mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency

被引：0

作者：

Cao, Jingsong ^{[1
]}

An, Ding ^{[1
]}

Galduroz, Mikel ^{[1
]}

Zhuo, Jenny ^{[1
]}

Liang, Shi ^{[1
]}

Eybye, Marianne ^{[1
]}

Frassetto, Andrea ^{[1
]}

Kuroda, Eishi ^{[2
]}

Funahashi, Aki ^{[2
]}

Santana, Jordan ^{[3
]}

Mihai, Cosmin ^{[3
]}

Benenato, Kerry E. ^{[4
]}

Kumarasinghe, Sathyajith ^{[4
]}

Sabnis, Staci ^{[5
]}

Salerno, Timothy ^{[5
]}

Coughlan, Kimberly ^{[1
]}

Miracco, Edward J. ^{[6
]}

Schultz, Joshua ^{[1
]}

Lukacs, Christine ^{[1
]}

Guey, Lin ^{[1
]}

Finn, Patrick ^{[1
]}

Furukawa, Tatsuhiko ^{[2
]}

Giangrande, Paloma H. ^{[1
]}

Saheki, Takeyori ^{[2
]}

Martini, Paolo G. V. ^{[1
]}

机构：

[1] Moderna Inc, Rare Dis, Cambridge, MA USA

[2] Kagoshima Univ, Kagoshima, Japan

[3] Moderna Inc, In Vitro Biol, Cambridge, MA USA

[4] Moderna Inc, Chem, Cambridge, MA USA

[5] Moderna Inc, Formulat & Delivery Technol, Cambridge, MA USA

[6] Moderna Inc, Drug Prod Proc Sci, Cambridge, MA USA

来源：

MOLECULAR THERAPY | 2019年 / 27卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

709

引用

页码：334 / 334

页数：1

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