Self-Inactivating Lentiviral Vectors for Correction of Rag1 Severe Combined Immunodeficiency

被引：0

作者：

Pike-Overzet, Karin ^{[1
]}

Wiekmeijer, Anna-Sophia ^{[1
]}

Baert, Miranda R. M. ^{[1
]}

Lagresle-Peyrou, Chantal ^{[2
,3
]}

Schambach, Axel ^{[4
]}

Zhang, Fang ^{[5
]}

Hoeben, Rob C. ^{[5
]}

Hacein-Bey-Abina, Salima ^{[2
,3
]}

Lankester, Arjen C. ^{[6
]}

Bredius, Robbert G. M. ^{[6
]}

Driessen, Gertjan J. A. ^{[7
]}

Thrasher, Adrian J. ^{[5
]}

Baum, Christopher ^{[4
]}

Cavazzana-Calvo, Marina ^{[2
,3
]}

van Dongen, Jacques J. M. ^{[8
]}

Staal, Frank J. T. ^{[1
]}

机构：

[1] LUMC, IHB, Leiden, Netherlands

[2] INSERM, Dept Biotherapy, Paris, France

[3] Hop Necker Enfants Malad, Paris, France

[4] Hannover Med Sch, Inst Expt Hematol, Hannover, Germany

[5] UCL, Inst Child Hlth, Mol Immunol Unit, London, England

[6] LUMC, MCB, Leiden, Netherlands

[7] LUMC, Leiden, Netherlands

[8] Erasmus MC, Pediat, Rotterdam, Netherlands

来源：

MOLECULAR THERAPY | 2013年 / 21卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

313

引用

页码：S120 / S121

页数：2

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