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Recombinant adeno-associated virus gene therapy for cystic fibrosis and α1-antitrypsin deficiency
被引:14
作者
:
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Florida, Gene Therapy Ctr, Gainesville, FL 32610 USA
Univ Florida, Gene Therapy Ctr, Gainesville, FL 32610 USA
Flotte, TR
[
1
]
机构
:
[1]
Univ Florida, Gene Therapy Ctr, Gainesville, FL 32610 USA
来源
:
CHEST
|
2002年
/ 121卷
/ 03期
关键词
:
D O I
:
10.1378/chest.121.3_suppl.98S
中图分类号
:
R4 [临床医学];
学科分类号
:
1002 ;
100602 ;
摘要
:
引用
收藏
页码:98S / 102S
页数:5
相关论文
共 32 条
[1]
In vivo model of adeno-associated virus vector persistence and rescue
Afione, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Afione, SA
Conrad, CK
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Conrad, CK
Kearns, WG
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Kearns, WG
Chunduru, S
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Chunduru, S
Adams, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Adams, R
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Reynolds, TC
Guggino, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Guggino, WB
Cutting, GR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Cutting, GR
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Carter, BJ
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Flotte, TR
[J].
JOURNAL OF VIROLOGY,
1996,
70
(05)
: 3235
-
3241
[2]
THE CRYPTIC LIFE-STYLE OF ADENOASSOCIATED VIRUS
BERNS, KI
论文数:
0
引用数:
0
h-index:
0
机构:
Dept of Microbiology, Cornell University Medical College, New York, New York, 10021
BERNS, KI
LINDEN, RM
论文数:
0
引用数:
0
h-index:
0
机构:
Dept of Microbiology, Cornell University Medical College, New York, New York, 10021
LINDEN, RM
[J].
BIOESSAYS,
1995,
17
(03)
: 237
-
245
[3]
BLACKLOW N R, 1988, P165
[4]
EPIDEMIOLOGY OF ADENOVIRUS-ASSOCIATED VIRUS INFECTION IN A NURSERY POPULATION
BLACKLOW, NR
论文数:
0
引用数:
0
h-index:
0
BLACKLOW, NR
HOGGAN, MD
论文数:
0
引用数:
0
h-index:
0
HOGGAN, MD
KAPIKIAN, AZ
论文数:
0
引用数:
0
h-index:
0
KAPIKIAN, AZ
AUSTIN, JB
论文数:
0
引用数:
0
h-index:
0
AUSTIN, JB
ROWE, WP
论文数:
0
引用数:
0
h-index:
0
ROWE, WP
[J].
AMERICAN JOURNAL OF EPIDEMIOLOGY,
1968,
88
(03)
: 368
-
&
[5]
Conrad CK, 1996, GENE THER, V3, P658
[6]
A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation
Duan, DS
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Duan, DS
Yue, YP
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Yue, YP
Yan, ZY
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Yan, ZY
Engelhardt, JF
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Engelhardt, JF
[J].
NATURE MEDICINE,
2000,
6
(05)
: 595
-
598
[7]
DEFECTIVE REGULATION OF OUTWARDLY RECTIFYING CL- CHANNELS BY PROTEIN KINASE-A CORRECTED BY INSERTION OF CFTR
EGAN, M
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
EGAN, M
FLOTTE, T
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
FLOTTE, T
AFIONE, S
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
AFIONE, S
SOLOW, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
SOLOW, R
ZEITLIN, PL
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
ZEITLIN, PL
CARTER, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
CARTER, BJ
GUGGINO, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
GUGGINO, WB
[J].
NATURE,
1992,
358
(6387)
: 581
-
584
[8]
A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease
Flotte, T
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Flotte, T
Carter, B
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Carter, B
Conrad, C
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Conrad, C
Guggino, W
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Guggino, W
Reynolds, T
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Reynolds, T
Rosenstein, B
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Rosenstein, B
Taylor, G
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Taylor, G
Walden, S
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Walden, S
Wetzel, R
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Wetzel, R
[J].
HUMAN GENE THERAPY,
1996,
7
(09)
: 1145
-
1159
[9]
Flotte TR, 1998, METHOD ENZYMOL, V292, P717
[10]
STABLE IN-VIVO EXPRESSION OF THE CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR WITH AN ADENOASSOCIATED VIRUS VECTOR
FLOTTE, TR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
FLOTTE, TR
AFIONE, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
AFIONE, SA
CONRAD, C
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
CONRAD, C
MCGRATH, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
MCGRATH, SA
SOLOW, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
SOLOW, R
OKA, H
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
OKA, H
ZEITLIN, PL
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
ZEITLIN, PL
GUGGINO, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
GUGGINO, WB
CARTER, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
CARTER, BJ
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1993,
90
(22)
: 10613
-
10617
←
1
2
3
4
→
共 32 条
[1]
In vivo model of adeno-associated virus vector persistence and rescue
Afione, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Afione, SA
Conrad, CK
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Conrad, CK
Kearns, WG
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Kearns, WG
Chunduru, S
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Chunduru, S
Adams, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Adams, R
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Reynolds, TC
Guggino, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Guggino, WB
Cutting, GR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Cutting, GR
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Carter, BJ
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Flotte, TR
[J].
JOURNAL OF VIROLOGY,
1996,
70
(05)
: 3235
-
3241
[2]
THE CRYPTIC LIFE-STYLE OF ADENOASSOCIATED VIRUS
BERNS, KI
论文数:
0
引用数:
0
h-index:
0
机构:
Dept of Microbiology, Cornell University Medical College, New York, New York, 10021
BERNS, KI
LINDEN, RM
论文数:
0
引用数:
0
h-index:
0
机构:
Dept of Microbiology, Cornell University Medical College, New York, New York, 10021
LINDEN, RM
[J].
BIOESSAYS,
1995,
17
(03)
: 237
-
245
[3]
BLACKLOW N R, 1988, P165
[4]
EPIDEMIOLOGY OF ADENOVIRUS-ASSOCIATED VIRUS INFECTION IN A NURSERY POPULATION
BLACKLOW, NR
论文数:
0
引用数:
0
h-index:
0
BLACKLOW, NR
HOGGAN, MD
论文数:
0
引用数:
0
h-index:
0
HOGGAN, MD
KAPIKIAN, AZ
论文数:
0
引用数:
0
h-index:
0
KAPIKIAN, AZ
AUSTIN, JB
论文数:
0
引用数:
0
h-index:
0
AUSTIN, JB
ROWE, WP
论文数:
0
引用数:
0
h-index:
0
ROWE, WP
[J].
AMERICAN JOURNAL OF EPIDEMIOLOGY,
1968,
88
(03)
: 368
-
&
[5]
Conrad CK, 1996, GENE THER, V3, P658
[6]
A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation
Duan, DS
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Duan, DS
Yue, YP
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Yue, YP
Yan, ZY
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Yan, ZY
Engelhardt, JF
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Iowa, Coll Med, Dept Anat & Cell Biol, Iowa City, IA 52242 USA
Engelhardt, JF
[J].
NATURE MEDICINE,
2000,
6
(05)
: 595
-
598
[7]
DEFECTIVE REGULATION OF OUTWARDLY RECTIFYING CL- CHANNELS BY PROTEIN KINASE-A CORRECTED BY INSERTION OF CFTR
EGAN, M
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
EGAN, M
FLOTTE, T
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
FLOTTE, T
AFIONE, S
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
AFIONE, S
SOLOW, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
SOLOW, R
ZEITLIN, PL
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
ZEITLIN, PL
CARTER, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
CARTER, BJ
GUGGINO, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL & BIOPHYS,BALTIMORE,MD 21205
GUGGINO, WB
[J].
NATURE,
1992,
358
(6387)
: 581
-
584
[8]
A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease
Flotte, T
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Flotte, T
Carter, B
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Carter, B
Conrad, C
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Conrad, C
Guggino, W
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Guggino, W
Reynolds, T
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Reynolds, T
Rosenstein, B
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Rosenstein, B
Taylor, G
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Taylor, G
Walden, S
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Walden, S
Wetzel, R
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Children's Center, Baltimore, MD
Wetzel, R
[J].
HUMAN GENE THERAPY,
1996,
7
(09)
: 1145
-
1159
[9]
Flotte TR, 1998, METHOD ENZYMOL, V292, P717
[10]
STABLE IN-VIVO EXPRESSION OF THE CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR WITH AN ADENOASSOCIATED VIRUS VECTOR
FLOTTE, TR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
FLOTTE, TR
AFIONE, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
AFIONE, SA
CONRAD, C
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
CONRAD, C
MCGRATH, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
MCGRATH, SA
SOLOW, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
SOLOW, R
OKA, H
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
OKA, H
ZEITLIN, PL
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
ZEITLIN, PL
GUGGINO, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
GUGGINO, WB
CARTER, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV,SCH MED,DEPT PHYSIOL,BALTIMORE,MD 21205
CARTER, BJ
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1993,
90
(22)
: 10613
-
10617
←
1
2
3
4
→