Prevention of Neurocognitive Deficit by Ex Vivo Lentiviral Transduction of Hematopoietic Stem Cells in a Murine Model of Mucopolysaccharidosis Type II

被引：0
|
作者：
Podetz-Pedersen, Kelly M. [1 ]
Karlen, Andrea D. [1 ]
Buckvold, Megan P. [1 ]
Nan, Zenhong [2 ]
Slepushkin, Vladimir [3 ]
Roy, Andre [3 ]
Yakovief, Galina [2 ]
Gong, Zi [2 ]
Muenzer, Joseph [4 ]
Dropulic, Boro [3 ]
Low, Walter C. [2 ]
McIvor, R. Scott [1 ]
机构：
[1] Univ Minnesota, Dept Genet Cell Biol & Dev, Minneapolis, MN USA
[2] Univ Minnesota, Dept Neurosurg, Minneapolis, MN 55455 USA
[3] Lentigen Corp, Gaithersburg, MD USA
[4] Univ North Caroliz, Dept Pediat, Chapel Hill, NC USA
来源：
MOLECULAR THERAPY | 2013年 / 21卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
495
引用
收藏
页码：S191 / S191
页数：1
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