PROGRESS TOWARD GENERATING A CFTR NULL FERRET MODEL OF CYSTIC FIBROSIS WITH INTESTINAL-SPECIFIC EXPRESSION OF FERRET CFTR

被引:0
|
作者
Liu, X. [1 ,2 ]
Sun, X. [1 ,2 ]
Luo, M. [1 ]
Yi, Y. [1 ]
Shui, H. [1 ]
Fisher, J. T. [1 ]
Goodheart, M. [1 ]
Lukacs, G. L. [3 ]
Meyerholz, D. K. [1 ,2 ]
Engelhardt, J. F. [1 ,2 ]
机构
[1] Univ Iowa, Carver Coll Med, Iowa City, IA USA
[2] Univ Iowa, Ctr Gene Therapy, Iowa City, IA USA
[3] McGill Univ, Dept Physiol, Montreal, PQ, Canada
关键词
D O I
暂无
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
206
引用
收藏
页码:283 / 283
页数:1
相关论文
共 20 条
  • [1] PROGRESS TOWARD GENERATING A ΔF508-CFTR CYSTIC FIBROSIS FERRET MODEL
    Yan, Z.
    Lei-Butters, D.
    Sun, X.
    Yi, Y.
    Fisher, J. T.
    Engelhardt, J. F.
    PEDIATRIC PULMONOLOGY, 2009, : 284 - 284
  • [2] Novel Cystic Fibrosis Ferret Model Enables Visualization of CFTR Expression Cells and Genetic CFTR Reactivation
    Yuan, Feng
    Sun, Xingshen
    Park, Soo Yeun
    Tang, Yinghua
    Feng, Zehua
    Ebadi, Mehrnoosh
    Yi, Yaling
    Thompson, Adriane E.
    Karippaparambil, Joseph D.
    Engelhardt, John F.
    Yan, Ziying
    HUMAN GENE THERAPY, 2025,
  • [3] Disease phenotype of a ferret CFTR-knockout model of cystic fibrosis
    Sun, Xingshen
    Sui, Hongshu
    Fisher, John T.
    Yan, Ziying
    Liu, Xiaoming
    Cho, Hyung-Ju
    Joo, Nam Soo
    Zhang, Yulong
    Zhou, Weihong
    Yi, Yaling
    Kinyon, Joann M.
    Lei-Butters, Diana C.
    Griffin, Michelle A.
    Naumann, Paul
    Luo, Meihui
    Ascher, Jill
    Wang, Kai
    Frana, Timothy
    Wine, Jeffrey J.
    Meyerholz, David K.
    Engelhardt, John F.
    JOURNAL OF CLINICAL INVESTIGATION, 2010, 120 (09): : 3149 - 3160
  • [4] Progress toward generating a ferret model of cystic fibrosis by somatic cell nuclear transfer
    Ziyi Li
    John F Engelhardt
    Reproductive Biology and Endocrinology, 1 (1)
  • [5] TISSUE SPECIFIC ROLE OF CFTR IN CYSTIC FIBROSIS INTESTINAL OBSTRUCTION
    Vitko, M.
    Valerio, D.
    Drumm, M. L.
    Hodges, C.
    PEDIATRIC PULMONOLOGY, 2014, 49 : 412 - 413
  • [6] Tissue-Specific Complementation of Intestinal Disease in a Transgenic CFTR-Knockout Ferret Model Generated by SCNT
    Sun, Xingshen
    Sui, Hongshu
    Liu, Xiaoming
    Fisher, John
    Yan, Ziying
    Yi, Yaling
    Luo, Meihui
    Zhang, Yulong
    Zhou, Weihong
    Meyerholz, David K.
    Engelhardt, John F.
    BIOLOGY OF REPRODUCTION, 2010, : 137 - 138
  • [7] Intestinal CFTR expression alleviates meconium ileus in cystic fibrosis pigs
    Stoltz, David A.
    Rokhlina, Tatiana
    Ernst, Sarah E.
    Pezzulo, Alejandro A.
    Ostedgaard, Lynda S.
    Karp, Philip H.
    Samuel, Melissa S.
    Reznikov, Leah R.
    Rector, Michael V.
    Gansemer, Nicholas D.
    Bouzek, Drake C.
    Abou Alaiwa, Mahmoud H.
    Hoegger, Mark J.
    Ludwig, Paula S.
    Taft, Peter J.
    Wallen, Tanner J.
    Wohlford-Lenane, Christine
    McMenimen, James D.
    Chen, Jeng-Haur
    Bogan, Katrina L.
    Adam, Ryan J.
    Hornick, Emma E.
    Nelson, George A.
    Hoffman, Eric A.
    Chang, Eugene H.
    Zabner, Joseph
    McCray, Paul B., Jr.
    Prather, Randall S.
    Meyerholz, David K.
    Welsh, Michael J.
    JOURNAL OF CLINICAL INVESTIGATION, 2013, 123 (06): : 2685 - 2693
  • [8] DEVELOPMENT OF A PORCINE MODEL OF CYSTIC FIBROSIS WITH INDUCIBLE CFTR EXPRESSION
    Bogan, K. L.
    Rokhlina, T.
    Ernst, S. E.
    Stoltz, D. A.
    Welsh, M. J.
    PEDIATRIC PULMONOLOGY, 2012, 47 : 279 - 279
  • [9] INTESTINAL EXPRESSION OF CFTR ALLEVIATES THE MECONIUM ILEUS PHENOTYPE IN CYSTIC FIBROSIS PIGS
    Stoltz, D. A.
    Meyerholz, D. K.
    Pezzulo, A. A.
    Rokhlina, T.
    Chen, J.
    Ostedgaard, L. S.
    Karp, P. H.
    Ernst, S. E.
    Ludwig, P. S.
    Rector, M., V
    Reznikov, L.
    Taft, P. J.
    Wohlford-Lenane, C.
    Dohrn, C.
    Hornick, E. E.
    Gansemer, N. D.
    Hoegger, M.
    Samuel, M. S.
    Brogden, K. A.
    Uc, A.
    McCray, P. B.
    Zabner, J.
    Prather, R. S.
    Welsh, M. J.
    PEDIATRIC PULMONOLOGY, 2011, : 276 - 276
  • [10] INTESTINAL EXPRESSION OF CFTR ALLEVIATES THE MECONIUM ILEUS PHENOTYPE IN CYSTIC FIBROSIS PIGS
    Stoltz, D.
    Meyerholz, D. K.
    Rokhlina, T.
    Pezzulo, A. A.
    Ostedgaard, L. S.
    Ernst, S. E.
    Ludwig, P. S.
    Reznikov, L. R.
    Uc, A.
    McCray, P. B.
    Zabner, J.
    Karp, P. H.
    Welsh, M. J.
    Samuel, M.
    Prather, R.
    JOURNAL OF INVESTIGATIVE MEDICINE, 2012, 60 (04) : 743 - 743