Intravitreal rAAV2/2-ND4 (GS010): A gene therapy for vision loss in Leber's Hereditary Optic Neuropathy (LHON) caused by the G11778A ND4 mitochondrial mutation

被引：0

作者：

Uretsky, Scott ^{[1
]}

Vignal, Catherine ^{[5
]}

Thomasson, Nitza ^{[2
]}

Bouquet, Celine ^{[3
]}

Galy, Anne ^{[4
]}

Combal, Jean Philipppe ^{[4
]}

Fitoussi, Serge ^{[1
]}

Sahel, Jose-Alain ^{[6
,7
]}

机构：

[1] Clin, Paris, France

[2] Preclin, Paris, France

[3] Gen Sight Biol, Preclin, Paris, France

[4] GenSight Biol, Paris, France

[5] Fdn Adolphe De Rothschild, Paris, France

[6] CHNO Quinze Vignts, Retina, Ophthalmol, Paris, France

[7] Inst Vis, Paris, France

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D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

S26.005

引用

页数：3