Increased Frequency of Permanent Integration Following Liver-Directed Gene Therapy with rDNA-AAV2/8 In Murine Phenylketonuria

被引：0

作者：

Winn, Shelley R.

Cobb, Katherine E.

Morcinek, Nick ^{[1
]}

Roy, Laura M. ^{[1
]}

Wang, Zhonya ^{[1
]}

Koeberl, Dwight D. ^{[2
]}

Grompe, Markus ^{[1
]}

Harding, Cary O.

机构：

[1] Oregon Hlth & Sci Univ, Oregon Stem Cell Ctr, Portland, OR 97201 USA

[2] Duke Univ, Med Ctr, Durham, NC USA

来源：

MOLECULAR THERAPY | 2012年 / 20卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

136

引用

页码：S55 / S55

页数：1

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