Broadening the Indications for Hematopoietic Stem Cell Genetic Therapies

被引：11

作者：

Williams, David A. ^{[1
,2
]}

机构：

[1] Childrens Hosp, Div Hematol Oncol, Boston, MA 02115 USA

[2] Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA 02115 USA

来源：

CELL STEM CELL | 2013年 / 13卷 / 03期

关键词：

MOUSE;

D O I：

10.1016/j.stem.2013.08.006

中图分类号：

Q813 [细胞工程];

学科分类号：

摘要：

The use of recombinant retroviral vectors to effect corrective genetic therapies in hematopoietic stem cells (HSCs) has long been predicted to revolutionize medicine. Two recent papers in Science now show that this technology could be considered as effective as, and perhaps superior to, allogeneic HSC transplants in some rare diseases.

引用

页码：263 / 264

页数：2

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