Lentiviral Vector Mediated Haematopoietic Stem Cell Gene Therapy for the Treatment of Lysosomal Disease

被引：0

作者：

McDermott, J. H. ^{[1
]}

Langford-Smith, A. ^{[1
]}

Sergijenko, A. ^{[1
]}

Langford-Smith, K. J. ^{[1
]}

Liao, A. ^{[1
]}

Jones, S. A. ^{[2
]}

Wraith, J. E. ^{[2
]}

Wynn, R. F. ^{[3
]}

Wilkinson, F. W. ^{[1
]}

Bigger, B. W. ^{[1
]}

机构：

[1] Univ Manchester, Manchester, Lancs, England

[2] St Marys Hosp, Manchester M13 0JH, Lancs, England

[3] RMCH, Blood & Marrow Transplant Unit, Manchester, Lancs, England

来源：

JOURNAL OF PATHOLOGY | 2013年 / 231卷

关键词：

D O I：

暂无

中图分类号：

R73 [肿瘤学];

学科分类号：

100214 ;

摘要：

引用

页码：20 / 20

页数：1

共 50 条

[41] High-resolution cellular and molecular follow up of lysosomal disease patients treated with hematopoietic stem cell lentiviral gene therapy [J].

Loperfido, Mariana ;

Baricordi, Cristina ;

Yan, Aimin ;

Barbarossa, Luigi ;

Nguyen, Quoc ;

Abrahamsen, Ingrid ;

Cherqui, Stephanie ;

Escolar, Diana ;

Mason, Chris ;

Biasco, Luca .

MOLECULAR GENETICS AND METABOLISM, 2022, 135 (02) :S75-S76

[42] Gene Therapy for Lysosomal Storage Diseases using an enhanced lentiviral vector delivery system [J].

Alonso-Ferrero, Maria E. ;

Langford-Smith, Alexander ;

Burke, Derek ;

Heales, Simon ;

Bigger, Brian W. ;

Thrasher, Adrian ;

Gaspar, Bobby .

HUMAN GENE THERAPY, 2012, 23 (05) :A14-A14

[43] Immunological barriers to haematopoietic stem cell gene therapy [J].

Carsten T. Charlesworth ;

Ian Hsu ;

Adam C. Wilkinson ;

Hiromitsu Nakauchi .

Nature Reviews Immunology, 2022, 22 :719-733

[44] Immunological barriers to haematopoietic stem cell gene therapy [J].

Charlesworth, Carsten T. ;

Hsu, Ian ;

Wilkinson, Adam C. ;

Nakauchi, Hiromitsu .

NATURE REVIEWS IMMUNOLOGY, 2022, 22 (12) :719-733

[45] Optimizing lentiviral vector transduction of hematopoietic stem cells for gene therapy [J].

Yoonjeong Jang ;

Yoon-Sang Kim ;

Matthew M. Wielgosz ;

Francesca Ferrara ;

Zhijun Ma ;

Jose Condori ;

Lance E. Palmer ;

Xiwen Zhao ;

Guolian Kang ;

David J. Rawlings ;

Sheng Zhou ;

Byoung Y. Ryu .

Gene Therapy, 2020, 27 :545-556

[46] Optimizing lentiviral vector transduction of hematopoietic stem cells for gene therapy [J].

Jang, Yoonjeong ;

Kim, Yoon-Sang ;

Wielgosz, Matthew M. ;

Ferrara, Francesca ;

Ma, Zhijun ;

Condori, Jose ;

Palmer, Lance E. ;

Zhao, Xiwen ;

Kang, Guolian ;

Rawlings, David J. ;

Zhou, Sheng ;

Ryu, Byoung Y. .

GENE THERAPY, 2020, 27 (12) :545-556

[47] Enhancing the potency of in vivo lentiviral vector mediated gene therapy to hepatocytes [J].

Canepari, Cesare ;

Milani, Michela ;

Simoni, Chiara ;

Starinieri, Francesco ;

Volpin, Monica ;

Fabiano, Anna ;

Biffi, Mauro ;

Russo, Fabio ;

Norata, Rossana ;

Rocchi, Martina ;

Brombin, Chiara ;

Cugnata, Federica ;

Montini, Eugenio ;

Sanvito, Francesca ;

Grompe, Markus ;

Cantore, Alessio .

NATURE COMMUNICATIONS, 2025, 16 (01)

[48] Lentiviral Vector-Based Gene Therapy in Parkinson Disease [J].

Richardson, Mark .

NEUROSURGERY, 2014, 74 (06) :N11-N12

[49] Myeloid Driven Stem Cell Gene Therapy Corrects the Neuropathology of Lysosomal Disease [J].

McDermott, J. H. ;

Sergijenko, A. ;

Langford-Smith, A. ;

Liao, A. ;

Pickford, C. E. ;

Nowinski, G. ;

Langford-Smith, K. J. ;

Merry, C. L. R. ;

Jones, S. A. ;

Wraith, J. E. ;

Wynn, R. F. ;

Wilkinson, F. W. ;

Bigger, B. W. .

JOURNAL OF PATHOLOGY, 2013, 229 :S30-S30

[50] ADVANCING LENTIVIRAL VECTOR MANUFACTURE FOR CLINICAL CELL AND GENE THERAPY [J].

Michelet, F. ;

Szyniarowski, P. ;

Radhakrishnan, S. ;

Sin, W. ;

Leo, V. Ivon ;

Alagppan, D. ;

Lam, P. ;

Chan, L. .

CYTOTHERAPY, 2021, 23 (05) :S174-S175

← 1 2 3 4 5 →