Combination of Low-Dose Gene Therapy and Monthly Enzyme Replacement Therapy Improves the Phenotype of a Mouse Model of Lysosomal Storage Disease

被引：0
|
作者：
Ferla, Rita [1 ,2 ]
Alliegro, Marialuisa [1 ,2 ]
Nusco, Edoardo [1 ]
Claudiani, Pamela [1 ,2 ]
Auricchio, Alberto [1 ,2 ]
机构：
[1] Telethon Inst Genet & Med, Naples, Italy
[2] Univ Naples Federico II, Dept Translat Med, Med Genet, Naples, Italy
来源：
MOLECULAR THERAPY | 2015年 / 23卷
关键词：
D O I：
10.1016/S1525-0016(16)33889-8
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
280
引用
收藏
页码：S112 / S112
页数：1
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