Gene therapy for haemophilia

被引：12
|
作者：
Pasi, KJ [1 ]
机构：
[1] Univ Leicester, Leicester Royal Infirm, Div Haematol, Leicester LE2 7LX, Leics, England
来源：
BRITISH JOURNAL OF HAEMATOLOGY | 2001年 / 115卷 / 04期
关键词：
gene therapy; haemophilia; factor VIII; factor IX;
D O I：
10.1046/j.1365-2141.2001.03225.x
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
[No abstract available]
引用
收藏
页码：744 / 757
页数：14
相关论文
共 50 条
  • [41] Current and emerging Gene Therapies for Haemophilia A and B
    Kaczmarek, Radoslaw
    Miesbach, Wolfgang
    Ozelo, Margareth C.
    Chowdary, Pratima
    HAEMOPHILIA, 2024, 30 : 12 - 20
  • [42] Prophylactic therapy in haemophilia
    Ljung, Rolf
    BLOOD REVIEWS, 2009, 23 (06) : 267 - 274
  • [43] The 1st WFH Gene Therapy Round Table: Understanding the landscape and challenges of gene therapy for haemophilia around the world
    Pierce, Glenn F.
    Coffin, Donna
    Lillicrap, David
    Ozelo, Margareth
    Pasi, John
    Rotellini, Dawn
    Safadi Marquez, Carlos
    Sannie, Thomas
    Srivastava, Alok
    van den Berg, Marijke
    Weill, Alain
    Almeida, Antonio
    Baumann, Alain
    Brooker, Mark
    Durante, Luisa
    Naccache, Mayss
    Robinson, Fiona
    HAEMOPHILIA, 2019, 25 (02) : 189 - 194
  • [44] Gene therapy for haemophilia...yes, but...with non-viral vectors?
    Liras, A.
    Olmedillas, S.
    HAEMOPHILIA, 2009, 15 (03) : 811 - 816
  • [45] A Survey to Assess the Knowledge and Perceptions about Gene Therapy in Indian Haemophilia Patients
    Kharat, Shruti
    Tawde, Shreyas
    Ross, Cecil
    John, M. Joseph
    Dabhade, Shruti
    Kshirsagar, Shrinath
    Patil, Kranti
    Saini, Gurpreet Kaur
    More, Apurva
    Kaunchale, Nazish
    Sarwan, Diksha
    Makkar, Mridul
    D'silva, Magdalene
    Masurkar, Shrushti
    Rangarajan, Savita
    Hajirnis, Kalpana
    Shetty, Shrimati
    INDIAN JOURNAL OF HEMATOLOGY AND BLOOD TRANSFUSION, 2025,
  • [46] Accreditation model of European Haemophilia Centres in the era of novel treatments and gene therapy
    Boban, Ana
    Baghaei, Fariba
    Karin, Fijnvandraat
    Klamroth, Robert
    Miesbach, Wolfgang
    Stephensen, David
    Kavanagh, Mary
    Noone, Declan
    Crato, Miguel
    Peyvandi, Flora
    HAEMOPHILIA, 2023, 29 (06) : 1442 - 1449
  • [47] Uncertainty in an era of transformative therapy for haemophilia: Addressing the unknowns
    Pierce, Glenn F.
    HAEMOPHILIA, 2021, 27 : 103 - 113
  • [48] Combination therapy for inhibitor reversal in haemophilia A using monoclonal anti-CD20 and rapamycin
    Biswas, Moanaro
    Rogers, Geoffrey L.
    Sherman, Alexandra
    Byrnes, Barry J.
    Markusic, David M.
    Jiang, Haiyan
    Herzog, Roland W.
    THROMBOSIS AND HAEMOSTASIS, 2017, 117 (01) : 33 - 43
  • [49] Using the World Federation of Haemophilia gene therapy registry for the long-term follow-up of haemophilia patients treated with gene therapy
    Konkle, Barbara A.
    Coffin, Donna
    Naccache, Mayss
    Clark, Cary
    George, Lindsey A.
    Iorio, Alfonso
    Miesbach, Wolfgang
    Noone, Declan
    Peyvandi, Flora
    Pipe, Steven
    Recht, Michael
    Skinner, Mark
    Valentino, Leonard
    Mahlangu, Johnny N.
    Pierce, Glenn F.
    HAEMOPHILIA, 2022, 28 : 34 - 36
  • [50] An exploration of why men with severe haemophilia might not want gene therapy: The exigency study
    Fletcher, Simon
    Jenner, Kathryn
    Holland, Michael
    Chaplin, Steve
    Khair, Kate
    HAEMOPHILIA, 2021, 27 (05) : 760 - 768
12345