Strategies in the delivery of Cas9 ribonucleoprotein for CRISPR/Cas9 genome editing

被引:289
作者
Zhang, Song [1 ]
Shen, Jiangtao [2 ]
Li, Dali [3 ]
Cheng, Yiyun [1 ,3 ]
机构
[1] South China Univ Technol, Sch Mol Sci & Engn, South China Adv Inst Soft Matter Sci & Technol, Guangzhou 510640, Peoples R China
[2] Yangzhou Univ, Peoples Hosp Taizhou 2, Taizhou 225500, Peoples R China
[3] East China Normal Univ, Shanghai Key Lab Regulatory Biol, Shanghai 200241, Peoples R China
基金
国家重点研发计划; 中国国家自然科学基金;
关键词
genome editing; CRISPR; RNP; polymers; nanoparticles; SPHERICAL NUCLEIC-ACIDS; BLACK PHOSPHORUS NANOSHEETS; HOMOLOGY-DIRECTED REPAIR; EFFICIENT DELIVERY; PROTEIN DELIVERY; IN-VITRO; EXTRACELLULAR VESICLES; NANOPARTICLE DELIVERY; INTRACELLULAR PROTEIN; MEDIATED DELIVERY;
D O I
10.7150/thno.47007
中图分类号
R-3 [医学研究方法]; R3 [基础医学];
学科分类号
1001 ;
摘要
CRISPR/Cas9 genome editing has gained rapidly increasing attentions in recent years, however, the translation of this biotechnology into therapy has been hindered by efficient delivery of CRISPR/Cas9 materials into target cells. Direct delivery of CRISPR/Cas9 system as a ribonucleoprotein (RNP) complex consisting of Cas9 protein and single guide RNA (sgRNA) has emerged as a powerful and widespread method for genome editing due to its advantages of transient genome editing and reduced off-target effects. In this review, we summarized the current Cas9 RNP delivery systems including physical approaches and synthetic carriers. The mechanisms and beneficial roles of these strategies in intracellular Cas9 RNP delivery were reviewed. Examples in the development of stimuli-responsive and targeted carriers for RNP delivery are highlighted. Finally, the challenges of current Cas9 RNP delivery systems and perspectives in rational design of next generation materials for this promising field will be discussed.
引用
收藏
页码:614 / 648
页数:35
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