共 9 条
[1]
Efficacy and Safety of Ivacaftor in Patients Aged 6 to 11 Years with Cystic Fibrosis with a G551D Mutation
[J].
Davies, Jane C.
;
Wainwright, Claire E.
;
Canny, Gerard J.
;
Chilvers, Mark A.
;
Howenstine, Michelle S.
;
Munck, Anne
;
Mainz, Jochen G.
;
Rodriguez, Sally
;
Li, Haihong
;
Yen, Karl
;
Ordonez, Claudia L.
;
Ahrens, Richard
.
AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE,
2013, 187 (11)
:1219-1225

Davies, Jane C.
论文数: 0 引用数: 0
h-index: 0
机构:
Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England
Univ London Imperial Coll Sci Technol & Med, London SW3 6LR, England Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Wainwright, Claire E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Canny, Gerard J.
论文数: 0 引用数: 0
h-index: 0
机构:
Our Ladys Childrens Hosp, Dublin, Ireland Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Chilvers, Mark A.
论文数: 0 引用数: 0
h-index: 0
机构:
British Columbia Childrens Hosp, Vancouver, BC V6H 3V4, Canada Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Howenstine, Michelle S.
论文数: 0 引用数: 0
h-index: 0
机构:
Riley Hosp Children, Indianapolis, IN USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Munck, Anne
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Robert Debre, F-75019 Paris, France Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Mainz, Jochen G.
论文数: 0 引用数: 0
h-index: 0
机构:
Jena Univ Hosp, Dept Pediat, Cyst Fibrosis Ctr, Jena, Germany Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Rodriguez, Sally
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Li, Haihong
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Yen, Karl
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Ordonez, Claudia L.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England

Ahrens, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Iowa, Dept Pediat, Iowa City, IA 52242 USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England
[2]
Cystic fibrosis drug trial design in the era of CFTR modulators associated with substantial clinical benefit: stakeholders' consensus view
[J].
De Boeck, K.
;
Lee, T.
;
Amaral, M.
;
Drevinek, P.
;
Elborn, J. S.
;
Fajac, I
;
Kerem, E.
;
Davies, J. C.
.
JOURNAL OF CYSTIC FIBROSIS,
2020, 19 (05)
:688-695

De Boeck, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium

Lee, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Leeds Childrens Hosp, Leeds Reg Paediat Cyst Fibrosis Ctr, Great George St, Leeds LS1 3EX, W Yorkshire, England Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium

Amaral, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Lisbon, Fac Sci, BioISI Biosyst & Integrat Sci Inst, C8 Bdg, P-1749016 Lisbon, Portugal Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium

论文数: 引用数:
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Elborn, J. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Queens Univ, Ctr Expt Med, Belfast, Antrim, North Ireland Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium

论文数: 引用数:
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机构:

Kerem, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Hadassah Hebrew Univ Hosp, Dept Paediat, Jerusalem, Israel
Hadassah Hebrew Univ Hosp, CF Ctr, Jerusalem, Israel Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium

Davies, J. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll London, London, England
Royal Brompton & Harefield NHS Fdn Trust, London, England Univ Leuven, Univ Hosp Leuven, Dept Paediat, Leuven, Belgium
[3]
The US Food and Drug Administration's Experience with Ivacaftor in Cystic Fibrosis Establishing Efficacy Using In Vitro Data in Lieu of a Clinical Trial
[J].
Durmowicz, Anthony G.
;
Lim, Robert
;
Rogers, Hobart
;
Rosebraugh, Curtis J.
;
Chowdhury, Badrul A.
.
ANNALS OF THE AMERICAN THORACIC SOCIETY,
2018, 15 (01)
:1-2

Durmowicz, Anthony G.
论文数: 0 引用数: 0
h-index: 0
机构:
US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA

Lim, Robert
论文数: 0 引用数: 0
h-index: 0
机构:
US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA

Rogers, Hobart
论文数: 0 引用数: 0
h-index: 0
机构:
US FDA, Ctr Drug Evaluat & Res, Off Clin Pharmacol, Silver Spring, MD USA US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA

Rosebraugh, Curtis J.
论文数: 0 引用数: 0
h-index: 0
机构:
US FDA, Ctr Drug Evaluat & Res, Off Drug Evaluat 2, Silver Spring, MD USA US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA

Chowdhury, Badrul A.
论文数: 0 引用数: 0
h-index: 0
机构:
US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA US FDA, Ctr Drug Evaluat & Res, Div Pulm Allergy & Rheumatol Prod, Silver Spring, MD USA
[4]
Acronyms Confuse Everyone: Combating the use of acronyms to describe paediatric research studies
[J].
Isles, Alan F.
;
Pearn, John H.
.
JOURNAL OF PAEDIATRICS AND CHILD HEALTH,
2014, 50 (10)
:756-758

Isles, Alan F.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Queensland, Royal Childrens Hosp, Dept Resp Med, Brisbane, Qld, Australia
Univ Queensland, Royal Childrens Hosp, Dept Paediat, Brisbane, Qld, Australia
Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Queensland, Royal Childrens Hosp, Dept Resp Med, Brisbane, Qld, Australia

Pearn, John H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Queensland, Royal Childrens Hosp, Dept Resp Med, Brisbane, Qld, Australia
Univ Queensland, Royal Childrens Hosp, Dept Paediat, Brisbane, Qld, Australia Univ Queensland, Royal Childrens Hosp, Dept Resp Med, Brisbane, Qld, Australia
[5]
Building global development strategies for cf therapeutics during a transitional cftr modulator era
[J].
Mayer-Hamblett, N.
;
Van Koningsbruggen-Rietschel, S.
;
Nichols, D. P.
;
VanDevanter, D. R.
;
Davies, J. C.
;
Lee, T.
;
Durmowicz, A. G.
;
Ratjen, F.
;
Konstan, M. W.
;
Pearson, K.
;
Bell, S. C.
;
Clancy, J. P.
;
Taylor-Cousar, J. L.
;
De Boeck, K.
;
Donaldson, S. H.
;
Downey, D. G.
;
Flume, P. A.
;
Drevinek, P.
;
Goss, C. H.
;
Fajac, I
;
Magaret, A. S.
;
Quon, B. S.
;
Singleton, S. M.
;
VanDalfsen, J. M.
;
Retsch-Bogart, G. Z.
.
JOURNAL OF CYSTIC FIBROSIS,
2020, 19 (05)
:677-687

Mayer-Hamblett, N.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA
Seattle Childrens Hosp, POB 5371,M-S CW8-5B, Seattle, WA 98145 USA Univ Washington, Seattle, WA 98195 USA

Van Koningsbruggen-Rietschel, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cologne, Childrens Hosp, Cyst Fibrosis Ctr, Cologne, Germany
Fac Med, Cologne, Germany
Univ Hosp Cologne, Cologne, Germany Univ Washington, Seattle, WA 98195 USA

Nichols, D. P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA
Seattle Childrens Hosp, POB 5371,M-S CW8-5B, Seattle, WA 98145 USA Univ Washington, Seattle, WA 98195 USA

VanDevanter, D. R.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Cleveland, OH USA Univ Washington, Seattle, WA 98195 USA

Davies, J. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll London, Natl Heart & Lung Inst, London, England
Royal Brompton & Harefield NHS Fdn Trust, London, England Univ Washington, Seattle, WA 98195 USA

Lee, T.
论文数: 0 引用数: 0
h-index: 0
机构:
Leeds Reg Paediat Cyst Fibrosis Ctr, Leeds, W Yorkshire, England Univ Washington, Seattle, WA 98195 USA

Durmowicz, A. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Cyst Fibrosis Fdn, Bethesda, MD USA Univ Washington, Seattle, WA 98195 USA

论文数: 引用数:
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机构:

Konstan, M. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Cleveland, OH USA
Rainbow Babies & Childrens Hosp, 2101 Adelbert Rd, Cleveland, OH 44106 USA Univ Washington, Seattle, WA 98195 USA

Pearson, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Seattle Childrens Hosp, POB 5371,M-S CW8-5B, Seattle, WA 98145 USA Univ Washington, Seattle, WA 98195 USA

Bell, S. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Queensland, Childrens Hlth Res Ctr, Brisbane, Qld, Australia Univ Washington, Seattle, WA 98195 USA

Clancy, J. P.
论文数: 0 引用数: 0
h-index: 0
机构:
Cyst Fibrosis Fdn, Bethesda, MD USA Univ Washington, Seattle, WA 98195 USA

Taylor-Cousar, J. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth, Denver, CO USA Univ Washington, Seattle, WA 98195 USA

De Boeck, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Leuven, Leuven, Belgium Univ Washington, Seattle, WA 98195 USA

Donaldson, S. H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Chapel Hill, NC 27515 USA Univ Washington, Seattle, WA 98195 USA

Downey, D. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Queens Univ Belfast, Ctr Expt Med, Belfast, Antrim, North Ireland Univ Washington, Seattle, WA 98195 USA

Flume, P. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Med Univ South Carolina, Charleston, SC 29425 USA Univ Washington, Seattle, WA 98195 USA

论文数: 引用数:
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机构:

Goss, C. H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA
Seattle Childrens Hosp, POB 5371,M-S CW8-5B, Seattle, WA 98145 USA Univ Washington, Seattle, WA 98195 USA

论文数: 引用数:
h-index:
机构:

Magaret, A. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA
Seattle Childrens Hosp, POB 5371,M-S CW8-5B, Seattle, WA 98145 USA Univ Washington, Seattle, WA 98195 USA

Quon, B. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ British Columbia, Vancouver, BC, Canada Univ Washington, Seattle, WA 98195 USA

Singleton, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Cyst Fibrosis Fdn, Bethesda, MD USA Univ Washington, Seattle, WA 98195 USA

VanDalfsen, J. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Seattle Childrens Hosp, POB 5371,M-S CW8-5B, Seattle, WA 98145 USA Univ Washington, Seattle, WA 98195 USA

Retsch-Bogart, G. Z.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Chapel Hill, NC 27515 USA Univ Washington, Seattle, WA 98195 USA
[6]
Elexacaftor-Tezacaftor-Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
[J].
Middleton, P. G.
;
Mall, M. A.
;
Drevinek, P.
;
Lands, L. C.
;
McKone, E. F.
;
Polineni, D.
;
Ramsey, B. W.
;
Taylor-Cousar, J. L.
;
Tullis, E.
;
Vermeulen, F.
;
Marigowda, G.
;
Mckee, C. M.
;
Moskowitz, S. M.
;
Nair, N.
;
Savage, J.
;
Simard, C.
;
Tian, S.
;
Waltz, D.
;
Xuan, F.
;
Rowe, S. M.
;
Jain, R.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2019, 381 (19)
:1809-1819

Middleton, P. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia
Univ Sydney, Westmead Inst Med Res, Ludwig Engel Ctr Resp Res, CF Res Grp, Westmead, NSW, Australia Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Mall, M. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Charite, Berlin Inst Hlth, Dept Pediat Pulmonol Immunol & Intens Care Med, Berlin, Germany
German Ctr Lung Res, Berlin, Germany Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

论文数: 引用数:
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机构:

Lands, L. C.
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Hlth Ctr, Pediat Resp Med & Pediat Cyst Fibrosis Clin, Montreal, PQ, Canada Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

McKone, E. F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin, Ireland
Univ Coll Dublin, Sch Med, Dublin, Ireland Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Polineni, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Kansas, Med Ctr, Dept Internal Med, Kansas City, KS 66103 USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Ramsey, B. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA
Seattle Childrens Res Inst, Seattle, WA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Taylor-Cousar, J. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth, Dept Med, Denver, CO USA
Natl Jewish Hlth, Dept Pediat, Denver, CO USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Tullis, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, St Michaels Hosp, Div Respirol, Toronto, ON, Canada Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Vermeulen, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Katholieke Univ Leuven, Dept Pediat, Cyst Fibrosis Reference Ctr, Leuven, Belgium Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Marigowda, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Mckee, C. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Moskowitz, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Nair, N.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Savage, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Simard, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Tian, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Waltz, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Xuan, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Rowe, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Dept Med, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Dept Pediat, Birmingham, AL USA
Univ Alabama Birmingham, Dept Cell Dev & Integrat Biol, Birmingham, AL USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Jain, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Internal Med, 5323 Harry Hines Blvd, Dallas, TX 75390 USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia
[7]
A CFTR Potentiator in Patients with Cystic Fibrosis and the G551D Mutation
[J].
Ramsey, Bonnie W.
;
Davies, Jane
;
McElvaney, N. Gerard
;
Tullis, Elizabeth
;
Bell, Scott C.
;
Drevinek, Pavel
;
Griese, Matthias
;
McKone, Edward F.
;
Wainwright, Claire E.
;
Konstan, Michael W.
;
Moss, Richard
;
Ratjen, Felix
;
Sermet-Gaudelus, Isabelle
;
Rowe, Steven M.
;
Dong, Qunming
;
Rodriguez, Sally
;
Yen, Karl
;
Ordonez, Claudia
;
Elborn, J. Stuart
.
NEW ENGLAND JOURNAL OF MEDICINE,
2011, 365 (18)
:1663-1672

Ramsey, Bonnie W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Pediat, Seattle, WA 98105 USA
Seattle Childrens Hosp, Seattle, WA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Davies, Jane
论文数: 0 引用数: 0
h-index: 0
机构:
Royal Brompton & Harefield Natl Hlth Serv Fdn Tru, Res Biomed Res Unit, London, England Univ Washington, Dept Pediat, Seattle, WA 98105 USA

McElvaney, N. Gerard
论文数: 0 引用数: 0
h-index: 0
机构:
Beaumont Hosp, Royal Coll Surg Ireland, Beaumont, TX USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Tullis, Elizabeth
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, St Michaels Hosp, Toronto, ON M5B 1W8, Canada Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Bell, Scott C.
论文数: 0 引用数: 0
h-index: 0
机构:
Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia
Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Drevinek, Pavel
论文数: 0 引用数: 0
h-index: 0
机构:
Charles Univ Prague, Dept Pediat, Sch Med 2, Prague, Czech Republic Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Griese, Matthias
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Washington, Dept Pediat, Seattle, WA 98105 USA

McKone, Edward F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin 4, Ireland Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Wainwright, Claire E.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin 4, Ireland
Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Konstan, Michael W.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Rainbow Babies & Childrens Hosp, Cleveland, OH USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Moss, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Sch Med, Stanford, CA 94305 USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Ratjen, Felix
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Sick Children, Dept Pediat, Toronto, ON M5G 1X8, Canada Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Sermet-Gaudelus, Isabelle
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, Ctr Invest Clin, Paris, France Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Rowe, Steven M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Birmingham, AL USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Dong, Qunming
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Rodriguez, Sally
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Yen, Karl
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Ordonez, Claudia
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Elborn, J. Stuart
论文数: 0 引用数: 0
h-index: 0
机构:
Queens Univ Belfast, Ctr Infect & Immun, Belfast, Antrim, North Ireland Univ Washington, Dept Pediat, Seattle, WA 98105 USA
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Tezacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del
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Taylor-Cousar, Jennifer L.
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Munck, Anne
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McKone, Edward F.
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van der Ent, Cornelis K.
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Moeller, Alexander
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Simard, Christopher
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Wang, Linda T.
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Ingenito, Edward P.
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Mckee, Charlotte
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Lu, Yimeng
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Lekstrom-Himes, Julie
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Elborn, J. Stuart
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NEW ENGLAND JOURNAL OF MEDICINE,
2017, 377 (21)
:2013-2023

Taylor-Cousar, Jennifer L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth, Denver, CO USA Natl Jewish Hlth, Denver, CO USA

Munck, Anne
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Robert Debre, AP HP, Paris, France Natl Jewish Hlth, Denver, CO USA

McKone, Edward F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Univ Coll Dublin, Sch Med, Dublin, Ireland Natl Jewish Hlth, Denver, CO USA

van der Ent, Cornelis K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr, Utrecht, Netherlands Natl Jewish Hlth, Denver, CO USA

Moeller, Alexander
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Childrens Hosp Zurich, Zurich, Switzerland Natl Jewish Hlth, Denver, CO USA

Simard, Christopher
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Natl Jewish Hlth, Denver, CO USA

Wang, Linda T.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Natl Jewish Hlth, Denver, CO USA

Ingenito, Edward P.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Natl Jewish Hlth, Denver, CO USA

Mckee, Charlotte
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Natl Jewish Hlth, Denver, CO USA

Lu, Yimeng
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Natl Jewish Hlth, Denver, CO USA

Lekstrom-Himes, Julie
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Natl Jewish Hlth, Denver, CO USA

Elborn, J. Stuart
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll, London, England
Royal Brompton Hosp, Guy Scadding Bldg,Cale St, London SW3 6LY, England
Harefield NHS Fdn Trust, London, England
Queens Univ, Belfast, Antrim, North Ireland Natl Jewish Hlth, Denver, CO USA
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Huang, X.
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Cipolli, M.
;
Colombo, C.
;
Davies, J. C.
;
De Boeck, K.
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Flume, P. A.
;
Konstan, M. W.
;
McColley, S. A.
;
Mccoy, K.
;
McKone, E. F.
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Munck, A.
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Ratjen, F.
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Rowe, S. M.
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Waltz, D.
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Boyle, M. P.
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NEW ENGLAND JOURNAL OF MEDICINE,
2015, 373 (03)
:220-231

Wainwright, C. E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Queensland, Sch Med, Brisbane, Qld, Australia Univ Queensland, Sch Med, Brisbane, Qld, Australia

Elborn, J. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Queens Univ Belfast, Belfast, Antrim, North Ireland Univ Queensland, Sch Med, Brisbane, Qld, Australia

Ramsey, B. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Seattle Childrens Hosp, Seattle, WA USA
Univ Washington, Sch Med, Seattle, WA USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Marigowda, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Huang, X.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Cipolli, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Azienda Osped Univ Integrata, Cyst Fibrosis Ctr, Verona, Italy Univ Queensland, Sch Med, Brisbane, Qld, Australia

论文数: 引用数:
h-index:
机构:

Davies, J. C.
论文数: 0 引用数: 0
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机构:
Royal Brompton & Harefield NHS Fdn Trust, London, England
Univ London Imperial Coll Sci Technol & Med, London, England Univ Queensland, Sch Med, Brisbane, Qld, Australia

De Boeck, K.
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h-index: 0
机构:
Univ Hosp Gasthuisberg, Leuven, Belgium Univ Queensland, Sch Med, Brisbane, Qld, Australia

Flume, P. A.
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h-index: 0
机构:
Med Univ S Carolina, Charleston, SC USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Konstan, M. W.
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h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Rainbow Babies & Childrens Hosp, Cleveland, OH 44106 USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

McColley, S. A.
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h-index: 0
机构:
Northwestern Univ, Stanley Manne Childrens Res Inst, Feinberg Sch Med, Chicago, IL 60611 USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Mccoy, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Dept Pediat, Div Pulm, Columbus, OH USA
Ohio State Univ, Columbus, OH 43210 USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

McKone, E. F.
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h-index: 0
机构:
St Vincents Univ Hosp, Dublin 4, Ireland
Univ Coll Dublin, Sch Med, Dublin 2, Ireland Univ Queensland, Sch Med, Brisbane, Qld, Australia

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Ratjen, F.
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机构:
Univ Toronto, Hosp Sick Children, Div Resp Med, Dept Pediat Physiol & Expt Med, Toronto, ON M5G 1X8, Canada Univ Queensland, Sch Med, Brisbane, Qld, Australia

Rowe, S. M.
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机构:
Univ Alabama Birmingham, Birmingham, AL USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Waltz, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Queensland, Sch Med, Brisbane, Qld, Australia

Boyle, M. P.
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h-index: 0
机构:
Johns Hopkins Med, Baltimore, MD USA Univ Queensland, Sch Med, Brisbane, Qld, Australia