共 58 条
[2]
A Mutation-Agnostic Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy
[J].
CRISPR JOURNAL,
2022, 5 (01)
:66-79
[7]
Immune Reconstitution After Gene Therapy Approaches in Patients With X-Linked Severe Combined Immunodeficiency Disease
[J].
FRONTIERS IN IMMUNOLOGY,
2020, 11