Dawn of a new therapeutic era for spinal muscular atrophy

被引:5
|
作者
Gillingwater, Thomas H. [1 ,2 ]
机构
[1] Univ Edinburgh, Euan MacDonald Ctr Motor Neurone Dis Res, Edinburgh EH8 9AG, Midlothian, Scotland
[2] Univ Edinburgh, Ctr Integrat Physiol, Edinburgh Med Sch Biomed Sci, Edinburgh EH8 9AG, Midlothian, Scotland
来源
LANCET | 2016年 / 388卷 / 10063期
关键词
RESCUE; GENE;
D O I
10.1016/S0140-6736(16)32390-X
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:2964 / 2965
页数:2
相关论文
共 50 条
  • [1] SPINAL MUSCULAR ATROPHY: DIAGNOSIS AND MANAGEMENT IN A NEW THERAPEUTIC ERA
    Arnold, W. David
    Kassar, Darine
    Kissel, John T.
    MUSCLE & NERVE, 2015, 51 (02) : 157 - 167
  • [2] Respiratory care in spinal muscular atrophy in the new therapeutic era
    Angelica Palomino, Maria
    Castiglioni, Claudia
    REVISTA CHILENA DE PEDIATRIA-CHILE, 2018, 89 (06): : 685 - 693
  • [3] Spinal muscular atrophy - challenges in the therapeutic era
    Faravelli, Irene
    Corti, Stefania
    NATURE REVIEWS NEUROLOGY, 2020, 16 (12) : 655 - 656
  • [4] Spinal Muscular Atrophy (SMA) in the Therapeutic Era
    Gibbons, Melissa
    Stratton, Anne
    Parsons, Julie
    CURRENT GENETIC MEDICINE REPORTS, 2019, 7 (03) : 162 - 167
  • [5] Spinal muscular atrophy — challenges in the therapeutic era
    Irene Faravelli
    Stefania Corti
    Nature Reviews Neurology, 2020, 16 : 655 - 656
  • [6] Spinal Muscular Atrophy (SMA) in the Therapeutic Era
    Melissa Gibbons
    Anne Stratton
    Julie Parsons
    Current Genetic Medicine Reports, 2019, 7 : 162 - 167
  • [7] Perspectives in genetic counseling for spinal muscular atrophy in the new therapeutic era
    Serra-Juhe, C.
    Abuli Vidal, A.
    Codina Sola, M.
    Rovira Moreno, E.
    Tizzano Ferrari, E. F.
    EUROPEAN JOURNAL OF HUMAN GENETICS, 2019, 27 : 1794 - 1794
  • [8] Innovating spinal muscular atrophy models in the therapeutic era
    Signoria, Ilaria
    van der Pol, W. Ludo
    Groen, Ewout J. N.
    DISEASE MODELS & MECHANISMS, 2023, 16 (09)
  • [9] Spinal muscular atrophy — the dawning of a new era
    Michelle A. Farrar
    Matthew C. Kiernan
    Nature Reviews Neurology, 2020, 16 : 593 - 594
  • [10] Spinal muscular atrophy - the dawning of a new era
    Farrar, Michelle A.
    Kiernan, Matthew C.
    NATURE REVIEWS NEUROLOGY, 2020, 16 (11) : 593 - 594