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- [27] Identification of a CNS-Targeting AAV Capsid Family with NHP and Human Cross-Reactivity through Directed EvolutionMOLECULAR THERAPY, 2024, 32 (04) : 482 - 482Quan, Jin论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAHung, Ka Ying论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAKashyap, Samneet论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USARouse, Emily论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAKelemen, Margaret论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USALu, Xiaodong论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAChittoda, Misha论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USASampath, Harini Dhamodaran论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USADesmarais, Samantha论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USABourque, Shawn Kyle论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAUtturkar, Aditya论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAGianni, Davide论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USADillon, Gregory论文数: 0 引用数: 0 h-index: 0机构: Biogen, Genet & Neurodev Disorders Res Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USASim, Sueon论文数: 0 引用数: 0 h-index: 0机构: Biogen, Genet & Neurodev Disorders Res Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAYu, Nam-Kyung论文数: 0 引用数: 0 h-index: 0机构: Biogen, Genet & Neurodev Disorders Res Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USACox, Kurt论文数: 0 引用数: 0 h-index: 0机构: Biogen, Chem Biol & Prote, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USABajrami, Bekim论文数: 0 引用数: 0 h-index: 0机构: Biogen, Chem Biol & Prote, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USANhu, Anh论文数: 0 引用数: 0 h-index: 0机构: Biogen, Genet & Neurodev Disorders Res Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAClarner, Pete论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAMartino, Richard Alexander论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAMeeks, Caitlin论文数: 0 引用数: 0 h-index: 0机构: Biogen, Biol Drug Discovery, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USATran, Jimmy论文数: 0 引用数: 0 h-index: 0机构: Biogen, Nonclin Safety, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAKumar, Amit论文数: 0 引用数: 0 h-index: 0机构: Biogen, Nonclin Safety, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USASeabrook, Tania论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAHenry, Kate论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAChoi, Jinkuk论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USADeng, Shuyun论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USACabral, Joseph论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USASuh, Junghae论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USAYuan, Yuan论文数: 0 引用数: 0 h-index: 0机构: Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA Biogen, Gene Therapy Accelerator Unit, Cambridge, MA USA
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- [29] The Use of Transcription-Dependent Directed Evolution (TRADE) to Identify a Novel AAV Capsid That Transduces Motor Neurons with High EfficiencyMOLECULAR THERAPY, 2023, 31 (04) : 56 - 56Chatzi, Christina论文数: 0 引用数: 0 h-index: 0机构: Capsigen Inc, Vancouver, WA USA Capsigen Inc, Vancouver, WA USADalwadi, Dhwanil论文数: 0 引用数: 0 h-index: 0机构: Capsigen Inc, Vancouver, WA USA Capsigen Inc, Vancouver, WA USAHuang, Samuel J.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Sch Med, Dept Mol & Med Genet, Portland, OR USA Capsigen Inc, Vancouver, WA USANakai, Hiroyuki论文数: 0 引用数: 0 h-index: 0机构: Capsigen Inc, Vancouver, WA USA Oregon Hlth & Sci Univ, Sch Med, Dept Mol & Med Genet, Portland, OR USA Capsigen Inc, Vancouver, WA USA
- [30] Rationally Designed Cardiotropic AAV Capsid Demonstrates Targeted Cellular Distribution in CardiomyocytesMOLECULAR THERAPY, 2023, 31 (04) : 625 - 625Chen, Youjun论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USASethna, Ferzin论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USASvancarek, Abbie论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USAEvans, Cody L.论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USAHatfield, Joshua T.论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USAHenry, Timothy D.论文数: 0 引用数: 0 h-index: 0机构: Christ Hosp, Cincinnati, OH USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USAChung, Eugene论文数: 0 引用数: 0 h-index: 0机构: Christ Hosp, Cincinnati, OH USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USAMikhail, Sheila论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USAHajjar, Roger J.论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USATretiakova, Anna P.论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USASamulski, R. Jude论文数: 0 引用数: 0 h-index: 0机构: Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC USA Univ N Carolina, Dept Pharmacol, Chapel Hill, NC USA Asklepios BioPharmaceut Inc AskBio, Res Triangle Pk, NC USA