PRACTICAL AND PSYCHOLOGICAL DIFFICULTIES EXPERIENCED BY PATIENTS WITH HEREDITARY TRANSTHYRETIN AMYLOIDOSIS (HATTR) IN ITALY: PRELIMINARY RESULTS FROM THE TELETHON GUP 15010 STUDY

被引：0

作者：

Magliano, L. ^{[1
]}

Citarelli, G. ^{[1
]}

Obici, L. ^{[2
]}

Sforzini, C. ^{[2
]}

Di Buduo, E. ^{[2
]}

Sabatelli, M. ^{[3
]}

Luigetti, M. ^{[3
]}

Bisogni, G. ^{[3
]}

Grandis, M. ^{[4
]}

Gemelli, C. ^{[4
]}

Fabrizi, G. ^{[5
]}

Cavallaro, T. ^{[5
]}

Pareyson, D. ^{[6
]}

Fenu, S. ^{[6
]}

Santoro, L. ^{[7
]}

Manganelli, F. ^{[7
]}

Mauro, A. ^{[8
]}

Pradotto, L. ^{[9
]}

Antonini, G. ^{[10
]}

Leonardi, L. ^{[10
]}

Vanoli, F. ^{[10
]}

Russo, M. ^{[11
]}

Stancanelli, C. ^{[11
]}

Mazzeo, A. ^{[12
]}

Vita, G. ^{[12
]}

机构：

[1] Univ Campania, Dept Psychol, Caserta, Italy

[2] IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy

[3] Policlin A Gemelli Fdn, Dept Geriatr Neurosci & Orthoped, Rome, Italy

[4] Univ Genoa, Dept Neurosci Rehabil Ophthalmol Genet & Maternal, Genoa, Italy

[5] Univ Verona, Dept Neurosci Biomed & Movement Sci, Verona, Italy

[6] Fdn IRCCS Ist Neurol Carlo Besta, Milan, Italy

[7] Univ Federico II, Dept Neurosci Reprod & Odontostomatol Sci, Naples, Italy

[8] Univ Torino, Dipartimento Neurosci Rita Levi Montalcini, Turin, Italy

[9] IRCCS, Ist Auxol Italiano, Div Neurol & Neuroriabilitaz, Osped S Giuseppe, Oggebbio, VB, Italy

[10] Sapienza Univ Roma, Osped St Andrea, Dip NESMOS, Rome, Italy

[11] Nemo Sud Clin Ctr, Messina, Italy

[12] Univ Messina, Unit Neurol & Neuromuscular Dis, Dept Clin & Expt Med, Messina, Italy

来源：

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2019年 / 24卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：S30 / S30

页数：1

共 50 条

[41] PRIMARY RESULTS FROM APOLLO-B, A PHASE 3 STUDY OF PATISIRAN IN PATIENTS WITH TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH CARDIOMYOPATHY
Longhi, Simone
Maurer, Mathew S.
Fontana, Marianna
Berk, John L.
Gustafsson, Finn
Simoes, Marcos
Grogan, Martha
Fernandes, Fabio
Gottlieb, Robert L.
Kubanek, Milos
Poulsen, Steen
Damy, Thibaud
Diemberger, Igor
Tahara, Nobuhiro
Yu, Wen-chuhg
Tang, W. H. Wilson
Obici, Laura
Gonzalez-duarte, Alejandra
Sekijima, Yoshiki
White, Matthew T.
Yureneva, Elena
Jay, Patrick Y.
Vest, John
Gillmore, Julian D.
EUROPEAN HEART JOURNAL SUPPLEMENTS, 2022, 24
[42] Primary Results From Apollo-B, A Phase 3 Study Of Patisiran In Patients With Transthyretin-Mediated Amyloidosis With Cardiomyopathy
Maurer, Mathew S.
Fontana, Marianna
Berk, John
Gustafsson, Finn
Simoes, Marcus
Grogan, Martha
Fernandes, Fabio
Gottlieb, Robert L.
Kubanek, Milos
Poulsen, Steen
Damy, Thibaud
Diemberger, Igor
Tahara, Nobuhiro
Yu, Wen-Chung
Tang, W. H. Wilson
Obici, Laura
Gonzalez-Duarte, Alejandra
Sekijima, Yoshiki
White, Matthew T.
Arum, Seth
Jay, Patrick Y.
Vest, John
Gillmore, Julian D.
JOURNAL OF CARDIAC FAILURE, 2023, 29 (04) : 550 - 550
[43] PRIMARY RESULTS FROM APOLLO-B OPEN-LABEL EXTENSION STUDY OF PATISIRAN IN PATIENTS WITH TRANSTHYRETIN CARDIAC AMYLOIDOSIS
Longhi, S.
Mauer, M.
Berk, J.
Hanna, M.
Gillmore, J.
Vellosa-schwartzmann, P.
Lairez, O.
Hatano, M.
Cho, H.
van der Meer, P.
White, M.
Yureneva, E.
Sweetser, M.
Jay, P.
Vest, J.
Fontana, M.
EUROPEAN HEART JOURNAL SUPPLEMENTS, 2024, 26 : ii2 - ii2
[44] Impact of Patisiran on Norfolk Quality of Life Questionnaire Diabetic Neuropathy (QOL-DN) in patients with Hereditary transthyretin-mediated Amyloidosis: results from the Phase-3 APOLLO study
Obici, L.
Coelho, T.
Adams, D.
Gonzalez-Duarte, A.
O'riordan, W.
Yang, C. -C.
Yamashita, T.
Kristen, A.
Tournev, I.
Schmidt, H.
Berk, J.
Lin, K. -P.
Gandhi, P.
Sweetser, M.
Chen, J.
Goyal, S.
Gollob, J.
Suhr, O.
EUROPEAN JOURNAL OF NEUROLOGY, 2018, 25 : 459 - 459
[45] Long-Term efficacy and safety of inotersen for hereditary transthyretin amyloidosis: 2-year results from the NEURO-TTR open-label extension study
Brannagan, T.
Waddington Cruz, M.
Wang, A. K.
Polydefkis, M. J.
Dyck, P. J.
Khella, S.
Plante-Bordeneuve, V.
Berk, J. L.
Barroso, F.
Merlini, G.
Conceicao, I.
Hughes, S. G.
Kwoh, J.
Jung, S. W.
Guthrie, S.
Pollock, M.
Benson, M. D.
Gertz, M.
Coelho, T.
EUROPEAN JOURNAL OF NEUROLOGY, 2019, 26 : 92 - 92
[46] APOLLO-B, a Study of Patisiran in Patients With Transthyretin Cardiac Amyloidosis: Primary LongTerm Results From the Open-Label Extension Period
Hung, Rebecca R.
Correia, Edileide D.
Berk, John L.
Drachman, Brian
Fontana, Marianna
Gillmore, Julian D.
Mesquita, Claudio T.
Simoes, Marcus V.
Yureneva, Elena
White, Matthew T.
Sweetser, Marianne T.
Jay, Patrick Y.
Vest, John
Maurer, Mathew S.
CIRCULATION, 2023, 148
[47] Distress in patients with proven and suspected amyloidosis - preliminary results from a prospective cross-sectional analysis of 35 patients of the ongoing Wuerzburg Amyloidosis Cohort Study (AmyKoS)
Ihne, S. M.
Schuett, M.
Morbach, C.
Hefner, J.
Geier, A.
Sommer, C.
Zeller, D.
Csef, H.
Frantz, S.
Einsele, H.
Knop, S.
Stoerk, S.
ONCOLOGY RESEARCH AND TREATMENT, 2018, 41 : 262 - 262
[48] RESULTS FROM APOLLO PHASE III STUDY OF PATISIRAN, THE FIRST APPROVED RNAI THERAPEUTIC, IN HEREDITARY ATTR AMYLOIDOSIS PATIENTS WITH POLYNEUROPATHY.
Zhang, X.
Sweetser, M. T.
Robbie, G. J.
CLINICAL PHARMACOLOGY & THERAPEUTICS, 2019, 105 : S31 - S31
[49] The Economic Impact of the Introduction of Infliximab-Biosimilar: Preliminary Results from a Study on Rheumatologic Patients in Tuscany, Italy
Lorenzoni, Valentina
Trieste, Leopoldo
Mosca, Marta
Convertino, Irma
Tuccori, Marco
Lucenteforte, Ersilia
Ferraro, Sara
Leonardi, Luca
Roberto, Giuseppe
Luciano, Nicoletta
Blandizzi, Corrado
Gini, Rosa
Turchetti, Giuseppe
PHARMACOEPIDEMIOLOGY AND DRUG SAFETY, 2019, 28 : 9 - 9
[50] LONG-TERM USE OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC, IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS: 12 MONTH EFFICACY AND SAFETY FROM GLOBAL OPEN LABEL EXTENSION STUDY
Gonzalez-Duarte, Alejandra
Coelho, Teresa
Adams, David
Yang, Chih-Chao
Polydefkis, Michael
Kristen, Arnt
Tournev, Ivaylo
Schmidt, Hartmut
Berk, John
Lin, Kon-Ping
Gandhi, Pritesh
Sweetser, Marianne
White, Matthew
Gollob, Jared
Suhr, Ole
MUSCLE & NERVE, 2018, 58 : S51 - S51

← 1 2 3 4 5 →