REDUCTION OF PROLONGED CAG REPEAT CONTAINING ALLELES IN HUNTINGTON'S DISEASE USING ANTISENSE OLIGONUCLEOTIDES

被引：0
|
作者：
Evers, M. M. [1 ]
van Deutekom, J. C. T. [2 ]
Mulders, S. A. M. [2 ]
Aartsma-Rus, A. M. [1 ]
Weiss, A. [3 ]
Roscic, A. [3 ]
den Dunnen, J. T. [1 ,4 ]
van Ommen, G-J B. [1 ]
van Roon-Mom, W. M. C. [1 ]
机构：
[1] Leiden Univ, Med Ctr, Ctr Human & Clin Genet, Leiden, Netherlands
[2] Prosensa Therapeut BV, Leiden, Netherlands
[3] Novartis Pharma AG, Novartis Inst Biomed Res, Basel, Switzerland
[4] Leiden Univ, Med Ctr, Genome Technol Ctr, Leiden, Netherlands
来源：
JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY | 2010年 / 81卷
关键词：
D O I：
10.1136/jnnp.2010.222596.8
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：A13 / A13
页数：1
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