Tissue Frataxin Increases After Administration of CTI-1601, a Frataxin Replacement Therapy in Development for the Treatment of Friedreich's Ataxia

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作者：
Bettoun, D.
Galas, T.
Schecter, D.
Ruiz, N.
Clayton, R.
Farmer, J.
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MOVEMENT DISORDERS | 2022年 / 37卷
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R74 [神经病学与精神病学];
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页码：S243 / S243
页数：1
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[2]   A Combined Nucleic Acid and Protein Analysis in Friedreich Ataxia: Implications for Diagnosis, Pathogenesis and Clinical Trial Design [J].
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PLOS ONE, 2011, 6 (03)
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