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- [21] Genotype of mucopolysaccharidosis type II severe form and the efficacy of enzyme replacement therapy or hematopoietic stem cell transplantation on cognitive functionMOLECULAR GENETICS AND METABOLISM, 2015, 114 (02) : S111 - S112Tanaka, Akemi论文数: 0 引用数: 0 h-index: 0机构: Osaka City Univ, Grad Sch Med, Osaka 558, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanHamazaki, Takashi论文数: 0 引用数: 0 h-index: 0机构: Osaka City Univ, Grad Sch Med, Osaka 558, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanOkuyama, Torayuki论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Child Hlth & Dev, Tokyo, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanSakai, Norio论文数: 0 引用数: 0 h-index: 0机构: Osaka Univ, Grad Sch Med, Osaka, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanKato, Koji论文数: 0 引用数: 0 h-index: 0机构: Japanese Red Cross Nagoya Daiichi Hosp, Childrens Med Ctr, Nagoya, Aichi, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanSuzuki, Yasuyuki论文数: 0 引用数: 0 h-index: 0机构: Gifu Univ, Gifu, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanYabe, Hiromasa论文数: 0 引用数: 0 h-index: 0机构: Tokai Univ, Isehara, Kanagawa, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanKosuga, Motomichi论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Child Hlth & Dev, Tokyo, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanShinpo, Michiko论文数: 0 引用数: 0 h-index: 0机构: Osaka Univ, Grad Sch Med, Osaka, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanIshige, Mika论文数: 0 引用数: 0 h-index: 0机构: Nippon Univ, Tokyo, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanKadono, Chiho论文数: 0 引用数: 0 h-index: 0机构: Osaka City Univ, Grad Sch Med, Osaka 558, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanKudo, Satoshi论文数: 0 引用数: 0 h-index: 0机构: Osaka City Univ, Grad Sch Med, Osaka 558, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanSawada, Tomo论文数: 0 引用数: 0 h-index: 0机构: Izumi City Hosp, Izumi, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanMugishima, Hideo论文数: 0 引用数: 0 h-index: 0机构: Nippon Univ, Tokyo, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanTabuchi, Ken论文数: 0 引用数: 0 h-index: 0机构: Tokyo Komagome Hosp, Tokyo, Japan Osaka City Univ, Grad Sch Med, Osaka 558, JapanKato, Shunichi论文数: 0 引用数: 0 h-index: 0机构: Tokai Univ, Isehara, Kanagawa, Japan Osaka City Univ, Grad Sch Med, Osaka 558, Japan
- [22] Musculoskeletal manifestations in mucopolysaccharidosis type I (Hurler syndrome) following hematopoietic stem cell transplantationOrphanet Journal of Rare Diseases, 11Mona Schmidt论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsSandra Breyer论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsUlrike Löbel论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsSinef Yarar论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsRalf Stücker论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsKurt Ullrich论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsIngo Müller论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of PediatricsNicole Muschol论文数: 0 引用数: 0 h-index: 0机构: University Medical Center Hamburg-Eppendorf,Department of Pediatrics
- [23] Hematopoietic Stem Cell Gene Therapy For Mucopolysaccharidosis Type IIICMOLECULAR THERAPY, 2022, 30 (04) : 300 - 301Badell-Grau, Rafael A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USARainaldi, Joseph论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USALosay, Pauline论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USADoung, Kalvin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USAPithia, Rushil论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USAPakravesh, Kasra论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USASilva, Alexander论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USAThai, Eric论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USASharma, Jay论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USAPaulchakrabarti, Mousumi论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Glycobiol Core, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USAKhare, Veenita论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USACherqui, Stephanie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA USA Univ Calif San Diego, Dept Pediat, San Diego, CA USA
- [24] Hematopoietic Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIICMOLECULAR THERAPY, 2024, 32 (04) : 420 - 420Badell-Grau, Rafael A.论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USAPakravesh, Kasra论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USAChen, Rola论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USAThai, Eric论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USASon, Frankie论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USADuong, Kalvin论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USALosay, Pauline论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USAPithia, Rushil论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USASivakumar, Anusha论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USAKhare, Veenita论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USACorl, Alexis N.论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USATran, Christine论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USAEsko, Jefferey论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USACherqui, Stephanie论文数: 0 引用数: 0 h-index: 0机构: UCSD, La Jolla, CA USA UCSD, La Jolla, CA USA
- [25] Hematopoietic Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIICMOLECULAR THERAPY, 2023, 31 (04) : 325 - 326Badell-Grau, Rafael A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USASivakumar, Anusha论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USAKhare, Veenita论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, La Jolla, CA USADuong, Kalvin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USALosay, Pauline论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USAPakravesh, Kasra论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USATran, Christine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USAPithia, Rushil论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USALengsfield, Mira论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USAThai, Kevin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USASharma, Jay论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USAChen, Rola论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USARainaldi, Joseph N.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USACherqui, Stephanie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Univ Calif San Diego, La Jolla, CA USA
- [26] Is hematopoietic stem cell transplantation a therapeutic option for mucolipidosis type II?MOLECULAR GENETICS AND METABOLISM REPORTS, 2021, 26Ammer, Luise Sophie论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Disorders ICLD, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyPohl, Sandra论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Disorders ICLD, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Osteol & Biomech, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyBreyer, Sandra Rafaela论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Disorders ICLD, Hamburg, Germany Childrens Hosp Altona, Dept Pediat Orthoped, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Orthoped, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyAries, Charlotte论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Disorders ICLD, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyDenecke, Jonas论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyPerez, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Disorders ICLD, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyPetzoldt, Martin论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Anesthesiol, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanySchrum, Johanna论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Div Pediat Stem Cell Transplantat & Immunol, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyMuller, Ingo论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Div Pediat Stem Cell Transplantat & Immunol, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, GermanyMuschol, Nicole Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Disorders ICLD, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Pediat, Hamburg, Germany
- [27] Hematopoietic stem cell gene therapy for mucopolysaccharidosis type IIICMOLECULAR GENETICS AND METABOLISM, 2023, 138 (02) : 13 - 13Badell-Grau, Rafael论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USAPakravesh, Kasra论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USASivakumar, Anusha论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USALosay, Pauline论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USADuong, Kalvin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USATran, Christine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USAPithia, Rushil论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USAKhare, Veenita论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USAThai, Kevin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USACherqui, Stephanie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA USA Univ Calif San Diego, San Diego, CA USA
- [28] Obstructive sleep apnea syndrome after hematopoietic stem cell transplantation in children with mucopolysaccharidosis type IMOLECULAR GENETICS AND METABOLISM, 2016, 117 (02) : S117 - S117Valayannopoulos, Vassili论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceBrassier, Anais论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceAmeddeo, Alessandro论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceNeven, Benedicte论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceCaillaud, Catherine论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceChabli, Allel论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceFernandez-Bolanos, Marta论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceOlmo, Jorge论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceMoreau, Johan论文数: 0 引用数: 0 h-index: 0机构: Univ Montpellier, F-34059 Montpellier, France Hop Necker Enfants Malad, Paris, FranceFauroux, Brigitte论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, France
- [29] A Mortal Complication in a Case with Mucopolysaccharidosis Type I Following Hematopoietic Stem Cell Transplantation: Pulmonary HaemorrhageIZMIR DR BEHCET UZ COCUK HASTANESI DERGISI, 2021, 11 (02): : 198 - 201Yazici, Havva论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyCanda, Ebru论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyEr, Esra论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyMalbora, Baris论文数: 0 引用数: 0 h-index: 0机构: Tepecik Egitim Arastirma Hastanesi, Pediatr Hematol Klin, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyHismi, Burcu Ozturk论文数: 0 引用数: 0 h-index: 0机构: Tepecik Egitim Arastirma Hastanesi, Pediat Metabolizma & Beslenme Klin, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyOnay, Huseyin论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Tibbi Genet Anabilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyAksoylar, Serap论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Hematol Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyUcar, Sema Kalkan论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyOzkinay, Ferda论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, TurkeyCoker, Mahmut论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey Ege Univ, Tip Fak, Pediat Metabolizma & Beslenme Bilim Dali, Izmir, Turkey
- [30] An Innovative Combinatorial Hematopoietic Stem Cell Transplantation Strategy Enhances the Therapeutic Potential of HSC-Based Strategies in Mucopolysaccharidosis Type IIMOLECULAR THERAPY, 2018, 26 (05) : 260 - 261Ferro, Francesca论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USADas, Sabyasachi论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USAPatel, Janki论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USACavalca, Eleonora论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USAYu, Hui论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USAPeviani, Marco论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USABiffi, Alessandra论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA Harvard Stem Cell Inst, Boston, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USA