Haploidentical transplantation with post-transplant cyclophosphamide following reduced-intensity conditioning for osteopetrosis: outcomes in three children

被引:15
作者
Bahr, T. L. [1 ]
Lund, T. [2 ]
Sando, N. M. [2 ]
Orchard, P. J. [2 ]
Miller, W. P. [2 ]
机构
[1] Univ Minnesota, Dept Pediat, Minneapolis, MN 55455 USA
[2] Univ Minnesota, Dept Pediat, Div Blood & Marrow Transplantat, Minneapolis, MN 55455 USA
关键词
STEM-CELL TRANSPLANTATION; AUTOSOMAL RECESSIVE OSTEOPETROSIS; BONE-MARROW-TRANSPLANTATION; SEVERE APLASTIC-ANEMIA; INFANTILE OSTEOPETROSIS;
D O I
10.1038/bmt.2016.180
中图分类号
Q6 [生物物理学];
学科分类号
071011 ;
摘要
引用
收藏
页码:1546 / 1548
页数:3
相关论文
共 15 条
[1]   Fludarabine and Exposure-Targeted Busulfan Compares Favorably with Busulfan/Cyclophosphamide-Based Regimens in Pediatric Hematopoietic Cell Transplantation: Maintaining Efficacy with Less Toxicity [J].
Bartelink, I. H. ;
van Reij, E. M. L. ;
Gerhardt, C. E. ;
van Maarseveen, E. M. ;
de Wildt, A. ;
Versluys, B. ;
Lindemans, C. A. ;
Bierings, M. B. ;
Boelens, Jaap Jan .
BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2014, 20 (03) :345-353
[2]   HLA-haploidentical bone marrow transplantation with posttransplant cyclophosphamide expands the donor pool for patients with sickle cell disease [J].
Bolanos-Meade, Javier ;
Fuchs, Ephraim J. ;
Luznik, Leo ;
Lanzkron, Sophie M. ;
Gamper, Christopher J. ;
Jones, Richard J. ;
Brodsky, Robert A. .
BLOOD, 2012, 120 (22) :4285-4291
[3]   Improved Early Outcomes Using a T Cell Replete Graft Compared with T Cell Depleted Haploidentical Hematopoietic Stem Cell Transplantation [J].
Ciurea, Stefan O. ;
Mulanovich, Victor ;
Saliba, Rima M. ;
Bayraktar, Ulas D. ;
Jiang, Ying ;
Bassett, Roland ;
Wang, Sa A. ;
Konopleva, Marina ;
Fernandez-Vina, Marcelo ;
Montes, Nivia ;
Bosque, Doyle ;
Chen, Julianne ;
Rondon, Gabriela ;
Alatrash, Gheath ;
Alousi, Amin ;
Bashir, Qaiser ;
Korbling, Martin ;
Qazilbash, Muzaffar ;
Parmar, Simrit ;
Shpall, Elizabeth ;
Nieto, Yago ;
Hosing, Chitra ;
Kebriaei, Partow ;
Khouri, Issa ;
Popat, Uday ;
de Lima, Marcos ;
Champlin, Richard E. .
BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2012, 18 (12) :1835-1844
[4]   Nonmyeloablative Peripheral Blood Haploidentical Stem Cell Transplantation for Refractory Severe Aplastic Anemia [J].
Clay, Jennifer ;
Kulasekararaj, Austin G. ;
Potter, Victoria ;
Grimaldi, Francesco ;
McLornan, Donal ;
Raj, Kavita ;
de Lavallade, Hugues ;
Kenyon, Michelle ;
Pagliuca, Antonio ;
Mufti, Ghulam J. ;
Marsh, Judith C. W. .
BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2014, 20 (11) :1711-1716
[5]   Stem cell transplantation in children with infantile osteopetrosis is associated with a high incidence of VOD, which could be prevented with defibrotide [J].
Corbacioglu, S. ;
Hoenig, M. ;
Lahr, G. ;
Stoehr, S. ;
Berry, G. ;
Friedrich, W. ;
Schulz, A. S. .
BONE MARROW TRANSPLANTATION, 2006, 38 (08) :547-553
[6]   Long-term outcome of haematopoietic stem cell transplantation in autosomal recessive osteopetrosis: an EBMT report [J].
Driessen, GJA ;
Gerritsen, EJA ;
Fischer, A ;
Fasth, A ;
Hop, WCJ ;
Veys, P ;
Porta, F ;
Cant, A ;
Steward, CG ;
Vossen, JM ;
Uckan, D ;
Friedrich, W .
BONE MARROW TRANSPLANTATION, 2003, 32 (07) :657-663
[7]   Haploidentical BMT and post-transplant Cy for severe aplastic anemia: a multicenter retrospective study [J].
Esteves, I. ;
Bonfim, C. ;
Pasquini, R. ;
Funke, V. ;
Pereira, N. F. ;
Rocha, V. ;
Novis, Y. ;
Arrais, C. ;
Colturato, V. ;
de Souza, M. P. ;
Torres, M. ;
Fernandes, J. F. ;
Kerbauy, F. R. ;
Ribeiro, A. A. F. ;
Santos, F. P. S. ;
Hamerschlak, N. .
BONE MARROW TRANSPLANTATION, 2015, 50 (05) :685-689
[8]  
GERRITSEN EJA, 1994, PEDIATRICS, V93, P247
[9]   Post-Transplantation Cyclophosphamide for Tolerance Induction in HLA-Haploidentical Bone Marrow Transplantation [J].
Luznik, Leo ;
O'Donnell, Paul V. ;
Fuchs, Ephraim J. .
SEMINARS IN ONCOLOGY, 2012, 39 (06) :683-693
[10]  
McCurdy SR, 2015, ADV HEMATOL, V2015