Novel image analysis to assess molecular functionality of dystrophin in Duchenne muscular dystrophy clinical trials

被引：0

作者：

Scaglioni, D. ^{[1
]}

Catapano, F. ^{[1
]}

Ellis, M. ^{[1
]}

Torelli, S. ^{[1
]}

Chambers, D. ^{[1
]}

Feng, L. ^{[1
]}

Husayni, S. ^{[2
]}

Malhotra, J. ^{[2
]}

Harriman, S. ^{[2
]}

Koenig, E. ^{[2
]}

Dugar, A. ^{[2
]}

Steiner, D. ^{[2
]}

Morgan, J. ^{[1
]}

Phadke, R. ^{[1
]}

Muntoni, F. ^{[1
]}

机构：

[1] UCL, London, England

[2] Sarepta Therapeut Inc, Cambridge, MA USA

来源：

NEUROMUSCULAR DISORDERS | 2020年 / 30卷

关键词：

D O I：

10.1016/j.nmd.2020.08.126

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

P.123

引用

页码：S82 / S82

页数：1

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