Silencing Mutant Htt by AAV-Mediated Expression of RNAi Ameliorates Disease Manifestations in the YAC128 Mouse Model of Huntington's Disease

被引：0
|
作者：
Stanek, Lisa M. [1 ]
Shihabuddin, Lamya S. [1 ]
Cheng, Seng H. [1 ]
机构：
[1] Genzyme Corp, Rare Dis Sci, Framingham, MA 01701 USA
来源：
MOLECULAR THERAPY | 2013年 / 21卷
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
282
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页码：S108 / S108
页数：1
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