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- [21] HELIOS-A: 9-month Results from the Phase 3 Study of Vutrisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with PolyneuropathyNEUROLOGY, 2021, 96 (15)Adams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, France Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceTournev, Ivailo L.论文数: 0 引用数: 0 h-index: 0机构: Med Univ Sofia, Univ Hosp Aleksandrovska, Dept Neurol, Clin Nervous Dis, Sofia, Bulgaria New Bulgarian Univ, Dept Cognit Sci, Sofia, Bulgaria Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceTaylor, Mark S.论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Westmead Hosp, Dept Clin Immunol & Allergy, Sydney, NSW, Australia Univ Sydney, Westmead Clin Sch, Sydney, NSW, Australia Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Hosp Santo Antonio, Ctr Hosp Porto, Porto, Portugal Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FrancePlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Assistance Publ Hop Paris, Neurol Amyloid network, Creteil, France Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Med Ctr, Boston, MA USA Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Medicas Nutr Salvador Zubiran, Madrid, Spain Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Univ Malaya, Dept Med, Div Neurol, Kuala Lumpur, Malaysia Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Dept Med Neurol Rheumatol, Sch Med, Matsumoto, Nagano, Japan Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceObici, Laura论文数: 0 引用数: 0 h-index: 0机构: IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceBlakesley, Rick论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceShilling, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FranceVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharm, Cambridge, England Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, FrancePolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21218 USA Univ Paris Saclay, CHU Bicetre, APHP, Dept Neurol,INSERM U1195, Paris, France
- [22] INOTERSEN IMPROVES NORFOLK QUALITY OF LIFE-DIABETIC NEUROPATHY (NORFOLK QOLDN) MEASURES IN PATIENTS WITH HEREDITARY TRANSTHYRETIN (HATTR) AMYLOIDOSIS IN THE PHASE 3 STUDY NEURO-TTRMUSCLE & NERVE, 2018, 58 : S54 - S54Polydefkis, Michael论文数: 0 引用数: 0 h-index: 0Cruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0Dyck, Peter论文数: 0 引用数: 0 h-index: 0Scheinberg, Morton论文数: 0 引用数: 0 h-index: 0Berk, John论文数: 0 引用数: 0 h-index: 0Barroso, Fabio论文数: 0 引用数: 0 h-index: 0Brannagan, Thomas论文数: 0 引用数: 0 h-index: 0Drachman, Brian论文数: 0 引用数: 0 h-index: 0Heitner, Stephen论文数: 0 引用数: 0 h-index: 0Gorevic, Peter论文数: 0 引用数: 0 h-index: 0Monia, Brett论文数: 0 引用数: 0 h-index: 0Gertz, Morie论文数: 0 引用数: 0 h-index: 0Benson, Merrill论文数: 0 引用数: 0 h-index: 0Wang, Annabel论文数: 0 引用数: 0 h-index: 0
- [23] Diagnosis of hereditary transthyretin amyloidosis in patients with suspected chronic inflammatory demyelinating polyneuropathy unresponsive to intravenous immunoglobulins: results of a retrospective studyORPHANET JOURNAL OF RARE DISEASES, 2025, 20 (01)Pereon, Yann论文数: 0 引用数: 0 h-index: 0机构: CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, CHU Bicetre, Ctr Reference Neuropathies Rares CERAMIC, Dept Neurol, Paris, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceCamdessanche, Jean-Philippe论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp St Etienne, Hop Nord, Neuromuscular Dis Reference Ctr, Dept Neurol, St Etienne, France Ctr Reference Neuromusculaire Nord Est Ile De Fran, Strasbourg, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceChanson, Jean-Baptiste论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Strasbourg, Ctr Reference Malad Neuromusculaires Nord Est Ile, Strasbourg, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceCintas, Pascal论文数: 0 引用数: 0 h-index: 0机构: Hop Pierre Paul Riquet, Ctr SLA, Toulouse, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceMagy, Laurent论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Dupuytren, Ctr Reference Natl Neuropathies Peripher Rares, Serv & Lab Neurol, F-87042 Limoges, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceSignate, Aissatou论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Martinique, Serv Neurol, Fort De France, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceSole, Guilhem论文数: 0 引用数: 0 h-index: 0机构: CHU Bordeaux, Ctr Hosp Univ Bordeaux, Ctr Reference Malad Neuromusculaires AOC, Serv Neurol & Malad Neuromusculaires,Filnemus,Euro, Bordeaux, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceSvahn, Juliette论文数: 0 引用数: 0 h-index: 0机构: Hosp Civils Lyon, Hosp Civils Lyon, Serv Pathol Neuromusculaires, Lyon, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceTard, Celine论文数: 0 引用数: 0 h-index: 0机构: CHU Lille, Ctr Reference Malad Neuromusculaires Nord Est Ile, Serv Neurol, Lille, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceHababou, Cyrla论文数: 0 引用数: 0 h-index: 0机构: EFS, 100 Ave Suffren, F-75015 Paris, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, FranceAttarian, Shahram论文数: 0 引用数: 0 h-index: 0机构: Aix Marseille Univ, CHU Timone, Ctr Reference Malad Neuromusculaires & SLA, Marseille, France CHU Nantes, Ctr Reference Malad Neuromusculaires AOC, Hotel Dieu, Euro NMD,Filnemus, Nantes, France
- [24] HELIOS-A: 18-MONTH EXPLORATORY CARDIAC RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSISEUROPEAN HEART JOURNAL SUPPLEMENTS, 2022, 24Mussinelli, Roberta论文数: 0 引用数: 0 h-index: 0机构: Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyGarcia-pavia, Pablo论文数: 0 引用数: 0 h-index: 0机构: Cibercv, Hosp Univ Puerta Hierro Majadahonda, Madrid, Spain Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyKale, Parag论文数: 0 引用数: 0 h-index: 0机构: Baylor Univ, Med Ctr, Ctr Adv Heart & Lung Dis, Dallas, TX USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Amyloidosis Ctr, Boston Med Ctr, Boston, MA USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyMaurer, Mathew S.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Med Ctr, Ctr Adv Cardiac Care, Div Cardiol,Dept Med, New York, NY USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal Fac Med, Lisbon, Portugal Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyDicarli, Marcelo论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Brigham & Womens Hosp, Dept Med, Boston, MA USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalySolomon, Scott论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens Hosp, Div Cardiovasc, Boston, MA USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyChen, Chongshu论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyGrogan, Martha论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Dept Cardiovasc Dis, Rochester, MN USA Fdn Irccs Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy
- [25] INOTERSEN IMPROVES MODIFIED NEUROPATHY IMPAIRMENT SCORE PLUS 7 (MNIS+7) MEASURES IN PATIENTS WITH HEREDITARY TRANSTHYRETIN (HATTR) AMYLOIDOSIS IN THE PHASE 3 STUDY NEURO-TTRMUSCLE & NERVE, 2018, 58 : S55 - S55Dyck, Peter论文数: 0 引用数: 0 h-index: 0Litchy, William论文数: 0 引用数: 0 h-index: 0Wang, Annabel论文数: 0 引用数: 0 h-index: 0Cruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0Polydefkis, Michael论文数: 0 引用数: 0 h-index: 0Scheinberg, Morton论文数: 0 引用数: 0 h-index: 0Berk, John论文数: 0 引用数: 0 h-index: 0Barroso, Fabio论文数: 0 引用数: 0 h-index: 0Brannagan, Thomas论文数: 0 引用数: 0 h-index: 0Drachman, Brian论文数: 0 引用数: 0 h-index: 0Heitner, Stephen论文数: 0 引用数: 0 h-index: 0Gorevic, Peter论文数: 0 引用数: 0 h-index: 0Monia, Brett论文数: 0 引用数: 0 h-index: 0Gertz, Morie论文数: 0 引用数: 0 h-index: 0Benson, Merrill论文数: 0 引用数: 0 h-index: 0
- [26] Long-term efficacy and safety of Inotersen in patients with hereditary transthyretin (hATTR) amyloidosis treated in the open-label extension of the phase-3 study NEURO-TTREUROPEAN JOURNAL OF NEUROLOGY, 2018, 25 : 30 - 30Plante-Bordeneuve, V.论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Creteil, France CHU Henri Mondor, Creteil, France论文数: 引用数: h-index:机构:Wang, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Orange, CA 92668 USA CHU Henri Mondor, Creteil, FranceCoelho, T.论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Porto, Portugal CHU Henri Mondor, Creteil, FranceCruz, M. Waddington论文数: 0 引用数: 0 h-index: 0机构: Fed Univ Rio de Janeiro Univ Hosp, Rio De Janeiro, Brazil CHU Henri Mondor, Creteil, FrancePolydefkis, M.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA CHU Henri Mondor, Creteil, FranceDyck, P.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA CHU Henri Mondor, Creteil, FranceScheinberg, M.论文数: 0 引用数: 0 h-index: 0机构: Assoc Assistencia Crianca Deficiente, Sao Paulo, Brazil CHU Henri Mondor, Creteil, France论文数: 引用数: h-index:机构:Barroso, F.论文数: 0 引用数: 0 h-index: 0机构: FLENI, Buenos Aires, DF, Argentina CHU Henri Mondor, Creteil, FranceAdams, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, CHU Bicetre, Le Kremlin Bicetre, France CHU Henri Mondor, Creteil, FranceWhelan, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, London, England CHU Henri Mondor, Creteil, FranceMerlini, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Pavia, IRCCS Policlin San Matteo, Amyloidosis Ctr, Pavia, Italy CHU Henri Mondor, Creteil, FranceDrachman, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Philadelphia, PA 19104 USA CHU Henri Mondor, Creteil, FranceHeitner, S.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Portland, OR 97201 USA CHU Henri Mondor, Creteil, FranceConceicao, I.论文数: 0 引用数: 0 h-index: 0机构: Hosp Santa Maria CHLN, Lisbon, Portugal UL, IMM Fac Med, Lisbon, Portugal CHU Henri Mondor, Creteil, FranceSchmidt, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Klinikum Munster, Munster, Germany CHU Henri Mondor, Creteil, FranceVita, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, AOU Policlin G Martino, Messina, Italy CHU Henri Mondor, Creteil, FranceCampistol, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Clin Barcelona, Barcelona, Spain CHU Henri Mondor, Creteil, FranceGamez, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall DHebron, Barcelona, Spain CHU Henri Mondor, Creteil, FranceGorevic, P.论文数: 0 引用数: 0 h-index: 0机构: Mt Sinai Med Ctr, New York, NY 10029 USA CHU Henri Mondor, Creteil, FranceMonia, B.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA CHU Henri Mondor, Creteil, FranceBenson, M.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA CHU Henri Mondor, Creteil, FranceGertz, M.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA CHU Henri Mondor, Creteil, France
- [27] Prevalence and Clinical Characteristics of Patients with Transthyretin Amyloidosis in the United States and Japan: Results from the OverTTuRe StudyMETABOLISM-CLINICAL AND EXPERIMENTAL, 2024, 153Wright, Jason论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USA AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAAlvarez, Christian S.论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut Med, Cardiovasc Renal & Metab Epidemiol, Gaithersburg, MD USA AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAHong, Lai San论文数: 0 引用数: 0 h-index: 0机构: Redsen Ltd, Bournemouth, Dorset, England AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAJarbrink, Krister论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, Cardiovasc Renal & Metab Evidence, BioPharmaceut Med, Gothenburg, Sweden AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAKumar, Neela论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut Med, Payer & Real World Evidence, Wilmington, DE USA AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAPao, Christina论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USA AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAWittbrodt, Eric论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut Med, Cardiovasc Renal & Metab Epidemiol, Gaithersburg, MD USA AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USAKohsaka, Shun论文数: 0 引用数: 0 h-index: 0机构: Keio Univ, Sch Med, Dept Cardiol, Tokyo, Japan AstraZeneca, BioPharmaceut Med, Global Med Affairs, Wilmington, DE USA
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