Pilot randomized, non-inferiority, cross-over trial of once-weekly vs. three times-weekly recombinant factor VIII prophylaxis in adults with severe haemophilia A

被引：3

作者：

Ragni, M. V. ^{[1
,2
]}

Yabes, J. G. ^{[3
]}

Fogarty, P. F. ^{[4
,10
]}

Josephson, N. C. ^{[5
]}

Kessler, C. M. ^{[6
]}

Neff, A. T. ^{[7
,11
]}

Raffini, L. ^{[8
]}

Brummel-Ziedins, K. ^{[9
]}

Moore, C. G. ^{[3
,12
]}

机构：

[1] Univ Pittsburgh, Dept Med, Med Ctr, Pittsburgh, PA USA

[2] Hemophilia Ctr Western Penn, Pittsburgh, PA USA

[3] Univ Pittsburgh, Ctr Res Hlth Care, Ctr Data, Pittsburgh, PA USA

[4] Univ Penn, Philadelphia, PA 19104 USA

[5] Puget Sound Blood Ctr, Seattle, WA 98104 USA

[6] Georgetown Univ, Med Ctr, Washington, DC 20007 USA

[7] Vanderbilt Univ, Med Ctr, Nashville, TN USA

[8] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[9] Univ Vermont, Dept Biochem, Colchester, VT USA

[10] Pfizer Inc, Collegeville, PA USA

[11] Cleveland Clin Fdn, 9500 Euclid Ave, Cleveland, OH 44195 USA

[12] Carolinas HealthCare Syst, Charlotte, NC USA

来源：

HAEMOPHILIA | 2017年 / 23卷 / 01期

基金：

美国国家卫生研究院;

关键词：

ADOLESCENT; DISEASE;

D O I：

10.1111/hae.13131

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：E43 / E46

页数：4

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