EFFICACY, SAFETY, AND TOLERABILITY OF AFQ056 FOR THE TREATMENT OF CHOREA IN PATIENTS WITH HUNTINGTON'S DISEASE

被引:0
|
作者
Reilmann, R. [1 ,2 ]
Rouzade-Dominguez, M. [3 ]
Saft, C. [4 ]
Suessmuth, S. D. [5 ]
Priller, J. [6 ]
Rosser, A. [7 ,8 ]
Rickards, H. [9 ]
Schoels, L. [10 ]
Pezous, N. [11 ]
Gasparini, F. [12 ]
Landwehrmeyer, G. B. [5 ]
Johns, D. [13 ]
Gomez-Mancilla, B. [12 ]
机构
[1] George Huntington Inst, D-48149 Munster, Germany
[2] Univ Munster, Dept Neurol, D-48149 Munster, Germany
[3] Novartis Pharma AG, Clin Sci & Innovat, CH-4056 Basel, Switzerland
[4] Ruhr Univ Bochum, Neurol Klin, D-44791 Bochum, Germany
[5] Univ Ulm, Dept Neurol, D-89081 Ulm, Germany
[6] Charite, Dept Neuropsychiat, D-10117 Berlin, Germany
[7] Cardiff Univ, Sch Med, Neurosci & Mental Hlth Res Inst, Cardiff CF10 3AX, S Glam, Wales
[8] Cardiff Univ, Sch Biosci, Neurosci & Mental Hlth Res Inst, Cardiff CF10 3AX, S Glam, Wales
[9] Barberry, Dept Neuropsychiat, Birmingham B15 2FG, W Midlands, England
[10] Inst Clin Brain Res, Ctr Neurol & Hertie, Clin Neurogenet Unit, D-72076 Tubingen, Germany
[11] Novartis Pharma AG, IIS Translat Sci Early Dev Stat Res, CH-4002 Basel, Switzerland
[12] Novartis Pharma AG, Novartis Inst Biomed Res, CH-4056 Basel, Switzerland
[13] Novartis Inst Biomed Res Inc, Neurosci Translat Med, Cambridge, MA 02139 USA
来源
JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY | 2014年 / 85卷
关键词
D O I
10.1136/jnnp-2014-309032.295
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
N03
引用
收藏
页码:A102 / A103
页数:3
相关论文
共 50 条
  • [31] SAFETY AND TOLERABILITY OF LUMBAR PUNCTURES (LP) PROCEDURE IN PATIENTS WITH HUNTINGTON'S DISEASE
    Hassan, Yara
    Rodrigues, Filipe Brogueira
    Zeun, Paul
    Byrne, Lauren
    Fraga, Carlos Estevez
    Tortelli, Rosanna
    Scahill, Rachael
    Wild, Edward
    Tabrizi, Sarah
    JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, 2021, 92 : A24 - A24
  • [32] Safety of Deutetrabenazine for the Treatment of Tardive Dyskinesia and Chorea Associated with Huntington Disease
    Frank, Samuel
    Anderson, Karen E.
    Fernandez, Hubert H.
    Hauser, Robert A.
    Claassen, Daniel O.
    Stamler, David
    Factor, Stewart A.
    Jimenez-Shahed, Joohi
    Barkay, Hadas
    Wilhelm, Amanda
    Alexander, Jessica K.
    Chaijale, Nayla
    Barash, Steve
    Savola, Juha-Matti
    Gordon, Mark Forrest
    Chen, Maria
    NEUROLOGY AND THERAPY, 2024, 13 (03) : 655 - 675
  • [33] AFQ056, an allosteric modulator of metabotropic glutamate receptor 5, inhibits gastro-esophageal reflux in animals and GERD patients
    Ruhl, A.
    Rouzade-Dominguez, M-L.
    Fox, A.
    Des Varannes, S. Bruley
    Tack, J.
    Malfer-Theiner, P.
    Tutuian, R.
    Allescher, H-D.
    NEUROGASTROENTEROLOGY AND MOTILITY, 2010, 22 : 52 - 52
  • [34] Deutetrabenazine for Treatment of Chorea in Huntington Disease
    Geschwind, Michael D.
    JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2016, 316 (01): : 33 - 35
  • [35] The long-term safety of deutetrabenazine for chorea in Huntington's disease
    Frank, S.
    Vaughan, C.
    Stamler, D.
    Oakes, D.
    Davis, M.
    Eberly, S.
    Kayson, E.
    Whaley, J.
    Goldstein, J.
    Testa, C.
    MOVEMENT DISORDERS, 2017, 32
  • [36] Minocycline safety and tolerability in Huntington disease
    Cha, JH
    Cudkowicz, ME
    Gevorkian, S
    Young, A
    de Blieck, EA
    Kieburtz, K
    Marshall, F
    Oakes, D
    Shinaman, MA
    Shoulson, I
    Zhao, HW
    Friedlander, R
    NEUROLOGY, 2004, 63 (03) : 547 - 549
  • [37] The selective metabotropic glutamate receptor 5 antagonist mavoglurant (AFQ056) reduces the incidence of reflux episodes in dogs and patients with moderate to severe gastroesophageal reflux disease
    Rouzade-Dominguez, M. -L.
    Pezous, N.
    David, O. J.
    Tutuian, R.
    des Varannes, S. Bruley
    Tack, J.
    Malfertheiner, P.
    Allescher, H. -D.
    Ufer, M.
    Ruhl, A.
    NEUROGASTROENTEROLOGY AND MOTILITY, 2017, 29 (08):
  • [38] Managing chorea in Huntington's disease
    Vaou, Okeanis
    Frank, Samuel
    NEURODEGENERATIVE DISEASE MANAGEMENT, 2011, 1 (04) : 295 - 306
  • [39] Safety and tolerability assessment of intrastriatal neural allografts in five patients with Huntington's disease
    Bachoud-Lévi, AC
    Bourdet, C
    Brugières, P
    Nguyen, JP
    Grandmougin, T
    Haddad, B
    Jény, R
    Bartolomeo, P
    Boissé, MF
    Dalla Barba, G
    Degos, JD
    Ergis, AM
    Lefaucheur, JP
    Lisovoski, F
    Pailhous, E
    Rémy, P
    Palfi, S
    Defer, GL
    Cesaro, P
    Hantraye, P
    Peschanski, M
    EXPERIMENTAL NEUROLOGY, 2000, 161 (01) : 194 - 202
  • [40] Chorea not due to Huntington's disease
    Gordji, A
    SEMAINE DES HOPITAUX, 1997, 73 (15-16): : 460 - 464