In vivo T-depleted reduced-intensity transplantation for GATA2-related immune dysfunction

被引:28
作者
Tholouli, Eleni [1 ]
Sturgess, Katherine [2 ]
Dickinson, Rachel E. [2 ]
Gennery, Andrew [2 ,3 ]
Cant, Andrew J. [2 ,3 ]
Jackson, Graham [3 ,4 ]
Lordan, Jim [3 ]
Hambleton, Sophie [2 ,3 ]
Slatter, Mary A. [3 ]
Bigley, Venetia [2 ,3 ]
Collin, Matthew [2 ,3 ]
机构
[1] Manchester Royal Infirm, Manchester, Lancs, England
[2] Newcastle Univ, Inst Cellular Med, Newcastle Upon Tyne, Tyne & Wear, England
[3] Newcastle Upon Tyne Hosp NHS Fdn Trust, Newcastle Upon Tyne, Tyne & Wear, England
[4] Newcastle Univ, Northern Inst Canc Res, Newcastle Upon Tyne, Tyne & Wear, England
基金
英国惠康基金;
关键词
STEM-CELL TRANSPLANTATION; ACUTE MYELOID-LEUKEMIA; GATA2; DEFICIENCY; MONOMAC SYNDROME; MUTATIONS; DISEASE;
D O I
10.1182/blood-2017-10-811489
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:1383 / 1387
页数:7
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