Tyrosine Kinase Inhibitor Therapy Induces Remission in a Patient With Refractory EBF1-PDGFRB-Positive Acute Lymphoblastic Leukemia

被引:171
作者
Weston, Brent W. [1 ]
Hayden, Melissa A. [2 ]
Roberts, Kathryn G. [3 ]
Bowyer, Susan [2 ]
Hsu, Johann [1 ]
Fedoriw, George [1 ]
Rao, Kathleen W. [1 ]
Mullighan, Charles G. [3 ]
机构
[1] Univ N Carolina, Chapel Hill, NC 27514 USA
[2] Univ North Carolina Hosp, McLendon Clin Labs, Chapel Hill, NC USA
[3] St Jude Childrens Res Hosp, Memphis, TN 38105 USA
关键词
GROWTH-FACTOR RECEPTOR; MYELOPROLIFERATIVE DISORDERS; IMATINIB MESYLATE; B-PROGENITOR; REARRANGEMENT; FUSION; BETA; ACTIVATION; RESPONSES; IKZF1;
D O I
10.1200/JCO.2012.47.6770
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
引用
收藏
页码:E413 / E416
页数:4
相关论文
共 17 条
[11]   Single-cell profiling identifies aberrant STAT5 activation in myeloid malignancies with specific clinical and biologic correlates [J].
Kotecha, Nikesh ;
Floress, Nikki J. ;
Irish, Jonathan M. ;
Simonds, Erin F. ;
Sakai, Debbie S. ;
Archambeault, Sophie ;
Diaz-Flores, Ernesto ;
Coram, Marc ;
Shannon, Kevin M. ;
Nolan, Garry P. ;
Loh, Mignon L. .
CANCER CELL, 2008, 14 (04) :335-343
[12]  
Loh ML, 2011, 53 AM SOC HEM M EXP
[13]   Rearrangement of CRLF2 in B-progenitor- and Down syndrome-associated acute lymphoblastic leukemia [J].
Mullighan, Charles G. ;
Collins-Underwood, J. Racquel ;
Phillips, Letha A. A. ;
Loudin, Michael G. ;
Liu, Wei ;
Zhang, Jinghui ;
Ma, Jing ;
Coustan-Smith, Elaine ;
Harvey, Richard C. ;
Willman, Cheryl L. ;
Mikhail, Fady M. ;
Meyer, Julia ;
Carroll, Andrew J. ;
Williams, Richard T. ;
Cheng, Jinjun ;
Heerema, Nyla A. ;
Basso, Giuseppe ;
Pession, Andrea ;
Pui, Ching-Hon ;
Raimondi, Susana C. ;
Hunger, Stephen P. ;
Downing, James R. ;
Carroll, William L. ;
Rabin, Karen R. .
NATURE GENETICS, 2009, 41 (11) :1243-U111
[14]   Deletion of IKZF1 and Prognosis in Acute Lymphoblastic Leukemia. [J].
Mullighan, Charles G. ;
Su, Xiaoping ;
Zhang, Jinghui ;
Radtke, Ina ;
Phillips, Letha A. A. ;
Miller, Christopher B. ;
Ma, Jing ;
Liu, Wei ;
Cheng, Cheng ;
Schulman, Brenda A. ;
Harvey, Richard C. ;
Chen, I-Ming ;
Clifford, Robert J. ;
Carroll, William L. ;
Reaman, Gregory ;
Bowman, W. Paul ;
Devidas, Meenakshi ;
Gerhard, Daniela S. ;
Yang, Wenjian ;
Relling, Mary V. ;
Shurtleff, Sheila A. ;
Campana, Dario ;
Borowitz, Michael J. ;
Pui, Ching-Hon ;
Smith, Malcolm ;
Hunger, Stephen P. ;
Willman, Cheryl L. ;
Downing, James R. .
NEW ENGLAND JOURNAL OF MEDICINE, 2009, 360 (05) :470-480
[15]   Acute lymphoblastic leukaemia [J].
Pui, Ching-Hon ;
Robison, Leslie L. ;
Look, A. Thomas .
LANCET, 2008, 371 (9617) :1030-1043
[16]   Genetic Alterations Activating Kinase and Cytokine Receptor Signaling in High-Risk Acute Lymphoblastic Leukemia [J].
Roberts, Kathryn G. ;
Morin, Ryan D. ;
Zhang, Jinghui ;
Hirst, Martin ;
Zhao, Yongjun ;
Su, Xiaoping ;
Chen, Shann-Ching ;
Payne-Turner, Debbie ;
Churchman, Michelle L. ;
Harvey, Richard C. ;
Chen, Xiang ;
Kasap, Corynn ;
Yan, Chunhua ;
Becksfort, Jared ;
Finney, Richard P. ;
Teachey, David T. ;
Maude, Shannon L. ;
Tse, Kane ;
Moore, Richard ;
Jones, Steven ;
Mungall, Karen ;
Birol, Inanc ;
Edmonson, Michael N. ;
Hu, Ying ;
Buetow, Kenneth E. ;
Chen, I-Ming ;
Carroll, William L. ;
Wei, Lei ;
Ma, Jing ;
Kleppe, Maria ;
Levine, Ross L. ;
Garcia-Manero, Guillermo ;
Larsen, Eric ;
Shah, Neil P. ;
Devidas, Meenakshi ;
Reaman, Gregory ;
Smith, Malcolm ;
Paugh, Steven W. ;
Evans, William E. ;
Grupp, Stephan A. ;
Jeha, Sima ;
Pui, Ching-Hon ;
Gerhard, Daniela S. ;
Downing, James R. ;
Willman, Cheryl L. ;
Loh, Mignon ;
Hunger, Stephen P. ;
Marra, Marco A. ;
Mullighan, Charles G. .
CANCER CELL, 2012, 22 (02) :153-166
[17]   Improved Early Event-Free Survival With Imatinib in Philadelphia Chromosome-Positive Acute Lymphoblastic Leukemia: A Children's Oncology Group Study [J].
Schultz, Kirk R. ;
Bowman, W. Paul ;
Aledo, Alexander ;
Slayton, William B. ;
Sather, Harland ;
Devidas, Meenakshi ;
Wang, Chenguang ;
Davies, Stella M. ;
Gaynon, Paul S. ;
Trigg, Michael ;
Rutledge, Robert ;
Burden, Laura ;
Jorstad, Dean ;
Carroll, Andrew ;
Heerema, Nyla A. ;
Winick, Naomi ;
Borowitz, Michael J. ;
Hunger, Stephen P. ;
Carroll, William L. ;
Camitta, Bruce .
JOURNAL OF CLINICAL ONCOLOGY, 2009, 27 (31) :5175-5181