共 50 条
[21]
Hematopoietic Stem Cell Lentiviral Gene Therapy for the Treatment of Angelman Syndrome
[J].
Luthers, Christopher
;
Juett, Colin
;
Cirigliano, Samuel
;
Quintos, Jason
;
Mittelhauser, Annika
;
Wu, Xiaomeng
;
Lueptow, Lindsay
;
Zhuravka, Irina
;
Medel, Servando
;
Santana-Gomez, Cesar
;
Shamas, Mohamad
;
Han, Linna
;
Keung, Albert
;
Staba, Richard
;
Mazarati, Andrey
;
Panagoulias, Jennifer
;
Berent, Allyson
;
Hollis, Roger
;
Kohn, Donald
.
MOLECULAR THERAPY,
2025, 33 (04)

Luthers, Christopher
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Juett, Colin
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Cirigliano, Samuel
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Quintos, Jason
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Mittelhauser, Annika
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Wu, Xiaomeng
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Lueptow, Lindsay
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Zhuravka, Irina
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Medel, Servando
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Santana-Gomez, Cesar
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Shamas, Mohamad
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Han, Linna
论文数: 0 引用数: 0
h-index: 0
机构:
North Carolina State Univ, Raleigh, NC USA UCLA, Los Angeles, CA USA

Keung, Albert
论文数: 0 引用数: 0
h-index: 0
机构: UCLA, Los Angeles, CA USA

Staba, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Mazarati, Andrey
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Panagoulias, Jennifer
论文数: 0 引用数: 0
h-index: 0
机构:
AS2 Bio, Middleton, MA USA UCLA, Los Angeles, CA USA

Berent, Allyson
论文数: 0 引用数: 0
h-index: 0
机构:
Fdn Angelman Syndrome Therapeut, New York, NY USA UCLA, Los Angeles, CA USA

Hollis, Roger
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA UCLA, Los Angeles, CA USA

Kohn, Donald
论文数: 0 引用数: 0
h-index: 0
机构:
UCLA, Los Angeles, CA USA
Univ Calif Tarzana, Tarzana, CA USA UCLA, Los Angeles, CA USA
[22]
Development of Lentiviral Mediated Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIIA
[J].
Ellison, Stuart
;
Sergijenko, Ana
;
Langford-Smith, Alex
;
Langford-Smith, Kia
;
Wraith, Ed
;
Wynn, Rob
;
Wilkinson, Fiona
;
Bigger, Brian
.
MOLECULAR THERAPY,
2014, 22
:S8-S8

论文数: 引用数:
h-index:
机构:

Sergijenko, Ana
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England

论文数: 引用数:
h-index:
机构:

Langford-Smith, Kia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England

Wraith, Ed
论文数: 0 引用数: 0
h-index: 0
机构:
Cent Manchester Hosp NHS Fdn Trust CMFT, Bone Marrow Transplant Unit, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England

Wynn, Rob
论文数: 0 引用数: 0
h-index: 0
机构:
Cent Manchester Hosp NHS Fdn Trust CMFT, Bone Marrow Transplant Unit, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England

Wilkinson, Fiona
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England

Bigger, Brian
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England
[23]
Pre-clinical Safety and Efficacy of Lentiviral Vector-Mediated Ex Vivo Stem Cell Gene Therapy for the Treatment of Mucopolysaccharidosis IIIA
[J].
Ellison, Stuart M.
;
Liao, Aiyin
;
Wood, Shaun
;
Taylor, Jessica
;
Youshani, Amir Saam
;
Rowlston, Sam
;
Parker, Helen
;
Armant, Myriam
;
Biffi, Alessandra
;
Chang, Lucas
;
Farzaneh, Farzin
;
Wynn, Rob
;
Jones, Simon A.
;
Heal, Paul
;
Gaspar, H. Bobby
;
Bigger, Brian W.
.
MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT,
2019, 13
:399-413

Ellison, Stuart M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Liao, Aiyin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Wood, Shaun
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Taylor, Jessica
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Youshani, Amir Saam
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Rowlston, Sam
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Parker, Helen
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Armant, Myriam
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston Childrens Canc & Blood Disorders Ctr, Boston, MA 02115 USA Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Biffi, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Boston Childrens Canc & Blood Disorders Ctr, Boston, MA 02115 USA Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Chang, Lucas
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, Mol Med Grp, Rayne Inst, Sch Canc & Pharmaceut Sci, London SE5 9NT, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Farzaneh, Farzin
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, Mol Med Grp, Rayne Inst, Sch Canc & Pharmaceut Sci, London SE5 9NT, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Wynn, Rob
论文数: 0 引用数: 0
h-index: 0
机构:
NHS Trust, Manchester Childrens Hosp, Manchester M13 9WL, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Jones, Simon A.
论文数: 0 引用数: 0
h-index: 0
机构:
NHS Trust, Manchester Childrens Hosp, Manchester M13 9WL, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Heal, Paul
论文数: 0 引用数: 0
h-index: 0
机构:
Orchard Therapeut Ltd, London EC4N 6EU, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Gaspar, H. Bobby
论文数: 0 引用数: 0
h-index: 0
机构:
Orchard Therapeut Ltd, London EC4N 6EU, England
UCL, Inst Child Hlth, London WC1N 1EH, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England

Bigger, Brian W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England Univ Manchester, Div Cell Matrix Biol & Regenerat Med, Fac Biol Med & Hlth, Stem Cell & Neurotherapies Grp,Sch Biol Sci, 3-721 Stopford Bldg,Oxford Rd, Manchester M13 9PT, Lancs, England
[24]
Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophy
[J].
Ungari, Silvia
;
Montepeloso, Annita
;
Morena, Francesco
;
Cocchiarella, Fabienne
;
Recchia, Alessandra
;
Martino, Sabata
;
Gentner, Bernhard
;
Naldini, Luigi
;
Biffi, Alessandra
.
MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT,
2015, 2
:15038

Ungari, Silvia
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy

Montepeloso, Annita
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy

论文数: 引用数:
h-index:
机构:

Cocchiarella, Fabienne
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Modena & Reggio Emilia, Dept Life Sci, Ctr Regenerat Med Stefano Ferrari, Modena, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy

Recchia, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Modena & Reggio Emilia, Dept Life Sci, Ctr Regenerat Med Stefano Ferrari, Modena, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy

论文数: 引用数:
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Gentner, Bernhard
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy

Naldini, Luigi
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy
Univ Vita Salute San Raffaele, Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy

Biffi, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy
Univ Vita Salute San Raffaele, Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Milan, Italy
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Split Intein Lentiviral Vector Hematopoietic Stem Cell Gene Therapy for the Treatment of DOCK8 Deficiency
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Sinha, Vrishti
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Long, Joseph
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Takenami, Ashley
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Kuo, Caroline
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MOLECULAR THERAPY,
2025, 33 (04)

Sinha, Vrishti
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USA

Long, Joseph
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USA

Takenami, Ashley
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USA

Kuo, Caroline
论文数: 0 引用数: 0
h-index: 0
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Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USA
[26]
Haematopoietic stem cell based gene therapy for the treatment of metachromatic leukodystrophy
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Biffi, A.
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Sessa, M.
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Capotondo, A.
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Cesani, M.
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Fasano, S.
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Del Carro, U.
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Tononi, L.
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Marchesini, S.
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Brambilla, R.
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Grompe, M.
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Quattrini, A.
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Bordignon, C.
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Roncarolo, M. G.
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Rovelli, A.
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Naldini, L.
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BONE MARROW TRANSPLANTATION,
2007, 39
:S36-S36

Biffi, A.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Sessa, M.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Capotondo, A.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Cesani, M.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Fasano, S.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Del Carro, U.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Tononi, L.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Marchesini, S.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Brambilla, R.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

论文数: 引用数:
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机构:

Quattrini, A.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Bordignon, C.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Roncarolo, M. G.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Rovelli, A.
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Sci Inst, I-20132 Milan, Italy

Naldini, L.
论文数: 0 引用数: 0
h-index: 0
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[27]
Lentiviral Vector-Mediated Ex Vivo Hematopoietic Stem Cell Gene Therapy for Mucopolysaccharidosis IVA Murine Model
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Celik, Betul
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Rintz, Estera
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Sansanwal, Nidhi
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Khan, Shaukat
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Bigger, Brian
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Tomatsu, Shunji
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HUMAN GENE THERAPY,
2024, 35 (21-22)
:917-937

Celik, Betul
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Delaware, Dept Biol Sci, Newark, DE USA
Nemours Childrens Hlth, Skeletal Dysplasia Res Lab, 1600 Rockland Rd, Wilmington, DE 19803 USA Univ Delaware, Dept Biol Sci, Newark, DE USA

Rintz, Estera
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hlth, Skeletal Dysplasia Res Lab, 1600 Rockland Rd, Wilmington, DE 19803 USA
Univ Gdansk, Fac Biol, Dept Mol Biol, Gdansk, Poland Univ Delaware, Dept Biol Sci, Newark, DE USA

Sansanwal, Nidhi
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Delaware, Dept Biol Sci, Newark, DE USA
Nemours Childrens Hlth, Skeletal Dysplasia Res Lab, 1600 Rockland Rd, Wilmington, DE 19803 USA Univ Delaware, Dept Biol Sci, Newark, DE USA

Khan, Shaukat
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hlth, Skeletal Dysplasia Res Lab, 1600 Rockland Rd, Wilmington, DE 19803 USA Univ Delaware, Dept Biol Sci, Newark, DE USA

Bigger, Brian
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Edinburgh, Inst Regenerat & Repair, Edinburgh, Scotland Univ Delaware, Dept Biol Sci, Newark, DE USA

Tomatsu, Shunji
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h-index: 0
机构:
Nemours Childrens Hlth, Skeletal Dysplasia Res Lab, 1600 Rockland Rd, Wilmington, DE 19803 USA Univ Delaware, Dept Biol Sci, Newark, DE USA
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Lentiviral vector mediated gene therapy for Parkinson's disease. What are the issues?
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Jolly, DJ
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CELL TRANSPLANTATION,
2003, 12 (03)
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Jolly, DJ
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BioMedica Inc, San Diego, CA USA BioMedica Inc, San Diego, CA USA
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Targeting the blood-brain barrier to increase haematopoietic stem cell engraftment for neurological lysosomal storage disease gene and cell therapy
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Critchley, B. J.
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Gaspar, H. B.
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Benedetti, S.
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HUMAN GENE THERAPY,
2021, 32 (19-20)
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Critchley, B. J.
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h-index: 0
机构:
UCL Inst Child Hlth, London, England UCL Inst Child Hlth, London, England

Gaspar, H. B.
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h-index: 0
机构:
UCL Inst Child Hlth, London, England
Orchard Therapeut Ltd, London, England UCL Inst Child Hlth, London, England

Benedetti, S.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, London, England
NIHR Great Ormond St Hosp Biomed Res Ctr, London, England UCL Inst Child Hlth, London, England
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A Lentiviral Vector-Based Gene Therapy Product for the Treatment of Wilson Disease
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Khoo, Cheen
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Hammond, Suzan M.
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Sherrington, Sarah
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Martins, Laura
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Powles, Robert J.
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Kennedy, Vicky
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Guzman, Efrain
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O'Connor, Deirdre
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Mitrophanous, Kyriacos
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Lad, Yatish
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MOLECULAR THERAPY,
2023, 31 (04)
:546-546

Khoo, Cheen
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h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Hammond, Suzan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Sherrington, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Martins, Laura
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Powles, Robert J.
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Kennedy, Vicky
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Guzman, Efrain
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

O'Connor, Deirdre
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Mitrophanous, Kyriacos
论文数: 0 引用数: 0
h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England

Lad, Yatish
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h-index: 0
机构:
Oxford Biomed, Oxford, England Oxford Biomed, Oxford, England