Advances in the treatment of mucopolysaccharidosis type I

被引:44
作者
Muenzer, J [1 ]
Fisher, A [1 ]
机构
[1] Univ N Carolina, Dept Pediat, Chapel Hill, NC 27514 USA
关键词
D O I
10.1056/NEJMp048084
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
[No abstract available]
引用
收藏
页码:1932 / 1934
页数:3
相关论文
共 3 条
[1]   HURLER AND HUNTER SYNDROMES - MUTUAL CORRECTION OF DEFECT IN CULTURED FIBROBLASTS [J].
FRATANTONI, JC ;
HALL, CW ;
NEUFELD, EF .
SCIENCE, 1968, 162 (3853) :570-+
[2]   Mannose 6-phosphate receptors: New twists in the tale [J].
Ghosh, P ;
Dahms, NM ;
Kornfeld, S .
NATURE REVIEWS MOLECULAR CELL BIOLOGY, 2003, 4 (03) :202-212
[3]  
Neufeld EF, 2001, METABOLIC MOL BASES, P3421, DOI DOI 10.1036/OMMBID.165