mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency

被引:0
|
作者
Cao, Jingsong [1 ]
An, Ding [1 ]
Galduroz, Mikel [1 ]
Zhuo, Jenny [1 ]
Liang, Shi [1 ]
Eybye, Marianne [1 ]
Frassetto, Andrea [1 ]
Kuroda, Eishi [2 ]
Funahashi, Aki [2 ]
Santana, Jordan [3 ]
Mihai, Cosmin [3 ]
Benenato, Kerry E. [4 ]
Kumarasinghe, Sathyajith [4 ]
Sabnis, Staci [5 ]
Salerno, Timothy [5 ]
Coughlan, Kimberly [1 ]
Miracco, Edward J. [6 ]
Schultz, Joshua [1 ]
Lukacs, Christine [1 ]
Guey, Lin [1 ]
Finn, Patrick [1 ]
Furukawa, Tatsuhiko [2 ]
Giangrande, Paloma H. [1 ]
Saheki, Takeyori [2 ]
Martini, Paolo G. V. [1 ]
机构
[1] Moderna Inc, Rare Dis, Cambridge, MA USA
[2] Kagoshima Univ, Kagoshima, Japan
[3] Moderna Inc, In Vitro Biol, Cambridge, MA USA
[4] Moderna Inc, Chem, Cambridge, MA USA
[5] Moderna Inc, Formulat & Delivery Technol, Cambridge, MA USA
[6] Moderna Inc, Drug Prod Proc Sci, Cambridge, MA USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
709
引用
收藏
页码:334 / 334
页数:1
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