Effects of Ivacaftor in Three Pediatric Siblings With Cystic Fibrosis Carrying the Mutations G551D And F508del

被引：7
作者：
Mainz, Jochen G. [1 ]
Arnold, Christin [1 ]
Hentschel, Julia [1 ,2 ]
Tabori, Harold [1 ,3 ]
机构：
[1] Jena Univ Hosp, Dept Pediat, Cyst Fibrosis Ctr, Jena, Germany
[2] Univ Hosp Leipzig, Inst Human Genet, Leipzig, Germany
[3] Jena Univ Hosp, Dept Internal Med Gastroenterol Hepatol & Infect, Jena, Germany
来源：
ARCHIVOS DE BRONCONEUMOLOGIA | 2018年 / 54卷 / 04期
关键词：
CFTR POTENTIATOR; VX-770;
D O I：
10.1016/j.arbres.2017.09.012
中图分类号：
R56 [呼吸系及胸部疾病];
学科分类号：
摘要：
[No abstract available]
引用
收藏
页码：232 / 234
页数：3
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