Immune response to enzyme replacement therapy in Fabry disease: Impact on clinical outcome?

被引：28

作者：

Hollak, C. E. M. ^{[1
]}

Linthorst, G. E. ^{[1
]}

机构：

[1] Univ Amsterdam, Acad Med Ctr, Dept Internal Med Endocrinol & Metab, NL-1105 AZ Amsterdam, Netherlands

来源：

MOLECULAR GENETICS AND METABOLISM | 2009年 / 96卷 / 01期

关键词：

Fabry disease; Antibody; GL-3; Globotriaosylceramide; Enzyme therapy; Agalsidase; AGALSIDASE-BETA THERAPY; HUMAN ALPHA-GALACTOSIDASE; NEUTRALIZING ANTIBODIES; GAUCHERS-DISEASE; EFFICACY; SAFETY; TRIAL; GLOBOTRIAOSYLCERAMIDE; MANIFESTATIONS; GLUCOSIDASE;

D O I：

10.1016/j.ymgme.2008.10.013

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：1 / 3

页数：3

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