Long-Term Treatment Outcome in IPEX Syndrome Patients: An International Multicenter Retrospective Study

被引：0
|
作者：
Barzaghi, Federica [1 ]
Hernandez, Laura Amaya [2 ]
Pai, Sung-Yun [3 ]
Neven, Benedicte [4 ]
Locatelli, Franco [5 ]
Goldman, Frederick [6 ]
Seidel, Markus [7 ]
Ehl, Stephan [8 ]
Albert, Michael H. [9 ]
Dvorak, Christopher C. [10 ]
Carneiro-Sampaio, Magda [11 ]
Gennery, Andrew [12 ]
Cowan, Morton J. [10 ]
Roncarolo, Maria Grazia [2 ]
Bacchetta, Rosa [2 ]
机构：
[1] Ist Sci San Raffaele, Milan, Italy
[2] Stanford Univ, Sch Med, Pediat, Stanford, CA 94305 USA
[3] Boston Childrens Hosp, Hematol Oncol, Boston, MA USA
[4] Hop Necker Enfants Malad, Paris, France
[5] Univ Pavia, Dept Pediat Hematol Oncol, Pavia, Italy
[6] Univ Alabama Birmingham, Dept Pediat, Birmingham, AL USA
[7] Med Univ Graz, Graz, Austria
[8] Univ Freiburg, Freiburg, Germany
[9] Dr von Hauner Univ Childrens Hosp, Pediat Hematol Oncol Immunol Stem Cell Transplant, Munich, Germany
[10] UCSF Benioff Childrens Hosp, Pediat Allergy Immunol & Blood & Marrow Transplan, San Francisco, CA USA
[11] Univ Sao Paulo, Inst Crianca, Hosp Clin, Fac Med, Sao Paulo, Brazil
[12] Newcastle Univ, Paediat Immunol, Newcastle Upon Tyne, Tyne & Wear, England
来源：
BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION | 2018年 / 24卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
84
引用
收藏
页码：S81 / S82
页数：2
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