Cystic Fibrosis in the Era of Highly Effective CFTR Modulators

被引:1
作者
Britto, Clemente J. [1 ]
Taylor-Cousar, Jennifer L. [2 ,3 ]
机构
[1] Yale Univ, Dept Internal Med, Div Pulm Crit Care & Sleep Med, Sch Med, 300 Cedar St,TAC S419, New Haven, CT 06520 USA
[2] Univ Colorado, Dept Med & Pediat, Div Pulm Sci & Crit Care Med, Anschutz Med Campus,1400 Jackson St,J318, Denver, CO 80206 USA
[3] Univ Colorado, Div Pediat Pulmonol, Anschutz Med Campus,1400 Jackson St,J318, Denver, CO 80206 USA
关键词
TEZACAFTOR-IVACAFTOR; THERAPY; CHILDREN; GENE;
D O I
10.1016/j.ccm.2022.07.003
中图分类号
R56 [呼吸系及胸部疾病];
学科分类号
摘要
引用
收藏
页码:XIII / XVI
页数:4
相关论文
共 50 条
  • [1] Gallium Compounds Exhibit Potential as New Therapeutic Agents against Mycobacterium abscessus
    Abdalla, Maher Y.
    Switzer, Barbara L.
    Goss, Christopher H.
    Aitken, Moira L.
    Singh, Pradeep K.
    Britigan, Bradley E.
    [J]. ANTIMICROBIAL AGENTS AND CHEMOTHERAPY, 2015, 59 (08) : 4826 - 4834
  • [2] Cystic fibrosis of the pancreas and its relation to celiac disease - A clinical and pathologic study
    Andersen, DH
    [J]. AMERICAN JOURNAL OF DISEASES OF CHILDREN, 1938, 56 (02): : 344 - 399
  • [3] [Anonymous], 2018, PATIENT REGISTRY
  • [4] Lumacaftor (VX-809) restores the ability of CF macrophages to phagocytose and kill Pseudomonas aeruginosa
    Barnaby, Roxanna
    Koeppen, Katja
    Nymon, Amanda
    Hampton, Thomas H.
    Berwin, Brent
    Ashare, Alix
    Stanton, Bruce A.
    [J]. AMERICAN JOURNAL OF PHYSIOLOGY-LUNG CELLULAR AND MOLECULAR PHYSIOLOGY, 2018, 314 (03) : L432 - L438
  • [5] Impact of Cystic Fibrosis Transmembrane Conductance Regulator Therapy on Chronic Rhinosinusitis and Health Status Deep Learning CT Analysis and Patient-reported Outcomes
    Beswick, Daniel M.
    Humphries, Stephen M.
    Balkissoon, Connor D.
    Strand, Matthew
    Vladar, Eszter K.
    Lynch, David A.
    Taylor-Cousar, Jennifer L.
    [J]. ANNALS OF THE AMERICAN THORACIC SOCIETY, 2022, 19 (01) : 12 - 19
  • [6] New approaches to genetic therapies for cystic fibrosis
    Boyd, A. Christopher
    Guo, Shuling
    Huang, Lulu
    Kerem, Batsheva
    Oren, Yifat S.
    Walker, Amy J.
    Hart, Stephen L.
    [J]. JOURNAL OF CYSTIC FIBROSIS, 2020, 19 : S54 - S59
  • [7] Bacteriophage therapy for infections in CF
    Chan, Benjamin K.
    Stanley, Gail
    Modak, Mrinalini
    Koff, Jon L.
    Turner, Paul E.
    [J]. PEDIATRIC PULMONOLOGY, 2021, 56 : S4 - S9
  • [8] CFTR modulator theratyping: Current status, gaps and future directions
    Clancy, John Paul
    Cotton, Calvin U.
    Donaldson, Scott H.
    Solomon, George M.
    VanDevanter, Donald R.
    Boyle, Michael P.
    Gentzsch, Martina
    Nick, Jerry A.
    Illek, Beate
    Wallenburg, John C.
    Sorscher, Eric J.
    Amaral, Margarida D.
    Beekman, Jeffrey M.
    Naren, Anjaparavanda P.
    Bridges, Robert J.
    Thomas, Philip J.
    Cutting, Garry
    Rowe, Steven
    Durmowicz, Anthony G.
    Mense, Martin
    Boeck, Kris D.
    Skach, William
    Penland, Christopher
    Joseloff, Elizabeth
    Bihler, Hermann
    Mahoney, John
    Borowitz, Drucy
    Tuggle, Katherine L.
    [J]. JOURNAL OF CYSTIC FIBROSIS, 2019, 18 (01) : 22 - 34
  • [9] Targeted Correction and Restored Function of the CFTR Gene in Cystic Fibrosis Induced Pluripotent Stem Cells
    Crane, Ana M.
    Kramer, Philipp
    Bui, Jacquelin H.
    Chung, Wook Joon
    Li, Xuan Shirley
    Gonzalez-Garay, Manuel L.
    Hawkins, Finn
    Liao, Wei
    Mora, Daniela
    Choi, Sangbum
    Wang, Jianbin
    Sun, Helena C.
    Paschon, David E.
    Guschin, Dmitry Y.
    Gregory, Philip D.
    Kotton, Darrell N.
    Holmes, Michael C.
    Sorscher, Eric J.
    Davis, Brian R.
    [J]. STEM CELL REPORTS, 2015, 4 (04): : 569 - 577
  • [10] Cystic fibrosis since 1938
    Davis, PB
    [J]. AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2006, 173 (05) : 475 - 482