Padua, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Spadini, Silvia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Women & Childs Hlth, Div Hematol Oncol & Stem Cell Transplantat, I-35128 Padua, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Corre, Guillaume
论文数: 0 引用数: 0
h-index: 0
机构:
Genethon, F-91000 Evry, France
AGC Biol, I-20091 Milan, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Patel, Janki
论文数: 0 引用数: 0
h-index: 0
机构:
Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Cavalca, Eleonora
论文数: 0 引用数: 0
h-index: 0
机构:
Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Ferro, Francesca
论文数: 0 引用数: 0
h-index: 0
机构:
Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Gatti, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Altheia Sci Srl, I-20122 Milan, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Milazzo, Rita
论文数: 0 引用数: 0
h-index: 0
机构:
Humanitas Univ, I-20090 Pieve Emanuele, MI, Italy
IRCCS Human Res Hosp, I-20090 Pieve Emanuele, MI, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Galy, Anne
论文数: 0 引用数: 0
h-index: 0
机构:
Genethon, F-91000 Evry, France
AGC Biol, I-20091 Milan, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

论文数: 引用数:
h-index:
机构:

Rizzardi, Gian Paolo
论文数: 0 引用数: 0
h-index: 0
机构:
Humanitas Univ, I-20090 Pieve Emanuele, MI, Italy
IRCCS Human Res Hosp, I-20090 Pieve Emanuele, MI, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Vallanti, Giuliana
论文数: 0 引用数: 0
h-index: 0
机构: Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Poletti, Valentina
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Women & Childs Hlth, Div Hematol Oncol & Stem Cell Transplantat, I-35128 Padua, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA

Bif, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Padua, Dept Women & Childs Hlth, Div Hematol Oncol & Stem Cell Transplantat, I-35128 Padua, Italy Dana Farber Boston Childrens Canc & Blood Disorder, Gene Therapy Program, Boston, MA 02115 USA
[40]
A novel preclinical model of mucopolysaccharidosis type II for developing human hematopoietic stem cell gene therapy
[J].
Shimada, Yohta
;
Ishii, Natsumi
;
Higuchi, Takashi
;
Goto, Motohito
;
Ohashi, Toya
;
Kobayashi, Hiroshi
.
GENE THERAPY,
2023, 30 (3-4)
:288-296

Shimada, Yohta
论文数: 0 引用数: 0
h-index: 0
机构:
Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan

Ishii, Natsumi
论文数: 0 引用数: 0
h-index: 0
机构:
Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan

Higuchi, Takashi
论文数: 0 引用数: 0
h-index: 0
机构:
Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan

Goto, Motohito
论文数: 0 引用数: 0
h-index: 0
机构:
Cent Inst Expt Anim CIEA, Anim Resource Technol Ctr, Kawasaki, Kanagawa 2100821, Japan Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan

Ohashi, Toya
论文数: 0 引用数: 0
h-index: 0
机构:
Jikei Univ, Dept Human Hlth Sci & Therapeut, Sch Nursing, Tokyo 1828570, Japan Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan

Kobayashi, Hiroshi
论文数: 0 引用数: 0
h-index: 0
机构:
Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan
Jikei Univ, Dept Pediat, Sch Med, Tokyo 1058461, Japan Jikei Univ, Res Ctr Med Sci, Div Gene Therapy, Sch Med, Tokyo 1058461, Japan