SELECTIVE LOWERING OF MUTANT-HUNTINGTIN BY ANTISENSE OLIGONUCLEOTIDES (ASOS) IN HUMAN CORTICAL NEURONS DERIVED FROM PATIENT-SPECIFIC INDUCED PLURIPOTENT STEM CELLS (HD-IPSC)

被引：0
|
作者：
Cotter, Laurent [1 ,2 ]
Lahaye, Romane A. [3 ]
Tseng, Wei Chou [4 ]
Liu, Yuanjing [4 ]
Lemesle, Aude [1 ,2 ]
Lenoir, Sophie [3 ]
Dale, Elena [4 ]
Saudou, Frederic [3 ]
Perrier, Anselme L. [1 ,2 ]
机构：
[1] Univ Paris Saclay, Mol Imaging Res Ctr, Commissariat Energie Atom & Energies Alternat, Fontenay Aux Roses, France
[2] Univ Paris Saclay, CNRS, Lab Malad Neurodegenerat Mecanismes Therapies Ima, Commissariat Energie Atom & Energies Alternat, Fontenay Aux Roses, France
[3] Univ Grenoble Alpes, Grenoble Inst Neurosci, INSERM, CHU Grenoble Alpes,U1216, Grenoble, France
[4] Wave Life Sci, Cambridge, MA USA
来源：
JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY | 2022年 / 93卷
关键词：
D O I：
10.1136/jnnp-2022-ehdn.233
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
I07
引用
收藏
页码：A87 / A87
页数：1
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