218th ENMC International Workshop: Revisiting the consensus on standards of care in SMA Naarden, The Netherlands, 19-21 February 2016

被引：49
作者：
Finkel, Richard S. [1 ]
Sejersen, Thomas [2 ,3 ]
Mercuri, Eugenio [4 ,5 ]
机构：
[1] Nemours Childrens Hosp, Pediat Neurol, Orlando, FL USA
[2] Karolinska Inst, Pediat Neurol, Stockholm, Sweden
[3] Karolinska Univ Hosp, Stockholm, Sweden
[4] Catholic Univ, Policlin Gemelli, Pediat Neurol, Rome, Italy
[5] Ctr Nemo, Rome, Italy
来源：
NEUROMUSCULAR DISORDERS | 2017年 / 27卷 / 06期
关键词：
SPINAL MUSCULAR-ATROPHY; WERDNIG-HOFFMANN-DISEASE; NATURAL-HISTORY; CLINICAL-TRIALS; GENOTYPE-PHENOTYPE; GROWING RODS; SURVIVAL; TYPE-2; APPLICABILITY; POPULATION;
D O I：
10.1016/j.nmd.2017.02.014
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：596 / 605
页数：10
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