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- [1] Effect of VX-770 in Persons with Cystic Fibrosis and the G551D-CFTR Mutation[J]. NEW ENGLAND JOURNAL OF MEDICINE, 2010, 363 (21) : 1991 - 2003Accurso, Frank J.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado Denver, Aurora, CO 80045 USA Childrens Hosp, Aurora, CO USA Univ Colorado Denver, Aurora, CO 80045 USARowe, Steven M.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Univ Colorado Denver, Aurora, CO 80045 USAClancy, J. P.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Univ Colorado Denver, Aurora, CO 80045 USABoyle, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Med Inst, Baltimore, MD 21205 USA Univ Colorado Denver, Aurora, CO 80045 USADunitz, Jordan M.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Colorado Denver, Aurora, CO 80045 USADurie, Peter R.论文数: 0 引用数: 0 h-index: 0机构: Hosp Sick Children, Toronto, ON M5G 1X8, Canada Univ Toronto, Toronto, ON, Canada Univ Colorado Denver, Aurora, CO 80045 USASagel, Scott D.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado Denver, Aurora, CO 80045 USA Childrens Hosp, Aurora, CO USA Univ Colorado Denver, Aurora, CO 80045 USAHornick, Douglas B.论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Carver Coll Med, Iowa City, IA USA Univ Colorado Denver, Aurora, CO 80045 USAKonstan, Michael W.论文数: 0 引用数: 0 h-index: 0机构: Rainbow Babies & Childrens Hosp, Cleveland, OH 44106 USA Case Western Reserve Univ, Sch Med, Cleveland, OH USA Univ Colorado Denver, Aurora, CO 80045 USADonaldson, Scott H.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Univ Colorado Denver, Aurora, CO 80045 USAMoss, Richard B.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Palo Alto, CA 94304 USA Univ Colorado Denver, Aurora, CO 80045 USAPilewski, Joseph M.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Pittsburgh, PA USA Univ Colorado Denver, Aurora, CO 80045 USARubenstein, Ronald C.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Penn, Sch Med, Philadelphia, PA 19104 USA Univ Colorado Denver, Aurora, CO 80045 USAUluer, Ahmet Z.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp, Boston, MA 02115 USA Univ Colorado Denver, Aurora, CO 80045 USAAitken, Moira L.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Seattle, WA 98195 USA Univ Colorado Denver, Aurora, CO 80045 USAFreedman, Steven D.论文数: 0 引用数: 0 h-index: 0机构: Beth Israel Deaconess Med Ctr, Boston, MA 02215 USA Univ Colorado Denver, Aurora, CO 80045 USARose, Lynn M.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Seattle, WA 98195 USA Seattle Childrens Hosp, Seattle, WA USA Univ Colorado Denver, Aurora, CO 80045 USAMayer-Hamblett, Nicole论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Seattle, WA 98195 USA Seattle Childrens Hosp, Seattle, WA USA Univ Colorado Denver, Aurora, CO 80045 USADong, Qunming论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USAZha, Jiuhong论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USAStone, Anne J.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USAOlson, Eric R.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USAOrdonez, Claudia L.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USACampbell, Preston W.论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Fdn Therapeut, Bethesda, MD USA Univ Colorado Denver, Aurora, CO 80045 USAAshlock, Melissa A.论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Fdn Therapeut, Bethesda, MD USA Univ Colorado Denver, Aurora, CO 80045 USARamsey, Bonnie W.论文数: 0 引用数: 0 h-index: 0机构: Seattle Childrens Hosp, Seattle, WA USA Univ Colorado Denver, Aurora, CO 80045 USA
- [2] Searching for a cure for cystic fibrosis. A 25-year quest in a nutshell[J]. EUROPEAN JOURNAL OF PEDIATRICS, 2016, 175 (01) : 1 - 8Bosch, Barbara论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Dept Paediat Pulmonol, B-3000 Louvain, Belgium Univ Hosp Leuven, Dept Paediat Pulmonol, B-3000 Louvain, BelgiumDe Boeck, Kris论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Dept Paediat Pulmonol, B-3000 Louvain, Belgium Univ Hosp Leuven, Dept Paediat Pulmonol, B-3000 Louvain, Belgium
- [3] Safety, pharmacokinetics, and pharmacodynamics of ivacaftor in patients aged 2-5 years with cystic fibrosis and a CFTR gating mutation (KIWI): an open-label, single-arm study[J]. LANCET RESPIRATORY MEDICINE, 2016, 4 (02) : 107 - 115Davies, Jane C.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, England Univ London Imperial Coll Sci Technol & Med, London, EnglandCunningham, Steve论文数: 0 引用数: 0 h-index: 0机构: Royal Hosp Sick Children, NHS Lothian, Edinburgh EH9 1LF, Midlothian, Scotland Univ London Imperial Coll Sci Technol & Med, London, EnglandHarris, William T.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Univ London Imperial Coll Sci Technol & Med, London, EnglandLapey, Allen论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Boston, MA 02114 USA Univ London Imperial Coll Sci Technol & Med, London, EnglandRegelmann, Warren E.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ London Imperial Coll Sci Technol & Med, London, EnglandSawicki, Gregory S.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Boston, MA USA Univ London Imperial Coll Sci Technol & Med, London, EnglandSouthern, Kevin W.论文数: 0 引用数: 0 h-index: 0机构: Univ Liverpool, Liverpool L69 3BX, Merseyside, England Univ London Imperial Coll Sci Technol & Med, London, EnglandRobertson, Sarah论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Boston, MA USA Univ London Imperial Coll Sci Technol & Med, London, EnglandGreen, Yulia论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Milton Pk, England Univ London Imperial Coll Sci Technol & Med, London, EnglandCooke, Jon论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Milton Pk, England Univ London Imperial Coll Sci Technol & Med, London, EnglandRosenfeld, Margaret论文数: 0 引用数: 0 h-index: 0机构: Seattle Childrens Hosp, Seattle, WA USA Univ London Imperial Coll Sci Technol & Med, London, England
- [4] Efficacy and Safety of Ivacaftor in Patients Aged 6 to 11 Years with Cystic Fibrosis with a G551D Mutation[J]. AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2013, 187 (11) : 1219 - 1225Davies, Jane C.论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England Univ London Imperial Coll Sci Technol & Med, London SW3 6LR, England Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandWainwright, Claire E.论文数: 0 引用数: 0 h-index: 0机构: Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandCanny, Gerard J.论文数: 0 引用数: 0 h-index: 0机构: Our Ladys Childrens Hosp, Dublin, Ireland Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandChilvers, Mark A.论文数: 0 引用数: 0 h-index: 0机构: British Columbia Childrens Hosp, Vancouver, BC V6H 3V4, Canada Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandHowenstine, Michelle S.论文数: 0 引用数: 0 h-index: 0机构: Riley Hosp Children, Indianapolis, IN USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandMunck, Anne论文数: 0 引用数: 0 h-index: 0机构: Hop Robert Debre, F-75019 Paris, France Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandMainz, Jochen G.论文数: 0 引用数: 0 h-index: 0机构: Jena Univ Hosp, Dept Pediat, Cyst Fibrosis Ctr, Jena, Germany Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandRodriguez, Sally论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandLi, Haihong论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandYen, Karl论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandOrdonez, Claudia L.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Cambridge, MA USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, EnglandAhrens, Richard论文数: 0 引用数: 0 h-index: 0机构: Univ Iowa, Dept Pediat, Iowa City, IA 52242 USA Royal Brompton & Harefield NHS Fdn Trust, Paediat Resp Med & Resp Biomed Res Unit, London, England
- [5] Flume PA, 2017, J CYST FIBROS
- [6] A CFTR Potentiator in Patients with Cystic Fibrosis and the G551D Mutation[J]. NEW ENGLAND JOURNAL OF MEDICINE, 2011, 365 (18) : 1663 - 1672Ramsey, Bonnie W.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Pediat, Seattle, WA 98105 USA Seattle Childrens Hosp, Seattle, WA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USADavies, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield Natl Hlth Serv Fdn Tru, Res Biomed Res Unit, London, England Univ Washington, Dept Pediat, Seattle, WA 98105 USAMcElvaney, N. Gerard论文数: 0 引用数: 0 h-index: 0机构: Beaumont Hosp, Royal Coll Surg Ireland, Beaumont, TX USA Univ Washington, Dept Pediat, Seattle, WA 98105 USATullis, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, St Michaels Hosp, Toronto, ON M5B 1W8, Canada Univ Washington, Dept Pediat, Seattle, WA 98105 USABell, Scott C.论文数: 0 引用数: 0 h-index: 0机构: Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Washington, Dept Pediat, Seattle, WA 98105 USADrevinek, Pavel论文数: 0 引用数: 0 h-index: 0机构: Charles Univ Prague, Dept Pediat, Sch Med 2, Prague, Czech Republic Univ Washington, Dept Pediat, Seattle, WA 98105 USAGriese, Matthias论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Washington, Dept Pediat, Seattle, WA 98105 USAMcKone, Edward F.论文数: 0 引用数: 0 h-index: 0机构: St Vincents Univ Hosp, Dublin 4, Ireland Univ Washington, Dept Pediat, Seattle, WA 98105 USAWainwright, Claire E.论文数: 0 引用数: 0 h-index: 0机构: St Vincents Univ Hosp, Dublin 4, Ireland Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Washington, Dept Pediat, Seattle, WA 98105 USAKonstan, Michael W.论文数: 0 引用数: 0 h-index: 0机构: Case Western Reserve Univ, Sch Med, Rainbow Babies & Childrens Hosp, Cleveland, OH USA Univ Washington, Dept Pediat, Seattle, WA 98105 USAMoss, Richard论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Stanford, CA 94305 USA Univ Washington, Dept Pediat, Seattle, WA 98105 USARatjen, Felix论文数: 0 引用数: 0 h-index: 0机构: Hosp Sick Children, Dept Pediat, Toronto, ON M5G 1X8, Canada Univ Washington, Dept Pediat, Seattle, WA 98105 USASermet-Gaudelus, Isabelle论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Ctr Invest Clin, Paris, France Univ Washington, Dept Pediat, Seattle, WA 98105 USARowe, Steven M.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Univ Washington, Dept Pediat, Seattle, WA 98105 USADong, Qunming论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USARodriguez, Sally论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USAYen, Karl论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USAOrdonez, Claudia论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USAElborn, J. Stuart论文数: 0 引用数: 0 h-index: 0机构: Queens Univ Belfast, Ctr Infect & Immun, Belfast, Antrim, North Ireland Univ Washington, Dept Pediat, Seattle, WA 98105 USA
- [7] Cystic fibrosis[J]. LANCET, 2003, 361 (9358) : 681 - 689Ratjen, F论文数: 0 引用数: 0 h-index: 0机构: Univ Essen Gesamthsch, Dept Paediat, Essen, Germany Univ Essen Gesamthsch, Dept Paediat, Essen, GermanyDöring, G论文数: 0 引用数: 0 h-index: 0机构: Univ Essen Gesamthsch, Dept Paediat, Essen, Germany
- [8] Clinical Mechanism of the Cystic Fibrosis Transmembrane Conductance Regulator Potentiator Ivacaftor in G551D-mediated Cystic Fibrosis[J]. AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2014, 190 (02) : 175 - 184Rowe, Steven M.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAHeltshe, Sonya L.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA Cyst Fibrosis Fdn Therapeut Dev Network, Seattle Childrens Res Inst, Seattle, WA USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAGonska, Tanja论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Hosp Sick Children, Res Inst, Dept Pediat, Toronto, ON M5G 1X8, Canada Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USADonaldson, Scott H.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Med, Chapel Hill, NC USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USABorowitz, Drucy论文数: 0 引用数: 0 h-index: 0机构: SUNY Buffalo, Sch Med & Biomed Sci, Dept Pediat, Buffalo, NY 14260 USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAGelfond, Daniel论文数: 0 引用数: 0 h-index: 0机构: SUNY Buffalo, Sch Med & Biomed Sci, Dept Pediat, Buffalo, NY 14260 USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USASagel, Scott D.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Colorado, Aurora, CO USA Univ Colorado, Sch Med, Aurora, CO USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAKhan, Umer论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Fdn Therapeut Dev Network, Seattle Childrens Res Inst, Seattle, WA USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAMayer-Hamblett, Nicole论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA Cyst Fibrosis Fdn Therapeut Dev Network, Seattle Childrens Res Inst, Seattle, WA USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAVan Dalfsen, Jill M.论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Fdn Therapeut Dev Network, Seattle Childrens Res Inst, Seattle, WA USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USAJoseloff, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Fdn Therapeut, Bethesda, MD USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USARamsey, Bonnie W.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA Cyst Fibrosis Fdn Therapeut Dev Network, Seattle Childrens Res Inst, Seattle, WA USA Univ Alabama, Dept Med, Tuscaloosa, AL 35487 USA
- [9] Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770[J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2009, 106 (44) : 18825 - 18830Van Goor, Fredrick论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAHadida, Sabine论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAGrootenhuis, Peter D. J.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USABurton, Bill论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USACao, Dong论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USANeuberger, Tim论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USATurnbull, Amanda论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USASingh, Ashvani论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAJoubran, John论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAHazlewood, Anna论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAZhou, Jinglan论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAMcCartney, Jason论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAArumugam, Vijayalaksmi论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USADecker, Caroline论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAYang, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAYoung, Chris论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAOlson, Eric R.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, Cambridge, MA 02139 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAWine, Jeffery J.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Psychol, Cyst Fibrosis Res Lab, Stanford, CA 94305 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAFrizzell, Raymond A.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Sch Med, Dept Cell Biol & Physiol, Pittsburgh, PA 15261 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USAAshlock, Melissa论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Fdn Therapeut Inc, Bethesda, MD 20814 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USANegulescu, Paul论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA