Arimoclomol increases the transcription of lysosomal genes, including NPC1 and NPC2, to facilitate lysosomal function

被引：2
|
作者：
Petersen, Nikolaj H. T. [1 ]
Klein, Pontus [1 ]
Valacca, Cristina [1 ]
Bie, Anne [1 ]
Magnoni, Raffaella [1 ]
Pedersen, Marianne T. [1 ]
Lampp, Andrea C. [1 ]
Fog, Cathrine K. [1 ]
Kirkegaard, Thomas T. [1 ]
机构：
[1] Orphazyme, Copenhagen, Denmark
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2021.11.251
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
236
引用
收藏
页码：S96 / S96
页数：1
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