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- [1] hATTR ITALIAN REGISTRY: PRELIMINARY DATA FROM THE COLLABORATIVE NETWORK OF TELETHON GUP 15010 STUDYJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2019, 24 : S38 - S39Russo, M.论文数: 0 引用数: 0 h-index: 0机构: Fdn Aurora Onlus, Messina, Italy Fdn Aurora Onlus, Messina, ItalyMerlini, G.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Fdn Aurora Onlus, Messina, ItalyObici, L.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Fdn Aurora Onlus, Messina, ItalyPacciolla, P.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Fdn Aurora Onlus, Messina, ItalyFabrizi, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Verona, Dept Neurosci Biomed & Movement Sci, Verona, Italy Fdn Aurora Onlus, Messina, ItalyCavallaro, T.论文数: 0 引用数: 0 h-index: 0机构: Univ Verona, Dept Neurosci Biomed & Movement Sci, Verona, Italy Fdn Aurora Onlus, Messina, ItalySabatelli, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin A Gemelli Fdn, Dept Geriatr Neurosci & Orthoped, Rome, Italy Fdn Aurora Onlus, Messina, ItalyLuigetti, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin A Gemelli Fdn, Dept Geriatr Neurosci & Orthoped, Rome, Italy Fdn Aurora Onlus, Messina, ItalyBisogni, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin A Gemelli Fdn, Dept Geriatr Neurosci & Orthoped, Rome, Italy Fdn Aurora Onlus, Messina, ItalyPareyson, D.论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ist Neurol Carlo Besta, Milan, Italy Fdn Aurora Onlus, Messina, ItalyFenu, S.论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ist Neurol Carlo Besta, Milan, Italy Fdn Aurora Onlus, Messina, ItalyCalabrese, D.论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ist Neurol Carlo Besta, Milan, Italy Fdn Aurora Onlus, Messina, ItalyRapezzi, C.论文数: 0 引用数: 0 h-index: 0机构: Amyloidosis Ctr, Bologna, Italy Fdn Aurora Onlus, Messina, ItalyBartolomei, I论文数: 0 引用数: 0 h-index: 0机构: Amyloidosis Ctr, Bologna, Italy Fdn Aurora Onlus, Messina, ItalyGrandis, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Genoa, Dept Neurosci Rehabil Ophthalmol Genet & Maternal, Genoa, Italy Fdn Aurora Onlus, Messina, ItalyGemelli, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Genoa, Dept Neurosci Rehabil Ophthalmol Genet & Maternal, Genoa, Italy Fdn Aurora Onlus, Messina, ItalyMauro, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Torino, Dipartimento Neurosci Rita Levi Montalcini, Turin, Italy Fdn Aurora Onlus, Messina, ItalyPradotto, L.论文数: 0 引用数: 0 h-index: 0机构: IRCCS, Ist Auxol Italiano, Div Neurol & Neuroriabilitaz, Oggebbio, VB, Italy Fdn Aurora Onlus, Messina, ItalySantoro, L.论文数: 0 引用数: 0 h-index: 0机构: Univ Federico II, Dept Neurosci Reprod & Odontostomatol Sci, Naples, Italy Fdn Aurora Onlus, Messina, ItalyManganelli, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Federico II, Dept Neurosci Reprod & Odontostomatol Sci, Naples, Italy Fdn Aurora Onlus, Messina, ItalyAntonini, G.论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Roma, Dip NESMOS, Osped St Andrea, Rome, Italy Fdn Aurora Onlus, Messina, ItalyLeonardi, L.论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Roma, Dip NESMOS, Osped St Andrea, Rome, Italy Fdn Aurora Onlus, Messina, ItalyVanoli, F.论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Roma, Dip NESMOS, Osped St Andrea, Rome, Italy Fdn Aurora Onlus, Messina, ItalyMy, F.论文数: 0 引用数: 0 h-index: 0机构: Osped V Fazzi, Div Neurol, Lecce, Italy Fdn Aurora Onlus, Messina, Italy论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Mazzeo, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, Neurol & Neuromuscular Dis, Dept Clin & Expt Med, Messina, Italy Fdn Aurora Onlus, Messina, ItalyVita, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, Neurol & Neuromuscular Dis, Dept Clin & Expt Med, Messina, Italy Fdn Aurora Onlus, Messina, Italy
- [2] Patisiran, an Investigational RNAi Therapeutic for Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Polyneuropathy: Results from the Phase 3 APOLLO studyNEUROLOGY, 2018, 90Adams, David论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, France CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Med Sci & Nutr Salvador Zubiran INCMNSZ, Mexico City, DF, Mexico CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceO'Riordan, William论文数: 0 引用数: 0 h-index: 0机构: eStudy Site, La Mesa, TX USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceYang, Chih-Chao论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Taipei, Taiwan CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceYamashita, Taro论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ, Kumamoto, Japan CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceKristen, Arnt论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Heidelberg, Germany CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceTournev, Ivaylo论文数: 0 引用数: 0 h-index: 0机构: Univ Multiprofile Hosp Act Treatment, Sofia, Bulgaria CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceSchmidt, Hartmut论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Muenster, Munster, Germany CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Hosp Santo Antonio, Porto, Portugal CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Amyloid Treatment & Res Program, Boston, MA 02215 USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceLin, Kon-Ping论文数: 0 引用数: 0 h-index: 0机构: Taipei Vet Gen Hosp, Taipei, Taiwan CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceDyck, Peter J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceGandhi, Pritesh论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceSweetser, Marianne论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceChen, Jihong论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceGoyal, Sunita论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceGollob, Jared论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, FranceSuhr, Ole论文数: 0 引用数: 0 h-index: 0机构: Umea Univ Hosp, Umea, Sweden CHU Bicetre Le Kremlin, Natl Reference Ctr FAP NNERF, AP HP, INSERM U 1195, Paris, France
- [3] Phase 3 Multicenter Study of Revusiran in Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Cardiomyopathy (ENDEAVOUR)CARDIOVASCULAR DRUGS AND THERAPY, 2020, 34 (03) : 357 - 370Judge, Daniel P.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ Hosp, Baltimore, MD 21287 USA Med Univ South Carolina, Charleston, SC 29425 USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAKristen, Arnt V.论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Dept Cardiol, Heidelberg, Germany Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAGrogan, Martha论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAMaurer, Mathew S.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Med Ctr, New York, NY USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAFalk, Rodney H.论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAHanna, Mazen论文数: 0 引用数: 0 h-index: 0机构: Cleveland Clin, Cleveland, OH 44106 USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAGillmore, Julian论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, UCL Med Sch, Div Med, Natl Amyloidosis Ctr, Rowland Hill St, London NW3 2PF, England Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAGarg, Pushkal论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAVaishnaw, Akshay K.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAHarrop, Jamie论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAPowell, Christine论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAKarsten, Verena论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAZhang, Xiaoping论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USASweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Johns Hopkins Univ Hosp, Baltimore, MD 21287 USAHawkins, Philip N.论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, UCL Med Sch, Div Med, Natl Amyloidosis Ctr, Rowland Hill St, London NW3 2PF, England Johns Hopkins Univ Hosp, Baltimore, MD 21287 USA
- [4] Phase 3 Multicenter Study of Revusiran in Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Cardiomyopathy (ENDEAVOUR)Cardiovascular Drugs and Therapy, 2020, 34 : 357 - 370Daniel P. Judge论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyArnt V. Kristen论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMartha Grogan论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMathew S. Maurer论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyRodney H. Falk论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMazen Hanna论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyJulian Gillmore论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyPushkal Garg论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyAkshay K. Vaishnaw论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyJamie Harrop论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyChristine Powell论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyVerena Karsten论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyXiaoping Zhang论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMarianne T. Sweetser论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyJohn Vest论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyPhilip N. Hawkins论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of Cardiology
- [5] Inotersen improves quality of life and neuropathy in patients with hereditary transthyretin (hATTR) amyloidosis with polyneuropathy: results of the phase 3 study NEURO-TTREUROPEAN JOURNAL OF NEUROLOGY, 2018, 25 : 376 - 376Coelho, T.论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Porto, Portugal Ctr Hosp Porto, Porto, PortugalWang, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Orange, CA 92668 USA Ctr Hosp Porto, Porto, PortugalWaddington Cruz, M.论文数: 0 引用数: 0 h-index: 0机构: Fed Univ Rio de Janeiro Univ Hosp, Rio De Janeiro, Brazil Ctr Hosp Porto, Porto, PortugalPolydefkis, M.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Ctr Hosp Porto, Porto, PortugalDyck, P.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Ctr Hosp Porto, Porto, PortugalScheinberg, M.论文数: 0 引用数: 0 h-index: 0机构: Assoc Assistencia Crianca Deficiente, Sao Paulo, Brazil Ctr Hosp Porto, Porto, PortugalPlante-Bordeneuve, V.论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Creteil, France Ctr Hosp Porto, Porto, Portugal论文数: 引用数: h-index:机构:Barroso, F.论文数: 0 引用数: 0 h-index: 0机构: FLENI, Buenos Aires, DF, Argentina Ctr Hosp Porto, Porto, PortugalAdams, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, CHU Bicetre, Le Kremlin Bicetre, France Ctr Hosp Porto, Porto, Portugal论文数: 引用数: h-index:机构:Whelan, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, London, England Ctr Hosp Porto, Porto, PortugalMerlini, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Pavia, IRCCS Policlin San Matteo, Amyloidosis Ctr, Pavia, Italy Ctr Hosp Porto, Porto, PortugalDrachman, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Philadelphia, PA 19104 USA Ctr Hosp Porto, Porto, PortugalHeitner, S.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Portland, OR 97201 USA Ctr Hosp Porto, Porto, PortugalConceicao, I.论文数: 0 引用数: 0 h-index: 0机构: CHLN, Hosp Santa Maria, Lisbon, Portugal UL, IMM Fac Med, Lisbon, Portugal Ctr Hosp Porto, Porto, PortugalSchmidt, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Klinikum Munster, Munster, Germany Ctr Hosp Porto, Porto, PortugalVita, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, AOU Policlin G Martino, Messina, Italy Ctr Hosp Porto, Porto, PortugalGamez, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall DHebron, Barcelona, Spain Ctr Hosp Porto, Porto, PortugalGane, E.论文数: 0 引用数: 0 h-index: 0机构: Auckland City Hosp, Auckland, New Zealand Ctr Hosp Porto, Porto, PortugalGorevic, P.论文数: 0 引用数: 0 h-index: 0机构: Mt Sinai Med Ctr, New York, NY 10029 USA Ctr Hosp Porto, Porto, PortugalSouza Bulle Oliveira, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Sao Paulo, Sao Paulo, Brazil Ctr Hosp Porto, Porto, PortugalMonia, B.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Ctr Hosp Porto, Porto, PortugalGertz, M.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Ctr Hosp Porto, Porto, PortugalBenson, M.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Ctr Hosp Porto, Porto, Portugal
- [6] Correction to: Phase 3 Multicenter Study of Revusiran in Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Cardiomyopathy (ENDEAVOUR)Cardiovascular Drugs and Therapy, 2020, 34 : 889 - 889Daniel P. Judge论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyArnt V. Kristen论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMartha Grogan论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMathew S. Maurer论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyRodney H. Falk论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMazen Hanna论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyJulian Gillmore论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyPushkal Garg论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyAkshay K. Vaishnaw论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyJamie Harrop论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyChristine Powell论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyVerena Karsten论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyXiaoping Zhang论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyMarianne T. Sweetser论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyJohn Vest论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of CardiologyPhilip N. Hawkins论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Hospital,Department of Cardiology
- [7] HEREDITARY TRANSTHYRETIN AMILOYDOSIS (HATTR): DESCRIPTION OF THE FIRST COHORT OF V122I PATIENTS FROM SOUTH ITALYJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2019, 24 : S24 - S24Gentile, L.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyDi Bella, G.论文数: 0 引用数: 0 h-index: 0机构: UOC Cardiol, Dipartimento Med Clin & Sperimentale, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyAguennouz, M.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyStancanelli, C.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyRusso, M.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Ctr Clin Nemo Sud, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyAntonio, T.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyVita, G.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, ItalyMazzeo, A.论文数: 0 引用数: 0 h-index: 0机构: Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy Policlin G Martino, Dipartimento Med Clin & Sperimentale, UOC Neurol & Malattie Neuromuscolari, Messina, Italy
- [8] Open-label extension of NEURO-TTR study in patients with hereditary transthyretin (hATTR) amyloidosis: Long-term updateJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2018, 23 (04) : 385 - 386论文数: 引用数: h-index:机构:Wang, Annabel论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Orange, CA 92668 USA Columbia Univ, Med Ctr, New York, NY USACoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Porto, Portugal Columbia Univ, Med Ctr, New York, NY USACruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Univ Hosp, Rio De Janeiro, Brazil Columbia Univ, Med Ctr, New York, NY USAPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Columbia Univ, Med Ctr, New York, NY USADyck, Peter论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Columbia Univ, Med Ctr, New York, NY USAPlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Creteil, France Columbia Univ, Med Ctr, New York, NY USA论文数: 引用数: h-index:机构:Barroso, Fabio论文数: 0 引用数: 0 h-index: 0机构: FLENI, Buenos Aires, DF, Argentina Columbia Univ, Med Ctr, New York, NY USAAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, CHU Bicetre, Paris, France Columbia Univ, Med Ctr, New York, NY USAMerlini, Giampaolo论文数: 0 引用数: 0 h-index: 0机构: Univ Pavia, Amyloidosis Ctr, IRCCS Policlin San Matteo, Pavia, Italy Columbia Univ, Med Ctr, New York, NY USAConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Hosp Santa Maria, CHLN, Lisbon, Portugal Columbia Univ, Med Ctr, New York, NY USAMonia, Brett论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Columbia Univ, Med Ctr, New York, NY USAHughes, Steven论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Columbia Univ, Med Ctr, New York, NY USAKwoh, Jesse论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Columbia Univ, Med Ctr, New York, NY USAJung, Shiangtung论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Columbia Univ, Med Ctr, New York, NY USABaker, Brenda论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Columbia Univ, Med Ctr, New York, NY USAAckermann, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Columbia Univ, Med Ctr, New York, NY USABenson, Merrill论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Columbia Univ, Med Ctr, New York, NY USAGertz, Morie论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Columbia Univ, Med Ctr, New York, NY USA
- [9] Evaluation of Quality of Life and Disability in Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Polyneuropathy Following Treatment with Patisiran, An Investigational RNAi Therapeutic: Results from the Phase 3 APOLLO StudyNEUROLOGY, 2018, 90Adams, David论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, France CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Med Sci & Nutr Salvador Zubiran INCMNSZ, Mexico City, DF, Mexico CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceO'Riordan, William论文数: 0 引用数: 0 h-index: 0机构: eStudy Site, La Mesa, TX USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceYang, Chih-Chao论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Taipei, Taiwan CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceYamashita, Taro论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ Hosp, Kumamoto, Japan CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceKristen, Arnt论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Heidelberg, Germany CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceTournev, Ivaylo论文数: 0 引用数: 0 h-index: 0机构: Univ Multiprofile Hosp Act Treatment, Sofia, Bulgaria CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceSchmidt, Hartmut论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Muenster, Munster, Germany CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Hosp Santo Antonio, Ctr Hosp Porto, Porto, Portugal CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Amyloid Treatment & Res Program, Boston, MA 02215 USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceLin, Kong-Ping论文数: 0 引用数: 0 h-index: 0机构: Taipei Vet Gen Hosp, Taipei, Taiwan CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceDyck, Peter J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceGandhi, Pritesh论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceSweetser, Marianne论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceChen, Jihong论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceGoyal, Sunita论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceGollob, Jared论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, FranceSuhr, Ole论文数: 0 引用数: 0 h-index: 0机构: Umea Univ Hosp, Umea, Sweden CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, France
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